Low Dose Treosulfan Based Conditioning Regimen in HSCT for Nijmegen Breakage Syndrome

Phase 2 Unknown 10 enrolled Federal Research Institute of Pediatric Hematology, Oncology and Immunology

NaSingle-groupOpen-labelTreatment

Summary

The aim of the current study is to evaluate the safety and efficacy of low dose treosulfan based conditioning regimen in HSCT in Nijmegen breakage syndrome

Timeline

Start: 2020-05-22
Primary completion: 2023-05
Completion: 2023-05

Drugs

Evaluation	Drug	Modality	Dose	Route
Subject	Treosulfan	Small molecule	21 mg/m2	—

Low Dose Treosulfan Based Conditioning Regimen in HSCT for Nijmegen Breakage Syndrome

Summary

Timeline

Drugs

Indications