drugset / Trial / NCT04409691

SCMC Trial on KHE With KMP (V.2020)

NCT04409691

Phase 1 Unknown 20 enrolled Shanghai Children's Medical Center
RandomizedParallel-groupOpen-labelTreatment

Summary

a phase I trial focusing on safety and efficacy of prednison shock plus sirolimus maintenance in treating Kaposiform hemangioendothelioma (KHE) with Kasabach-Merritt phenomenon (KMP)

Timeline

Start
2020-07-01
Primary completion
2023-01-31
Completion
2023-06-30

Drugs

EvaluationDrugModalityDoseRoute
Comparator Prednisone Other / unclassified 2 mg/kg Intravenous
Subject Sirolimus Small molecule 0.8 mg/m2 Oral