drugset / Trial / NCT04990388

Safety, Tolerability, and Pharmacokinetics of UX053 in Patients With Glycogen Storage Disease Type III (GSD III)

NCT04990388

Phase 1/2 Terminated 9 enrolled Ultragenyx Pharmaceutical Inc
RandomizedSequentialQuadruple-blindTreatment

Summary

The primary objective of the study is to evaluate the safety of UX053 in adults with Glycogen Storage Disease Type III (GSD III).

Timeline

Start
2021-10-18
Primary completion
2023-03-20
Completion
2023-03-20

Drugs

EvaluationDrugModalityDoseRoute
Subject UX053 Unknown Intravenous
Background Acetaminophen Small molecule Oral
Background Cetirizine Other / unclassified Oral
Background Famotidine Other / unclassified Oral
Background Ibuprofen Small molecule Oral