drugset / Trial / NCT06198842

Low Dose Treosulfan Based Conditioning Regimen and PTCy in HSCT for Nijmegen Breakage Syndrome

NCT06198842

NaSingle-groupOpen-labelTreatment

Summary

The aim of the current study is to evaluate the safety and efficacy of low dose treosulfan based conditioning regimen in HSCT with post-transplant cyclophosphamide in Nijmegen breakage syndrome

Timeline

Start
2023-11-22
Primary completion
2027-01-31
Completion
2029-01-31

Drugs

EvaluationDrugModalityDoseRoute
Subject Treosulfan Small molecule 21 mg/m2