Drugs / Sirolimus
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Sirolimus

also known as rapamycin · Rapamune · SRL · RAPA · PTX-022 · SIR · DE-109 · Encapsulated Rapamycin · +23 more

Small molecule targets CXCR4, IL2, MTOR via inhibition

Developed for
graft versus host disease · plasma cell myeloma · Hodgkins lymphoma · kidney failure · tuberous sclerosis · acute myeloid leukemia · cancer · leukemia
+294 more · acute lymphoblastic leukemia · cancer of unknown primary site · chronic myeloid leukemia · disease related to solid organ transplantation · non-small cell lung carcinoma · transplant rejection · type 1 diabetes mellitus · kaposiform hemangioendothelioma · vascular malformation · end stage renal failure · lymphangioleiomyomatosis · lymphatic malformation · lymphoma · sickle cell disease · age-related macular degeneration · aplastic anemia · chronic renal failure syndrome · non-Hodgkin lymphoma · renal cell carcinoma · breast cancer · chronic graft versus host disease · classic familial adenomatous polyposis · coronary restenosis · disease related to hematopoietic stem cell transplant · kidney disorder · mantle cell lymphoma · microcystic lymphatic malformation · osteosarcoma · ovarian carcinoma · prostate cancer · skin cancer · systemic lupus erythematosus · urinary bladder carcinoma · vascular neoplasm · acute graft versus host disease · acute myeloid leukemia with 11q23 abnormalities · acute myeloid leukemia with t(8;21)(q22;q22) translocation · autosomal dominant polycystic kidney disease · Burkitt lymphoma · capillary malformation · central nervous system neoplasm · childhood malignant neoplasm · coronary artery disorder · Ewing sarcoma · female breast carcinoma · germ cell tumor · hepatocellular carcinoma · HIV infectious disease · Kasabach-Merritt syndrome · liver cancer · liver disorder · malignant pancreatic neoplasm · malignant peripheral nerve sheath tumor · metastatic malignant neoplasm · neuroblastoma · pachyonychia congenita · peripheral arterial disease · polycystic kidney disease · posterior uveitis · premature aging syndrome · PTEN hamartoma tumor syndrome · tufted angioma · acute erythroid leukemia · acute megakaryoblastic leukemia in adult · acute myeloblastic leukemia with maturation · acute myeloblastic leukemia without maturation · acute myeloid leukemia with abnormal bone marrow eosinophils inv(16)(p13q22) or t(16;16)(p13;q22) · acute myeloid leukemia, inv(16)(p13.1;q22) · acute myeloid leukemia, t(16;16)(p13.1;q22) · acute myelomonocytic leukemia M4 · acute transplant rejection · adult acute monocytic leukemia · Alzheimer disease · autoimmune hemolytic anemia, warm type · benign vascular tumor · beta thalassemia · cancer or benign tumor · castration-resistant prostate carcinoma · choroidal neovascularization · chronic kidney disease · Cowden disease · diabetic macular edema · diffuse secondary choroid atrophy · disease of orbital part of eye adnexa · disease related to transplantation · epidermolysis bullosa simplex · epilepsy · glioblastoma · hemangioendothelioma · hereditary hemorrhagic telangiectasia · hormone receptor-positive breast cancer · hypopigmentation of the skin · intermediate uveitis · intracerebral hemorrhage · lymphoblastic lymphoma · lymphoproliferative syndrome · metastatic neoplasm · metastatic prostate carcinoma · neoplasm · neurofibromatosis · neurofibromatosis type 1 · panuveitis · PIK3CA-related overgrowth spectrum · precursor lymphoblastic lymphoma/leukemia · primary peritoneal carcinoma · refractory malignant neoplasm · rhabdomyosarcoma · sarcoma · soft tissue sarcoma · squamous cell lung carcinoma · Sturge-Weber syndrome · thalassemia · thrombocytopenia · uterine adnexa cancer · uveitis · Wilms tumor · acanthosis nigricans · activated PI3K-delta syndrome · acute leukemia of ambiguous lineage · acute myeloid leukemia with minimal differentiation · acute myeloid leukemia, del(5q31-q32) · adult T-cell leukemia/lymphoma · adult-onset Still disease · anaplastic astrocytoma · anaplastic oligoastrocytoma · anaplastic oligodendroglioma · angiokeratoma · angiomyolipoma · anterior scleritis · anterior uveitis · antiphospholipid syndrome · arteriovenous hemangioma/malformation · astrocytoma (excluding glioblastoma) · atypical teratoid rhabdoid tumor · autism · autoimmune disease · autoimmune lymphoproliferative syndrome · autoimmune thrombocytopenia · autoimmune thrombocytopenic purpura · Birt-Hogg-Dube syndrome · blue rubber bleb nevus · brain aneurysm · brain neoplasm · breast neoplasm · bronchiolitis obliterans syndrome · carcinoma of esophagus · cerebral cavernous malformation · cerebrovascular disorder · cervical squamous cell carcinoma · chronic transplant rejection · clear cell sarcoma · colorectal carcinoma · congenital anomaly of cardiovascular system · congenital vascular malformation · COVID-19 · Crohn disease · cutaneous melanoma · cytomegalovirus infection · dedifferentiated chondrosarcoma · desmoid tumor · diabetic kidney disease · diabetic retinopathy · differentiated thyroid carcinoma · digestive system neuroendocrine neoplasm · dilated cardiomyopathy · dry eye syndrome · endometrial carcinoma · eosinophilic esophagitis · eosinophilic gastroenteritis · ependymoma · epithelioid hemangioendothelioma · estrogen-receptor negative breast cancer · estrogen-receptor positive breast cancer · Evans syndrome · fallopian tube cancer · fallopian tube carcinoma · focal segmental glomerulosclerosis · gastric carcinoma · gliosarcoma · head and neck carcinoma · heart failure · hemolytic anemia · hemophilia · hepatitis C virus infection · hepatoblastoma · Her2-receptor negative breast cancer · hereditary thrombocytopenia and hematological cancer predisposition syndrome associated with RUNX1 · high grade malignant neoplasm · hormone-resistant breast carcinoma · hormone-resistant prostate carcinoma · human herpesvirus 8 infection · hydrocephalus · hyperinsulinism · hypertensive disorder · hypertrophic cardiomyopathy · idiopathic pulmonary fibrosis · IgA glomerulonephritis · immunoglobulin G4-related sclerosing disease · impaired renal function disease · inclusion body myositis · infertility disorder · inflammatory bowel disease · juvenile nasopharyngeal angiofibroma · keloid · kidney angiomyolipoma · kidney cancer · large B-cell lymphoma · Leigh syndrome, mitochondrial · leiomyoma · lichen planus, oral · liver failure · long COVID-19 · low grade glioma · lung adenocarcinoma · lung cancer · lung carcinoma · lung lymphangioleiomyomatosis · lung neoplasm · lupus nephritis · lymphangiectasis · malignant epithelial tumor of ovary · medulloblastoma · membranous glomerulonephritis · mesenchymal chondrosarcoma · metastatic carcinoma in the bone · methylmalonic acidemia · multicentric Castleman disease · multifocal lymphangioendotheliomatosis-thrombocytopenia syndrome · multiple cutaneous and mucosal venous malformations · multiple system atrophy · muscular atrophy · myelodysplastic syndrome associated with isolated del(5q) · myxoid liposarcoma · neoplasm with perivascular epithelioid cell differentiation · neutropenia · nevoid basal cell carcinoma syndrome · non-invasive bladder urothelial carcinoma · normal pressure hydrocephalus · oral cavity neoplasm · ovarian serous tumor · pancreatic acinar cell carcinoma · pancreatic adenocarcinoma · pancreatic ductal adenocarcinoma · pancytopenia · paroxysmal nocturnal hemoglobinuria · pemphigus · Peutz-Jeghers syndrome · pineoblastoma · plastic bronchitis · polycystic kidney disease 1 · polycystic kidney disease 2 · polyposis · premature menopause · primary acquired red cell aplasia · primary antiphospholipid syndrome · primary cutaneous T-cell lymphoma · prostate carcinoma · pulmonary branch stenosis · pure red-cell aplasia · rectal cancer · refractory plasma cell neoplasm · relapsing-remitting multiple sclerosis · renal cell adenocarcinoma · retinoblastoma · rheumatoid arthritis · Sjogren syndrome · skin atrophy · skin basal cell carcinoma · skin sarcoidosis · skin squamous cell carcinoma · small cell lung carcinoma · squamous cell carcinoma · systemic sclerosis · tongue neoplasm · urothelial carcinoma · uterine carcinoma · uterine corpus cancer · wet macular degeneration · yolk sac tumor · acute respiratory distress syndrome · alcohol dependence · amyotrophic lateral sclerosis · autosomal dominant polycystic liver disease · BK-virus nephropathy · chronic granulomatous disease · cognitive impairment with or without cerebellar ataxia · hemangioma · influenza · nicotine dependence · post-traumatic stress disorder · pulmonary fibrosis · swine influenza · urinary bladder cancer · vitiligo
Investigated by
National Cancer Institute (NCI) · Wyeth is now a wholly owned subsidiary of Pfizer · Pfizer · Mayo Clinic · National Heart, Lung, and Blood Institute (NHLBI) · Dana-Farber Cancer Institute
+404 more · National Institute of Allergy and Infectious Diseases (NIAID) · Peking Union Medical College Hospital · CSPC ZhongQi Pharmaceutical Technology Co., Ltd. · University of Chicago · Santen Inc. · Yale University · M.D. Anderson Cancer Center · National Eye Institute (NEI) · Palvella Therapeutics, Inc. · Stanford University · Children's Hospital of Philadelphia · Fred Hutchinson Cancer Center · Nobelpharma · The University of Texas Health Science Center at San Antonio · Brigham and Women's Hospital · Children's Hospital Medical Center, Cincinnati · Emory University · Genentech, Inc. · Immune Tolerance Network (ITN) · MacuSight, Inc. · Massachusetts General Hospital · National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) · Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University · University of Washington · West China Hospital · Boston Children's Hospital · Genzyme, a Sanofi Company · Hoffmann-La Roche · National Institutes of Health (NIH) · National Taiwan University Hospital · Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins · The Hospital for Sick Children · University Hospital, Tours · University of Regensburg · Aadi Bioscience, Inc. · Abramson Cancer Center at Penn Medicine · AgelessRx · Children's Hospital of Fudan University · Cliniques universitaires Saint-Luc- Université Catholique de Louvain · Columbia University · Concept Medical Inc. · Jonsson Comprehensive Cancer Center · National Institute of Neurological Disorders and Stroke (NINDS) · National Institute on Aging (NIA) · North China Pharmaceutical Group Corporation · Peking University People's Hospital · Roswell Park Cancer Institute · Samsung Medical Center · Seoul National University Hospital · The Emmes Company, LLC · University of California, Irvine · University of California, San Francisco · University of Cincinnati · University of Miami · Air Force General Hospital of the PLA · Astellas Pharma Inc · AstraZeneca · Bayer · Beckman Laser Institute University of California Irvine · Bing Han · Biodexa Pharmaceuticals · Blood and Marrow Transplant Clinical Trials Network · Bristol-Myers Squibb · Cancer Insight, LLC · Celgene Corporation · Children's National Research Institute · Chinese SLE Treatment And Research Group · Chong Kun Dang Pharmaceutical · CoreLab Black Forest · Dr. Reddy's Laboratories Limited · Duke University · FDA Office of Orphan Products Development · French National Institute of Health and Medical Research · Fujisawa GmbH · all 410 on the full record

Regulatory milestones approvals, filings & regulatory actions · 8 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Label expansions (6) US (FDA) RAPAMUNE 2003-04-11 – 2015-05-28 fda.gov
Approved EU (EMA) Rapamune 2001-03-13 europa.eu
Approved US (FDA) RAPAMUNE 1999-09-15 fda.gov

Trials 478 · started per year

today
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PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 017 trials
Phase 0 NCT06658093 Mar 2026 → Jul 2028 expected The University of Texas Health Science Center at San Antonio Recruiting No outcome recorded
Phase 0 NCT07354620 Feb 2025 → Feb 2026 overdue premature aging syndrome The Christ Hospital Active not recruiting No outcome recorded
Phase 0 NCT06719791 Dec 2024 → Dec 2027 expected epilepsy Xuanwu Hospital, Beijing Recruiting No outcome recorded
Phase 0 NCT05532072 Sep 2022 → Sep 2023 disease of orbital part of eye adnexa First Affiliated Hospital Xi'an Jiaotong University Unknown No outcome recorded
Phase 0 NCT04200911 Jun 2020 → Jan 2022 Alzheimer disease The University of Texas Health Science Center at San Antonio Completed No outcome recorded
Phase 0 NCT04049552 Jan → Aug 2020 keloid The University of Texas Health Science Center at San Antonio Completed No outcome recorded
Phase 0 NCT04115800 Oct 2019 → May 2020 dry eye syndrome Instituto de Oftalmología Fundación Conde de Valenciana Completed No outcome recorded
Phase 0 NCT02646319 Jan 2016 → Sep 2017 cervical squamous cell carcinoma, endometrial carcinoma, female breast carcinoma, head and neck carcinoma +5 Mayo Clinic Completed No outcome recorded
Phase 0 NCT01822015 Mar 2013 → Dec 2019 acute erythroid leukemia, acute megakaryoblastic leukemia in adult, acute myeloblastic leukemia with maturation, acute myeloblastic leukemia without maturation +7 Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University Completed No outcome recorded
Phase 0 NCT01658007 Aug 2012 → Jan 2017 acute lymphoblastic leukemia, lymphoblastic lymphoma Children's Hospital Medical Center, Cincinnati Terminated No outcome recorded
Phase 186 trials
Phase 1 NCT07667413 Jul → Dec 2026 expected hereditary hemorrhagic telangiectasia Columbia University Recruiting No outcome recorded
Phase 1 NCT07581704 Jun 2026 → Jun 2029 expected plasma cell myeloma Christopher Strouse Recruiting No outcome recorded
Phase 1 NCT07058974 Aug 2025 → Jul 2026 overdue Icahn School of Medicine at Mount Sinai Recruiting No outcome recorded
Phase 1 NCT06941142 Apr 2025 → Oct 2027 expected breast cancer CSPC ZhongQi Pharmaceutical Technology Co., Ltd. Not yet recruiting No outcome recorded
Phase 1 NCT06743503 Apr 2025 → May 2028 expected large B-cell lymphoma Nanjing IASO Biotechnology Co., Ltd. Recruiting No outcome recorded
Phase 1 NCT06528301 Mar 2025 → Mar 2029 expected B-cell chronic lymphocytic leukemia, diffuse large B-cell lymphoma Umoja Biopharma Recruiting No outcome recorded
Phase 1 NCT05949658 May 2024 → Mar 2027 expected University of Wisconsin, Madison Recruiting No outcome recorded
Phase 1 NCT05840510 Aug 2023 → Dec 2024 metastatic malignant neoplasm, non-small cell lung carcinoma Mirati Therapeutics Inc. Terminated No outcome recorded
Phase 1 NCT05386914 Mar 2023 → Sep 2025 overdue disease of genetic or genomic mechanism University of Missouri-Columbia Active not recruiting No outcome recorded
Phase 1 NCT05508620 Oct 2022 → Dec 2024 cancer CSPC ZhongQi Pharmaceutical Technology Co., Ltd. Unknown No outcome recorded
Phase 1/253 trials
Phase 1/2 NCT07662174 Jan → Dec 2027 expected hydrocephalus Massachusetts General Hospital Not yet recruiting No outcome recorded
Phase 1/2 NCT06876142 Jul 2026 → Jan 2033 plasma cell myeloma, refractory plasma cell neoplasm National Cancer Institute (NCI) Suspended No outcome recorded
Phase 1/2 NCT07241936 Nov 2025 → Oct 2027 expected cancer CSPC ZhongQi Pharmaceutical Technology Co., Ltd. Recruiting No outcome recorded
Phase 1/2 NCT06080165 Jul 2024 → Jun 2028 PTEN hamartoma tumor syndrome Stanford University Withdrawn No outcome recorded
Phase 1/2 NCT06279494 Mar → Jun 2024 acute leukemia, aplastic anemia, myelodysplastic syndrome Peking University People's Hospital Unknown No outcome recorded
Phase 1/2 NCT06022068 Sep 2023 → Dec 2024 Alzheimer disease Karolinska Institutet Completed No outcome recorded
Phase 1/2 NCT05778877 Dec 2022 → Aug 2025 methylmalonic acidemia Selecta Biosciences, Inc. Withdrawn No outcome recorded
Phase 1/2 NCT05605665 Dec 2022 → Dec 2023 Sjogren syndrome Peking University People's Hospital Completed No outcome recorded
Phase 1/2 NCT05625919 Nov 2022 → Nov 2024 neoplasm with perivascular epithelioid cell differentiation CSPC ZhongQi Pharmaceutical Technology Co., Ltd. Unknown No outcome recorded
Phase 1/2 NCT05920512 Apr 2022 → Apr 2025 hemophilia Xue-chun Lu Unknown No outcome recorded
Phase 2156 trials
Phase 2 NCT06308445 Sep 2026 → Sep 2030 expected classic familial adenomatous polyposis University Hospital, Toulouse Not yet recruiting No outcome recorded
Phase 2 NCT07684287 Aug 2026 → Nov 2027 expected epithelioid hemangioendothelioma CSPC ZhongQi Pharmaceutical Technology Co., Ltd. Not yet recruiting No outcome recorded
Phase 2 NCT07436611 Aug 2026 → Oct 2027 expected capillary malformation AFT Pharmaceuticals, Ltd. Not yet recruiting No outcome recorded
Phase 2 NCT07634120 Jun 2026 → Jun 2027 expected cerebrovascular disorder Huashan Hospital Not yet recruiting No outcome recorded
Phase 2 NCT07124078 May 2026 → Jan 2029 expected chronic graft versus host disease Incyte Corporation Recruiting No outcome recorded
Phase 2 NCT07587801 May → Jul 2026 overdue Central Adelaide Local Health Network Incorporated Not yet recruiting No outcome recorded
Phase 2 NCT07081763 May 2026 → May 2029 expected HIV infectious disease ANRS, Emerging Infectious Diseases Not yet recruiting No outcome recorded
Phase 2 NCT07552077 Apr 2026 → Aug 2027 expected angiokeratoma Palvella Therapeutics, Inc. Recruiting No outcome recorded
Phase 2 NCT05237687 Mar 2026 → Nov 2027 expected Irina Timofte Recruiting No outcome recorded
Phase 2 NCT07131644 Sep 2025 → Sep 2027 expected kaposiform hemangioendothelioma West China Hospital Not yet recruiting No outcome recorded
Show all 156 trials opens the full record — a long page
Phase 2/324 trials
Phase 2/3 NCT07656909 Jun 2026 → Dec 2027 expected Kasabach-Merritt syndrome, kaposiform hemangioendothelioma Yi Ji Recruiting No outcome recorded
Phase 2/3 NCT07657793 Jun 2026 → Sep 2027 expected autoimmune thrombocytopenia, systemic lupus erythematosus Chinese SLE Treatment And Research Group Recruiting No outcome recorded
Phase 2/3 NCT07359807 Apr 2026 → Dec 2027 expected peripheral arterial disease Concept Medical Inc. Not yet recruiting No outcome recorded
Phase 2/3 NCT07165886 Aug 2025 → Aug 2028 expected digestive system neuroendocrine neoplasm CSPC ZhongQi Pharmaceutical Technology Co., Ltd. Recruiting No outcome recorded
Phase 2/3 NCT07092618 Dec 2024 → Aug 2025 overdue AgelessRx Recruiting No outcome recorded
Phase 2/3 NCT06673290 Nov 2024 → Dec 2026 expected lymphatic malformation West China Hospital Recruiting No outcome recorded
Phase 2/3 NCT04892212 Jun 2021 → Jun 2023 lupus nephritis Peking Union Medical College Hospital Unknown No outcome recorded
Phase 2/3 NCT04987463 May 2021 → Mar 2026 tuberous sclerosis Katarzyna Kotulska Unknown No outcome recorded
Phase 2/3 NCT06341998 Jun 2020 → Jan 2024 yolk sac tumor Shandong First Medical University Completed No outcome recorded
Phase 2/3 NCT03826628 Jul 2019 → Sep 2022 tuberous sclerosis, vascular neoplasm Dermatology Specialties Limited Partnership Completed No outcome recorded
Phase 347 trials
Phase 3 NCT07475546 Jul 2025 → Apr 2026 overdue AgelessRx Active not recruiting No outcome recorded
Phase 3 NCT06960928 Apr 2025 → Dec 2026 expected long COVID-19 Icahn School of Medicine at Mount Sinai Recruiting No outcome recorded
Phase 3 NCT06929325 Apr 2025 → Oct 2026 expected hormone receptor-positive breast cancer CSPC ZhongQi Pharmaceutical Technology Co., Ltd. Not yet recruiting No outcome recorded
Phase 3 NCT06239480 Jul 2024 → Jan 2026 overdue microcystic lymphatic malformation Palvella Therapeutics, Inc. Active not recruiting No outcome recorded
Phase 3 NCT05860881 Feb 2024 → Sep 2027 expected disease related to solid organ transplantation, skin cancer Melanoma and Skin Cancer Trials Limited Active not recruiting No outcome recorded
Phase 3 NCT05643872 Nov 2022 → Oct 2023 overdue pachyonychia congenita Palvella Therapeutics, Inc. Recruiting No outcome recorded
Phase 3 NCT05425056 Aug 2022 → Mar 2025 chronic renal failure syndrome, end stage renal failure Vascular Therapies, Inc. Completed No outcome recorded
Phase 3 NCT05495425 Jun 2022 → Oct 2024 tuberous sclerosis Nobelpharma Completed No outcome recorded
Phase 3 NCT05549167 May 2022 → Sep 2029 expected juvenile nasopharyngeal angiofibroma Federal Research Institute of Pediatric Hematology, Oncology and Immunology Recruiting No outcome recorded
Phase 3 NCT04582136 Mar 2021 → Apr 2025 overdue systemic lupus erythematosus Chinese SLE Treatment And Research Group Active not recruiting No outcome recorded
Phase 463 trials
Phase 4 NCT06722586 Jan 2025 → Dec 2027 expected antiphospholipid syndrome, thrombocytopenia Peking University First Hospital Recruiting No outcome recorded
Phase 4 NCT06236022 Jan 2024 → Dec 2028 expected dilated cardiomyopathy, human herpesvirus 8 infection Tongji Hospital Recruiting No outcome recorded
Phase 4 NCT05193565 Nov 2021 → Jul 2026 overdue Chong Kun Dang Pharmaceutical Active not recruiting No outcome recorded
Phase 4 NCT04921722 Oct 2021 → Nov 2025 kaposiform hemangioendothelioma, lymphatic malformation, tufted angioma Children's Hospital of Fudan University Unknown No outcome recorded
Phase 4 NCT04700709 Jan 2021 → Dec 2024 Chong Kun Dang Pharmaceutical Unknown No outcome recorded
Phase 4 NCT04448873 Jul 2020 → Feb 2023 Kasabach-Merritt syndrome, kaposiform hemangioendothelioma Children's Hospital of Fudan University Completed No outcome recorded
Phase 4 NCT04470804 Jul 2020 → Jul 2022 primary acquired red cell aplasia Bing Han Completed No outcome recorded
Phase 4 NCT04406870 Jul 2020 → Jun 2024 hemangioendothelioma Shanghai Children's Medical Center Unknown No outcome recorded
Phase 4 NCT04324411 Apr 2020 → May 2023 autoimmune disease Peking Union Medical College Hospital Withdrawn No outcome recorded
Phase 4 NCT04177095 Feb 2020 → Sep 2021 transplant rejection Massachusetts General Hospital Completed No outcome recorded
Phase not applicable31 trials
NCT07518277 Apr 2026 → Apr 2028 expected autoimmune hemolytic anemia, warm type Chen Miao Not yet recruiting No outcome recorded
NCT07151157 Aug 2025 → Apr 2026 overdue adult-onset Still disease Ruijin Hospital Active not recruiting No outcome recorded
NCT06981845 Jun 2025 → Jun 2028 expected coronary restenosis China National Center for Cardiovascular Diseases Not yet recruiting No outcome recorded
NCT07033858 Mar 2025 → Mar 2026 overdue Shahid Beheshti University of Medical Sciences Recruiting No outcome recorded
NCT06856200 Feb → Oct 2025 overdue Her2-receptor negative breast cancer, hormone-resistant breast carcinoma Fudan University Recruiting No outcome recorded
NCT06618248 Dec 2023 → Sep 2025 overdue coronary artery disorder Dongguan TT Medical Recruiting No outcome recorded
NCT05925023 Jun 2023 → Dec 2025 overdue autoimmune hemolytic anemia, warm type Peking Union Medical College Hospital Recruiting No outcome recorded
NCT05746689 Mar 2023 → Dec 2026 expected immunoglobulin G4-related sclerosing disease Peking University International Hospital Not yet recruiting No outcome recorded
NCT04374903 Apr 2022 King Hussein Cancer Center Withdrawn No outcome recorded
NCT05233722 Feb 2022 → Jun 2029 expected University of Copenhagen Recruiting No outcome recorded
Phase not stated1 trial
NCT07689942 classic familial adenomatous polyposis Biodexa Pharmaceuticals Available No outcome recorded
Also used as a comparator or background therapy in 216 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 05 trials
Phase 0 NCT04608448 Comparator Apr 2021 → Apr 2022 The University of Texas Health Science Center at San Antonio Completed No outcome recorded
Phase 0 NCT03910452 Background Oct 2019 → Jun 2034 expected chronic granulomatous disease National Institute of Allergy and Infectious Diseases (NIAID) Active not recruiting No outcome recorded
Phase 0 NCT03421756 Background Mar → Sep 2018 sickle cell disease Kathleen Dorritie Terminated No outcome recorded
Phase 0 NCT02753309 Comparator Jun 2016 → Dec 2019 urinary bladder cancer The University of Texas Health Science Center at San Antonio Completed No outcome recorded
Phase 0 NCT00426517 Background Jan 2007 → Nov 2019 immunodeficiency disease National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 136 trials
Phase 1 NCT07162038 Background Nov 2025 → Nov 2030 expected hematopoietic and lymphoid cell neoplasm National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 1 NCT06287944 Background Jul 2025 → May 2028 expected acute lymphoblastic leukemia, acute myeloid leukemia, myelodysplastic syndrome City of Hope Medical Center Recruiting No outcome recorded
Phase 1 NCT07015684 Background Apr 2025 → Mar 2030 expected sickle cell disease Columbia University Recruiting No outcome recorded
Phase 1 NCT05298358 Background Nov 2022 → Nov 2024 systemic sclerosis Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins Terminated No outcome recorded
Phase 1 NCT05170828 Background Sep 2022 → Mar 2024 T-lymphoblastic lymphoma, acute biphenotypic leukemia, acute undifferentiated leukemia, myelodysplastic syndrome Ossium Health, Inc. Withdrawn No outcome recorded
Phase 1/244 trials
Phase 1/2 NCT06727305 Comparator May 2026 → Sep 2027 expected University of Texas Southwestern Medical Center Recruiting No outcome recorded
Phase 1/2 NCT07052929 Background Dec 2025 → Oct 2027 expected X-linked myotubular myopathy Astellas Gene Therapies Recruiting No outcome recorded
Phase 1/2 NCT04370795 Comparator Nov 2025 severe combined immunodeficiency National Institute of Allergy and Infectious Diseases (NIAID) Withdrawn No outcome recorded
Phase 1/2 NCT07270549 Background Nov 2025 → Dec 2032 expected CTNNB1-related neurodevelopmental disorder and/or vitreoretinopathy CTNNB1 Foundation Recruiting No outcome recorded
Phase 1/2 NCT07113743 Background Sep 2025 → Sep 2028 expected granulomatous disease, chronic, X-linked National Institute of Allergy and Infectious Diseases (NIAID) Enrolling by invitation No outcome recorded
Phase 269 trials
Phase 2 NCT07582172 Background Apr 2027 → Apr 2029 expected acute myeloid leukemia, chronic myelomonocytic leukemia, myelodysplastic syndrome City of Hope Medical Center Not yet recruiting No outcome recorded
Phase 2 NCT07715734 Background Sep 2026 → Mar 2031 expected skin squamous cell carcinoma Washington University School of Medicine Not yet recruiting No outcome recorded
Phase 2 NCT07616154 Background Sep 2026 → Sep 2034 expected sickle cell disease St. Jude Children's Research Hospital Not yet recruiting No outcome recorded
Phase 2 NCT06084780 Background Aug → Dec 2026 expected pseudomyxoma peritonei, retroperitoneal cancer Case Comprehensive Cancer Center Not yet recruiting No outcome recorded
Phase 2 NCT06752694 Background Sep 2025 → Jan 2026 overdue acquired aplastic anemia Fred Hutchinson Cancer Center Active not recruiting No outcome recorded
Phase 2/36 trials
Phase 2/3 NCT07366801 Comparator Sep 2025 → Jun 2027 expected acute lymphoblastic leukemia, acute myeloid leukemia Federal Research Institute of Pediatric Hematology, Oncology and Immunology Recruiting No outcome recorded
Phase 2/3 NCT04948203 Comparator Jul 2021 → Dec 2026 expected long COVID-19, pneumonia, pulmonary fibrosis University of Chicago Active not recruiting No outcome recorded
Phase 2/3 NCT04168944 Background Nov 2019 → Sep 2022 hepatocellular carcinoma RenJi Hospital Unknown No outcome recorded
Phase 2/3 NCT03512756 Background Mar 2018 → Dec 2021 malignant pancreatic neoplasm Tyme, Inc Terminated No outcome recorded
Phase 2/3 NCT01106833 Comparator Apr 2010 → Feb 2017 chronic graft versus host disease Medical College of Wisconsin Completed No outcome recorded
Phase 319 trials
Phase 3 NCT07378657 Comparator Nov 2025 → Nov 2027 expected lymphatic malformation Ain Shams University Recruiting No outcome recorded
Phase 3 NCT06821542 Background Jun 2025 → May 2028 expected chronic graft versus host disease Incyte Corporation Active not recruiting No outcome recorded
Phase 3 NCT03901001 Comparator May 2023 → Oct 2025 influenza Chinese University of Hong Kong Unknown No outcome recorded
Phase 3 NCT04789070 Comparator Jul 2022 → Dec 2027 expected inclusion body myositis University of Kansas Medical Center Active not recruiting No outcome recorded
Phase 3 NCT05180708 Comparator Nov 2021 → Jun 2023 pachyonychia congenita Palvella Therapeutics, Inc. Completed No outcome recorded
Phase 427 trials
Phase 4 NCT07542314 Background Jul 2026 → Mar 2027 expected Duchenne muscular dystrophy Sarepta Therapeutics, Inc. Not yet recruiting No outcome recorded
Phase 4 NCT07426484 Background Jul 2026 → Dec 2030 expected skin squamous cell carcinoma Dana-Farber Cancer Institute Not yet recruiting No outcome recorded
Phase 4 NCT04077515 Comparator May 2019 → Dec 2022 hemangioma, kaposiform hemangioendothelioma Children's Hospital of Fudan University Completed No outcome recorded
Phase 4 NCT02671318 Comparator Sep 2015 → Dec 2019 cytomegalovirus infection Hospital do Rim e Hipertensão Unknown No outcome recorded
Phase 4 NCT02062892 Comparator Dec 2013 → Jun 2014 University of Colorado, Denver Withdrawn No outcome recorded
Phase not applicable8 trials
NCT01976390 Comparator Oct 2013 → Jul 2018 kidney failure Ohio State University Completed No outcome recorded
NCT01850108 Background May 2013 → Nov 2023 sickle cell disease Vanderbilt-Ingram Cancer Center Unknown No outcome recorded
NCT01649609 Comparator Mar 2012 → Dec 2016 BK-virus nephropathy Columbia University Completed No outcome recorded
NCT01005706 Comparator Aug 2009 → Jul 2013 renal agenesis Medical University of South Carolina Completed No outcome recorded
NCT00934791 Comparator Feb 2009 → Dec 2012 autosomal dominant polycystic liver disease Mayo Clinic Terminated No outcome recorded
Phase not stated2 trials
NCT01309022 Background type 1 diabetes mellitus National Institute of Allergy and Infectious Diseases (NIAID) No longer available No outcome recorded
NCT01049633 Background type 1 diabetes mellitus National Institute of Allergy and Infectious Diseases (NIAID) No longer available No outcome recorded

Press releases naming this drug 3 releases

DateIssuerRelease
2015-05-29 Pfizer Pfizer’s RAPAMUNE® (sirolimus) Becomes First FDA-Approved Treatment for Lymphangioleiomyomatosis (LAM), A Rare Progressive Lung Disease pfizer.com
2015-02-20 Pfizer FDA Accepts Supplemental New Drug Application for Priority Review of RAPAMUNE® (sirolimus) for Treatment of Lymphangioleiomyomatosis (LAM) pfizer.com
2011-08-03 Pfizer Biotica regains worldwide rights to its rapamycin analogue program pfizer.com

Evidence & citations 36 cited values

Every value below carries the sentence it was read from. 718 sources stand behind the page.

FieldValueCited text
Known as sirolimus “The development of LAM-001 for lung transplant related BOS, conceptually a T-cell driven process against transplanted alloantigen, is based on the principal hypothesis that...” NCT06018766
579

“The BAT in this study was identified by the investigator prior to patient randomization among the following treatments currently used in this setting: anti-thymocyte globulin...” NCT02913261

“The BAT in this study will freely be identified by the Investigator prior to patient randomization and may include treatments such as: anti-thymocyte globulin (ATG),...” NCT04118556

“Patients will receive the recommended phase 2 dose (RP2D) of SM-88 (460 mg by mouth [PO] twice a day [BID] D1 - 28) as well as three conditioning agents (MPS): methoxsalen (10...” NCT04720664

“High-dose, post-transplantation cyclophosphamide (PTCy) 25-50 mg/kg on days +3 and +4, sirolimus 6 mg on days +5 through +90, and mycophenolate mofetil (MMF) on days +5 through...” NCT02579967

“The trial evaluates the safety and efficacy of the Magic Touch PTA sirolimus drug-coated balloon in comparison to the treatment with PTX drug-coated balloon (control device) in...” NCT04475783

“Stepwise reduction in the dose, and ultimate discontinuation of, all non-belatacept immunosuppression (mycophenolate, sirolimus, everolimus, prednisone) guided by monitoring of...” NCT04177095

“The purpose of this study is to evaluate the side effects of sirolimus (rapamycin) given in combination with chemotherapy (Mitoxantrone + Etoposide + Cytarabine (MEC)) on high...” NCT00780104

“LUMINA Phase III Study Assessing the Efficacy and Safety of Intravitreal Injections of 440 ug DE-109 Sirolimus for the Treatment of Active, Non-Infectious Uveitis of the...” NCT03711929

Sirolimus 0.2 mg/kg loading dose, then 0.1 mg/kg p.o. daily adjusted to reach target trough levels of 10-15 ng/ml during the first 3 months post transplant and 7-10 ng/ml thereafter” NCT00679042

“The PK sub-study is being conducted to assess the blood pharmacokinetics of the three drugs (Sirolimus, Rivaroxaban, Argatroban) eluted from the DESyne BDS Plus after implantation.” NCT05033964

Sirolimus (INN/USAN), also known as rapamycin, is an immunosuppressant drug used to prevent rejection in organ transplantation; it is especially useful in kidney transplants.” NCT01889992

“The biodegradable polymer sirolimus eluting Combo stent is a dual-therapy sirolimus-eluting and CD34+ antibody coated stent capturing endothelial progenitor cells (EPCs).” PMID 39870125 Jan 2025

Sirolimus gel, 0.2%, demonstrated a significant clinical benefit for patients with TSC involving angiofibromas, thus providing a promising therapeutic modality.” PMID 29800026 Jul 2018

“Rapamycin (sirolimus) is a drug that targets the mTOR (mammalian target of rapamycin) protein involved in the PI3K-Akt signalling pathway downstream of PI3K.” NCT06308445

Sirolimus: given as an initial loading dose of 12 mg p.o. on day -3 pre-transplant, 4 mg starting day -2 pre-transplant and titrated for levels 3-12 ng/ml” NCT00520130

“This new formulation, encapsulated rapamycin (sirolimus), provides a more predictable bioavailability of this drug than \[the other formulation\].” NCT03618355

Sirolimus at least 7-10 days prior to receiving the first dose of cemiplimab (Cycle 1, Day 1) and then daily while receiving Cemiplimab” NCT04339062

“A Post Marketing Surveillance Looking at Safety of Rapamune (Sirolimus) in Indian Population Undergoing de Novo Renal Transplantation.” NCT00195481

“Racemetyrosine (SM-88) is an amino-acid analogue used with methoxsalen, phenytoin, and sirolimus (MPS) to enhance SM-88 activity.” PMID 32924093 Sep 2020

“ABI-009 is a nanoparticle albumin-bound (nab®) formulation of the mammalian Target of Rapamycin ( mTOR) inhibitor, sirolimus.” NCT02009332

“Assigned Interventions Sirolimus (Rapamune) Tacrolimus (Prograft) Prednisone (Deltasone, Prednicot, Rayos, Sterapred)” NCT04415476

Sirolimus orally, monitored two times a week to maintain a target therapeutic plasma level of 8-15 ng/ml from day +5.” NCT03434704

Sirolimus will be used for GVHD prophylaxis and given for 9 months post-transplant and then tapered off by one year” NCT02165007

“Subject will be randomized to take Sirolimus (Rapamycin) 0.5mg once daily for 2 years or until disease recurrence” NCT03298958

“Sodium valproate extended-release tablets 0.5g/day; sirolimus tablets 1mg/day and calcitriol capsules 0.25μg/day.” NCT05920512

“such as Etanercept and infliximab, pentostatin, sirolimus, mycophenolate mofetil and extracorporeal photopheresis” NCT02694770

“take oral Sirolimus (1 mg/m2/day) for 7 days (from 3 days before UCB infusion until 3 days after UCB infusion)” NCT03871972

Sirolimus: Start at 5 mg/day as soon as treatment allocation arrives to obtain targeting levels to 8 -15 ng/ml” NCT01195194

“Immunosuppressive regimen consisting of calcineurin inhibitor, mycophenolate mofetil, sirolimus or ivermus” NCT04168944

“Subjects will receive either Hydroxychloroquine with Azithromycin or Hydroxychloroquine with SirolimusNCT04374903

“Evaluate the tolerability and efficacy of sirolimus (rapamycin) in combination with low-dose aracytin” NCT00235560

“test two of these drugs, Rapamycin (Sirolimus) and Everolimus (Afinitor), in healthy older adults” NCT06658093

“Postgrafting immunosuppression with mycophenolate mofetil (15 mg/kg TID) and sirolimus (2 mg QD)” NCT01582048

“the combination of the drugs daclizumab and sirolimus can effectively treat adults with uveitis” NCT00078689

“Study Evaluating Sirolimus in End Stage Renal Disease in High Risk Kidney Transplant Recipients” NCT00044720

“Intravitreal injections of sirolimus 440mcg/20mcL at baseline and months 1, 2, 3, 4, and 5.” NCT01280669

“The patients also receive rabbit Antithymocyte Globulin (rATG), tacrolimus, and sirolimus.” NCT02166177

“Safety Evaluation of Panitumumab and Sirolimus in Advanced Non-Small Cell Lung Cancer” NCT00352950

Sirolimus: 12 mg PO on days -3 to 60, followed by a taper if GVHD does not develop.” NCT02356159

“• A mammalian target of rapamycin (mTOR) inhibitor (everolimus or sirolimus)” NCT06821542

“• A mammalian target of rapamycin (mTOR) inhibitor (everolimus or sirolimus)” NCT07124078

Sirolimus (rapamycin, Rapamune , RAPA) is a novel immunosuppressive agent” NCT00061360

“an immunotherapy called SEL-110, a nano-encapsulated form of sirolimus.” NCT05778877

“The study allowed SOC regimen is tacrolimus + sirolimus or everolimus.” NCT06552169

Sirolimus 8mg-12mg oral loading dose followed by single dose 4mg/day.” NCT02991898

Sirolimus is an inhibitor of the mammalian target of rapamycin (mTOR)” NCT02776202

“mTOR inhibitors (everolimus or sirolimus), vedolizumab, ruxolitinib.” NCT05132166

“Participants will receive sirolimus orally (3 mg/day) for 6 months.” NCT02554955

“Rapamycin (Sirolimus) Treatment for Amyotrophic Lateral Sclerosis” NCT03359538

“mycophenolate mofetil (MMF) and tacrolimus converted to sirolimusNCT00619528

Sirolimus: Starting dose 1 mg/d, orally, once a day.” NCT07518277

“Rapamune® (sirolimus) 2 mg tablet for oral dosing.” NCT03972462

sirolimus po trough levels 10-15 ng/ml X 3 months” NCT00566813

Sirolimus may be substituted for tacrolimus.” NCT05298358

“NPC-12G gel is containing 0.2% SirolimusNCT04461886

“NPC-12Y gel is containing 0.2% SirolimusNCT05495425

“NPC-12G gel is containing 0.2% SirolimusNCT02634931

Sirolimus, MMF, Mycophenolate Mofetil” NCT01062555

“PTX-022 (Sirolimus) Topical Gel 3.9%” NCT06653842

Sirolimus 3.9% Topical Gel (PTX-022)” NCT05050149

“PTX-022 (Sirolimus) Topical Gel 3.9%” NCT07552077

“QTORIN 3.9 % Sirolimus Topical Gel” NCT04893486

“advagrf+sirolimus one time to eat.” NCT01964014

“plus 1 mg of sirolimus/rapamycin” NCT01031901

Sirolimus on days +5 through +60” NCT03922724

“Rapamune, sirolimus, rapamycin” NCT01843998

“prednisone + sirolimusNCT06981845

“Rapamycin (sirolimus)” NCT00375245

Sirolimus (Rapamune®)” NCT01680952

Sirolimus (Rapamune)” NCT00252655

“rapamune (Sirolimus)” NCT01005706

Sirolimus, RAPA” NCT04629495

SirolimusNCT02165007

SirolimusNCT01889992

NCT02449564

NCT03018223

NCT01266057

NCT03587272

NCT00957320

NCT00141804

NCT01303965

NCT01027000

NCT01087983

NCT00478608

NCT00388362

NCT06022068

NCT00672204

NCT01318915

NCT04348292

NCT04473911

NCT01163357

NCT07542314

NCT07587801

NCT05549167

NCT00038948

NCT00672243

NCT05324384

NCT06752694

NCT00374647

NCT00355862

NCT03942926

NCT02517918

NCT05088356

NCT01038505

NCT02629120

NCT00768729

NCT03866681

NCT03016715

NCT05193565

NCT01791088

NCT01428973

NCT07715734

NCT00866879

NCT00183248

NCT05327023

NCT00426517

NCT03589976

NCT03292861

NCT04470804

NCT06843811

NCT01625351

NCT00195273

NCT06145282

NCT04469530

NCT05805605

NCT00089037

NCT04177004

NCT00195429

NCT01522820

NCT00140543

NCT01195922

NCT01363752

NCT00014911

NCT00977691

NCT03952637

NCT03421756

NCT02117596

NCT00811915

NCT00556933

NCT00812123

NCT00866684

NCT02753309

NCT02357342

NCT00821080

NCT06799195

NCT04959175

NCT00602693

NCT04789070

NCT00489281

NCT02917096

NCT01305395

NCT04341675

NCT04172922

NCT03188068

NCT06341998

NCT00037531

NCT02513303

NCT00670423

NCT02833506

NCT05860881

NCT01754389

NCT01699360

NCT04772300

NCT05746689

NCT04128722

NCT03112603

NCT04461340

NCT03583307

NCT01797315

NCT00328770

NCT05125523

NCT07366801

NCT01453140

NCT00428064

NCT07081763

NCT03192397

NCT00275522

NCT01958190

NCT02756572

NCT00999258

NCT00166712

NCT01675947

NCT01649609

NCT03582878

NCT07165886

NCT00061568

NCT01116232

NCT00275535

NCT02688881

NCT00166816

NCT06287944

NCT01592253

NCT03877809

NCT00577278

NCT00766649

NCT01120028

NCT00166829

NCT07684287

NCT04362293

NCT04047576

NCT07270549

NCT01842594

NCT00565773

NCT00499486

NCT00995059

NCT05925023

NCT00396721

NCT02296749

NCT02296762

NCT00457808

NCT04775173

NCT02979873

NCT02428296

NCT00062712

NCT00098462

NCT04339101

NCT00040508

NCT00369382

NCT00876434

NCT00612274

NCT03099356

NCT01843998

NCT07359807

NCT00518271

NCT03933904

NCT01492894

NCT06802055

NCT07582172

NCT01134952

NCT00766337

NCT02565901

NCT01383668

NCT00144677

NCT00634244

NCT01537107

NCT03878524

NCT02686619

NCT03468478

NCT05663944

NCT02145559

NCT06618248

NCT00634270

NCT00144703

NCT02487485

NCT00368914

NCT00005113

NCT04936854

NCT00518375

NCT04892212

NCT00507793

NCT03242096

NCT02524639

NCT04127578

NCT07634120

NCT00166842

NCT01162551

NCT00908466

NCT05384756

NCT07581704

NCT00223028

NCT00137345

NCT01802268

NCT03121001

NCT02509468

NCT03047980

NCT04077515

NCT04247750

NCT05949658

NCT01166724

NCT01087554

NCT00455013

NCT00519116

NCT06856200

NCT00896012

NCT06325709

NCT03688191

NCT00167947

NCT04448873

NCT04700709

NCT01595841

NCT05036226

NCT02588339

NCT07131644

NCT01446484

NCT01888302

NCT00513474

NCT04736953

NCT01265030

NCT00814944

NCT04161144

NCT05625919

NCT00922129

NCT00993499

NCT04370795

NCT02766465

NCT01962896

NCT06091332

NCT05386914

NCT05425056

NCT00555373

NCT01462006

NCT04371640

NCT00713284

NCT03970096

NCT03246906

NCT00993343

NCT00305396

NCT00490789

NCT05508620

NCT00305682

NCT03910452

NCT01488253

NCT06876142

NCT04083183

NCT00464555

NCT05426252

NCT03531281

NCT01499888

NCT02683291

NCT01850108

NCT00254709

NCT04707209

NCT02821507

NCT00406393

NCT01885689

NCT01313923

NCT00975819

NCT01061853

NCT02821026

NCT05414292

NCT00068302

NCT06261060

NCT01445548

NCT01223755

NCT00544115

NCT02960997

NCT01231412

NCT03972592

NCT00452361

NCT01680250

NCT02042326

NCT07241936

NCT00266123

NCT01737502

NCT03077542

NCT00895583

NCT03150914

NCT05463133

NCT06929325

NCT02638389

NCT00189202

NCT00050713

NCT01927120

NCT01217125

NCT01135563

NCT02208791

NCT00973804

NCT00433485

NCT03225417

NCT00146614

NCT02105766

NCT01331135

NCT06673290

NCT00604357

NCT02678143

NCT02528877

NCT01251575

NCT03072485

NCT00554125

NCT03778996

NCT07162038

NCT03456700

NCT01938573

NCT02711202

NCT01620307

NCT00491517

NCT07426484

NCT03500848

NCT00450320

NCT00681213

NCT01709136

NCT01689987

NCT00118742

NCT00656643

NCT00382109

NCT05237687

NCT00346151

NCT00392951

NCT02990312

NCT06358638

NCT00321906

NCT03304678

NCT01034345

NCT02574728

NCT04094675

NCT03095703

NCT00086346

NCT02008877

NCT04861064

NCT00548717

NCT07378657

NCT03253913

NCT03504241

NCT01049633

NCT07151157

NCT02123966

NCT00409461

NCT01536054

NCT06236022

NCT06084780

NCT05170828

NCT00434811

NCT00552669

NCT04921722

NCT00133367

NCT00940381

NCT00434850

NCT01184885

NCT05840510

NCT00743509

NCT01632605

NCT04324411

NCT04598815

NCT02806947

NCT07616154

NCT00095329

NCT00890500

NCT00346918

NCT02732899

NCT02214706

NCT01670175

NCT06055608

NCT07656909

NCT01713400

NCT00076570

NCT00319878

NCT05436418

NCT00188955

NCT00170053

NCT02867800

NCT01534143

NCT03667313

NCT00589563

NCT00473551

NCT01658007

NCT00023244

NCT03987152

NCT06960928

NCT00446264

NCT02062944

NCT02062892

NCT00121810

NCT02891603

NCT00092222

NCT01809860

NCT00240994

NCT02110069

NCT01220297

NCT00859183

NCT00621101

NCT06504420

NCT06959771

NCT01184898

NCT00282217

NCT00789308

NCT00023231

NCT07015684

NCT06940895

NCT07657793

NCT00105001

NCT02061397

NCT00350181

NCT00282282

NCT01379209

NCT06941142

NCT02055079

NCT00971789

NCT03983850

NCT02282904

NCT01517074

NCT05104983

NCT00311311

NCT05458492

NCT01822015

NCT06719791

NCT03605927

NCT02671318

NCT06080165

NCT07113743

NCT00468442

NCT04582136

NCT06727305

NCT01181271

NCT00261820

NCT04141020

NCT00928018

NCT05357482

NCT03365869

NCT07052929

NCT00043979

NCT00792948

NCT01203722

NCT03214354

NCT00317798

NCT02013375

NCT00078559

NCT01811667

NCT02365415

NCT01869114

NCT06078696

NCT00934791

NCT03660930

NCT00493194

NCT03901001

NCT00352092

NCT06957379

NCT00317785

NCT05896839

NCT00129961

NCT03364764

NCT00509613

NCT04115800

NCT06722586

NCT02177760

NCT00079183

NCT00509431

NCT01976390

NCT00006178

NCT00693446

NCT00923845

NCT00711490

NCT02423915

NCT00358657

NCT02728700

NCT04948203

NCT02126527

NCT00002790

NCT04411654

NCT04393454

NCT00352976

NCT05269849

NCT00923273

NCT01764607

NCT01309022

NCT07667413

NCT01374750

NCT03433183

NCT00931255

NCT02583893

NCT00353301

NCT01687179

NCT04888741

NCT06872333

NCT02443818

NCT00790439

NCT02793544

NCT01814059

NCT02722668

NCT01106833

NCT01929642

NCT02152007

NCT07662174

NCT01054313

NCT06279494

NCT03217669

NCT03512756

NCT04409691

NCT00204321

NCT03662412

NCT02584647

NCT00712491

NCT01236378

NCT00414648

NCT00506948

NCT03363763

NCT04408625

NCT02440789

NCT02790515

NCT04406870

Known as (RAPA, RapamuneR) (sirolimus) (RAPA, RapamuneR) (sirolimus)NCT00795886
Known as ABI-009 ABI-009 is a nanoparticle albumin-bound (nab®) formulation of the mammalian Target of Rapamycin ( mTOR) inhibitor, sirolimus.” NCT02009332
Known as DE-109 “LUMINA Phase III Study Assessing the Efficacy and Safety of Intravitreal Injections of 440 ug DE-109 Sirolimus for the Treatment of Active, Non-Infectious Uveitis of the...” NCT03711929
2

NCT01358266

NCT02251938

Known as Encapsulated Rapamycin “The eRapa (encapsulated rapamycin) drug product consists of sub-micron rapamycin particles incorporated into poly(methyl methacrylate) polymer (Eudragit® L 100 / S 100).” NCT03618355
1

Encapsulated Rapamycin (eRapa)” NCT04230499

Known as eRapa “The eRapa (encapsulated rapamycin) drug product consists of sub-micron rapamycin particles incorporated into poly(methyl methacrylate) polymer (Eudragit® L 100 / S 100).” NCT03618355
1

“0.5mg eRapa (encapsulated rapamycin) oral capsules” NCT04375813

Known as MS-R001 ClinicalTrials.gov intervention name — accepted as the source's own label NCT00401115
Known as MS-R001, rapamycin MS-R001, rapamycinNCT00656643
Known as MS-R002, rapamycin MS-R002, rapamycinNCT00656643
Known as MS-R003, rapamycin MS-R003, rapamycinNCT00656643
Known as NPC-12G “The purpose of this trial is to evaluate the safety and efficacy of long-term treatment with NPC-12G gel (0.2% sirolimus gel) to angiofibroma and other skin lesions in patients...” NCT02634931
1

NPC-12G gel (topical formulation of sirolimus)” NCT02635789

Known as PTX-022 “The purpose of this OLT study is to investigate the safety of long term exposure and pharmacokinetics (PK) of QTORIN rapamycin 3.9% anhydrous gel or "PTX-022".” NCT05643872
4

“This study evaluates the safety and efficacy of PTX-022, topical rapamycin, in the treatment of adults with moderate to severe Pachyonychia Congenita.” NCT03920228

“This study evaluates the safety and efficacy of PTX-022 (sirolimus) Topical Gel 3.9% w/w in the treatment of Microcystic Lymphatic Malformations.” NCT05050149

PTX-022 (Sirolimus) Topical Gel 3.9%” NCT06653842

PTX-022 (Sirolimus) Topical Gel 3.9%” NCT07552077

Known as QTORIN “A Multicenter, Phase 3 Randomized, Double-Blind, Vehicle-Controlled Study Evaluating the Safety and Efficacy of QTORIN 3.9% Rapamycin Anhydrous Gel in the Treatment of...” NCT05180708
1

QTORIN 3.9% Rapamycin Anhydrous Gel” NCT06239480

Known as QTORIN Sirolimus “Study Evaluating the Safety and Efficacy of PTX-022 (QTORIN Sirolimus) in the Treatment of Microcystic Lymphatic Malformations” NCT05050149
Known as Rap “the mTOR inhibitor sirolimus (Rap) found that administering the drug” NCT06719791
Known as RAPA “Evaluation of central nervous system penetration of orally administered Rapamune (RAPA) in older adults with Mild Cognitive Impairment (MCI) or early Alzheimer's disease (AD)...” NCT04200911
7

“Inhibition of the mTOR pathway by rapamycin (RAPA), an immunosuppressive drug used as adjunct therapy in preventing solid organ allograft rejection, enhances longevity in mice.” NCT02874924

“the autophagy inhibitor: hydroxychloroquine (HCQ) and the autophagy inducer: sirolimus (rapamycin, Rapa) would reduce glucose utilization in sarcoma patients.” PMID 26375670 Oct 2015

rapamycin (RAPA), a key component of the immunosuppressive regimen in clinical islet transplantation” PMID 21084848 Jul 2009

“daily 0.5-1.0 ml applications of 8% RAPA (Rapamycin) in a petrolatum vehicle” NCT04049552

“Sirolimus (rapamycin, Rapamune , RAPA) is a novel immunosuppressive agent” NCT00061360

Rapamycin (RAPA)” NCT00803010

“Sirolimus, RAPANCT04629495

Known as rapamun “Sirolimus (rapamun) is an mTOR inhibitor” NCT05549167
Known as Rapamune “Trial of Continuous Once Daily Oral Treatment Using BIBW 2992 (Afatinib) Plus Sirolimus (Rapamune®) in Patients With Non-small Cell Lung Cancer Harbouring an EGFR Mutation...” NCT00993499
41

“At 1 month, they will have a kidney biopsy and if it is ok, patients will be treated long term with either continued tacrolimus/mycophenolate mofetil or be switched to...” NCT00170053

“Study to Compare the Safety and Efficacy of Sirolimus (Rapamune) to Tacrolimus (Advagraf) Associated to Mycophenolate Mofetil (CellCept) Between 12 and 36 Months After Kidney...” NCT00811915

“In detail: Tacrolimus (Prograf or FDA approved generic 0.5 mg, 1 mg or 5 mg capsules, once a day) in combination with Sirolimus (Rapamune, 0.5, 1, and 2mg tablets).” NCT02062892

“A Post Marketing Surveillance Looking at Safety of Rapamune (Sirolimus) in Indian Population Undergoing de Novo Renal Transplantation.” NCT00195481

“Sirolimus (Rapamune ) for Relapse Prevention in People With Severe Aplastic Anemia Responsive to Immunosuppressive Therapy” NCT02979873

“A Phase I/II, Open-Label Pilot Trial to Evaluate the Safety of Rapamune (Sirolimus) in Patients With Multiple Sclerosis” NCT00095329

“These newer medications include Prograf (tacrolimus), Cellcept (mycophenolate mofetil), and Rapamune (sirolimus).” NCT00352092

“A Phase I/II Trial of Sirolimus (Rapamune) and Cyclosporine in Patients With Refractory Aplastic Anemia” NCT00319878

“Sirolimus (rapamycin, Rapamune , RAPA) is a novel immunosuppressive agent” NCT00061360

“Sirolimus (Rapamune 2mg/day, Pfizer) or not for a course of 14 days.” NCT01620307

“Mycophenolate Mofetil; MMF (CellCept) and Sirolimus (Rapamune)” NCT00374647

“Sirolimus (RAPAMUNE) drug-coated balloon angioplasty catheter” NCT07359807

“CellCept® (Mycophenolate mofetil) OR Rapamune® (Sirolimus)” NCT00789308

Rapamune® (sirolimus) 2 mg tablet for oral dosing.” NCT03972462

“induction therapy with CsA and RapamuneNCT00195468

“Sirolimus (rapamycin, Rapamune)” NCT00743509

Rapamune, sirolimus, rapamycin” NCT01843998

Rapamune (sirolimus/rapamycin)” NCT00896012

“TOPICAL SIROLIMUS (RAPAMUNE*)” NCT01061853

“Drug: Rapamune (Sirolimus)” NCT00167947

“Sirolimus (Rapamune®)” NCT07378657

Rapamune® (Sirolimus)” NCT00518271

Rapamune® (rapamycin)” NCT02505893

“Sirolimus (Rapamune®)” NCT01680952

Rapamune® (Sirolimus)” NCT00518375

“Sirolimus (Rapamune®)” NCT00478608

Rapamune® (Sirolimus)” NCT00519116

“Sirolimus (Rapamune®)” NCT07662174

“Sirolimus (Rapamune)” NCT00252655

“Sirolimus (RAPAMUNE)” NCT07656909

“Sirolimus (RAPAMUNE)” NCT07587801

“Sirolimus (Rapamune)” NCT00086346

“Sirolimus (RAPAMUNE)” NCT00037531

NCT07033858

NCT00248313

NCT00337376

NCT04200911

NCT01853423

NCT00286156

NCT01601821

NCT00470665

Known as rapamune (Sirolimus) rapamune (Sirolimus)NCT01005706
Known as Rapamune (sirolimus, rapamycin) Rapamune (sirolimus, rapamycin)NCT01488253
Known as Rapamune [Registered Trademark] “This study will determine the safety and effectiveness of sirolimus (Rapamune® (Registered Trademark)) in treating focal segmental glomerulosclerosis (FSGS), a disease...” NCT00040508
1

“A Phase II Trial of Pemetrexed (Alimta [Registered Trademark]) Combined With Sirolimus (Rapamycin, Rapamune [Registered Trademark]) in Subjects With Relapsed or Refractory NSCLC” NCT00923273

Known as rapamycin “PURPOSE: Pharmacodynamic studies are frequently incorporated into phase I trials, but it is uncommon that they guide dose selection. We conducted a dose selection study with...” PMID 18757332 Sep 2008
155

“BACKGROUND: Perturbation of the mechanistic target of rapamycin (mTOR) pathway can instruct effector versus memory cell fate of tumor antigen-specific T cells in preclinical...” PMID 40132910 Mar 2025

“The purpose of this study is to determine the safety and efficacy of an ocular sirolimus (rapamycin) formulation compared to Placebo on the signs and symptoms of dry eye in the...” NCT00814944

“Sirolimus, also known as rapamycin, is a macrolide compound that inhibits its mechanistic target (mTOR), which regulates cell growth and metabolism in response to environmental cues.” NCT05746689

“A Phase II Trial of Pemetrexed (Alimta [Registered Trademark]) Combined With Sirolimus (Rapamycin, Rapamune [Registered Trademark]) in Subjects With Relapsed or Refractory NSCLC” NCT00923273

“Sirolimus (INN/USAN), also known as rapamycin, is an immunosuppressant drug used to prevent rejection in organ transplantation; it is especially useful in kidney transplants.” NCT01889992

“Sirolimus, also known as rapamycin, is a lipophilic macrolide isolated from a strain of Streptomyces hygroscopicus that serves as a strong HbF inducer in vitro and in vivo.” PMID 35755297 Jun 2022

“Sirolimus, also known as rapamycin, is an immunosuppressant that is used to prevent organ transplant rejection by inhibiting mammalian target of rapamycin (mTOR) kinase.” NCT04461340

“The purpose of this OLT study is to investigate the safety of long term exposure and pharmacokinetics (PK) of QTORIN rapamycin 3.9% anhydrous gel or "PTX-022".” NCT05643872

“the autophagy inhibitor: hydroxychloroquine (HCQ) and the autophagy inducer: sirolimus (rapamycin, Rapa) would reduce glucose utilization in sarcoma patients.” PMID 26375670 Oct 2015

Rapamycin or sirolimus is an anti-inflammatory and immunomodulatory drug that has an enormous potential in ocular surface pathologies such as dry eye disease.” NCT04115800

“This study evaluates the safety and efficacy of PTX-022, topical rapamycin, in the treatment of adults with moderate to severe Pachyonychia Congenita.” NCT03920228

“We examined the effect of the mTOR inhibitor sirolimus (rapamycin) on renal functional loss and cyst progression in the Han:SPRD rat model of ADPKD.” PMID 16221708 Oct 2005

“This will be paired with chronic therapy with Sirolimus (rapamycin, Wyeth-Ayerst), an oral immunosuppressant agent recently approved by the FDA.” NCT00006178

“Sirolimus (rapamycin) is an mTOR inhibitor that promotes α-synuclein autophagy and reduces its associated neurotoxicity in preclinical models.” PMID 35040506 Jan 2022

“The purpose of this research is to see if the drug rapamycin will improve the heart's ability to pump by improving your oxygen consumption.” NCT04996719

“Sirolimus (rapamycin) is an agent produced by the bacterium Streptomyces hygroscopicus, inhibits the mammalian target of rapamycin (mTOR).” NCT03364764

“Sirolimus (rapamycin) is an agent produced by the bacterium Streptomyces hygroscopicus, inhibits the mammalian target of rapamycin (mTOR).” NCT04470804

Rapamycin (as Sirolimus) is an immunosuppressant agent, approved by the FDA for acute rejection prevention in renal transplant recipients.” NCT04247750

“Treatment of port wine stains using Pulsed Dye Laser, Erbium YAG Laser, and topical rapamycin (sirolimus)-A randomized controlled trial.” PMID 27320685 Jun 2016

“Phase II Clinical, Biological and Pharmacological Study of Rapamycin (Rapamune®, Sirolimus) in Patients With Advanced Pancreatic Cancer” NCT00499486

“Sirolimus (rapamycin)-based therapy in human renal transplantation: similar efficacy and different toxicity compared with cyclosporine.” PMID 10221490 Apr 1999

“Sirolimus (rapamycin), produced by the bacterium Streptomyces hygroscopicus, is a mammalian target of Rapamycin (mTOR) inhibitor.” NCT03866681

“This will be combined with sirolimus (rapamycin, Wyeth-Ayerst), an oral immunosuppressant agent recently approved by the FDA.” NCT00062712

“The experimental group received rapamycin 2 mg/day orally for 24 weeks on the basis of methylprednisolone pulse therapy” NCT05532072

“Sirolimus, also known as rapamycin, is currently the only FDA-approved mammalian target of rapamycin (mTOR) inhibitor.” NCT03987152

Rapamycin or sirolimus is a macrocyclic immunosuppressive drug that inhibits the mammalian target of rapamycin (mTOR).” NCT05237687

“Sirolimus (formerly known as Rapamycin) is a drug commonly used after renal transplants to prevent organ rejection.” NCT01313923

“Sirolimus (Rapamycin) is an immunosuppressant mostly used for the management of kidney transplant recipients.” NCT00491517

Rapamycin is given orally, starting at a dose of 1 mg daily beginning on day 1 and terminating on day 30.” NCT00317798

“A PHASE I/II STUDY OF RAPAMYCIN (SIROLIMUS) IN COMBINATION WITH METHOTREXATE (MTX) AND CYCLOSPORINE (CPS)” NCT00002790

“Pre-clinical data suggests that dMMR tumors are susceptible to rapamycin (sirolimus), an mTOR inhibitor.” NCT04393454

“Sirolimus (rapamycin) will be given by mouth (tablet or suspension) once daily throughout the cycle.” NCT01135563

“Infusion with SC-DARIC33 followed by intermittent oral rapamycin administration” NCT05105152

Rapamycin (sirolimus) treatment suppresses mTORC1 but also induces autophagy” PMID 31299246 Jul 2019

“Sirolimus (rapamycin, Rapamune , RAPA) is a novel immunosuppressive agent” NCT00061360

“Oral rapamycin is given as a monotherapy at a initial dose of 0.8mg/m2” NCT04598204

“pre-Tx rapamycin treatment (0.1 mg/kg/day) for at least 30 days” NCT01346085

“Sirolimus (Rapamycin) for Slow-Flow Malformations in Children:” PMID 34524406 Nov 2021

Rapamycin p.o.: 4 mg/d, (target 8-15 ng/ml) (starting day -7)” NCT03963024

“subjects will take a once weekly 6 mg dose of rapamycinNCT04994561

“0.5mg eRapa (encapsulated rapamycin) oral capsules” NCT04375813

“sirolimus (rapamycin; Th2.rapa cells)” NCT00923845

“Pralatrexate Rapamycin Regorafenib” NCT02551718

“Sirolimus (rapamycin, Rapamune)” NCT00743509

“Rapamune, sirolimus, rapamycinNCT01843998

“Rapamune (sirolimus/rapamycin)” NCT00896012

“Sirolimus (Rapamycin)” NCT01054313

“Sirolimus (rapamycin)” NCT00993499

Rapamycin, sirolimus” NCT00457808

“MS-R001 (rapamycin)” NCT00401115

rapamycinNCT01536054

NCT04488601

NCT07436611

NCT00375245

NCT03383380

NCT01526356

NCT02646319

NCT01467986

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NCT02724332

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NCT00780104

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NCT00276744

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NCT01827618

NCT06743503

NCT02240407

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NCT00555256

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NCT07092618

NCT00803010

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NCT00779194

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NCT00874562

NCT03732248

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NCT01060605

NCT00449280

NCT00525889

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NCT00891696

NCT00133887

NCT02675153

NCT00708591

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NCT06563817

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NCT06528301

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NCT04987463

NCT02596828

NCT05342519

NCT00409994

NCT00241189

NCT02803892

NCT07058974

NCT01014234

NCT04742777

NCT05233722

NCT00290069

NCT04230499

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NCT00311623

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NCT02048384

NCT00623012

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NCT00235560

NCT00411788

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NCT00123331

NCT04629495

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NCT02874924

NCT01396200

NCT06239480

NCT03161340

NCT03359538

NCT00776373

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NCT01183247

Known as SEL-110 “an immunotherapy called SEL-110, a nano-encapsulated form of sirolimus.” NCT05778877
Known as SIR “Because sirolimus (SIR) monotherapy was successful in kidney transplantation under antithymocyte globulin (ATG), we undertook a pilot study comparing SIR monotherapy with...” PMID 18212631 Jan 2008
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Sirolimus (SIR) will be administered and dosed according to Moffitt Cancer Center, Department of Blood and Marrow Transplantation standard practice.” NCT02891603

“comparing sirolimus (SIR) with azathioprine (AZA) in a tacrolimus-based immunosuppressive regimen in lung transplantation.” PMID 20833822 Sep 2010

“rapamycin (mTOR) inhibitor sirolimus (SIR) is an immunosuppressant” PMID 25899445 Apr 2015

Known as Siro “BACKGROUND: In an attempt to reduce chronic calcineurin inhibitor induced allograft nephropathy in first cadaver and human leukocyte antigen non-identical living-donor renal...” PMID 14742990 Jan 2004