drugset / Trial / NCT06321796

Microbiota Transfer Therapy for Children and Adults With Both Pitt Hopkins Syndrome and Gastrointestinal Disorders

NCT06321796

RandomizedParallel-groupQuadruple-blindTreatment

Summary

The investigators propose to investigate Microbiota Transfer Therapy (MTT) for treating patients with Pitt-Hopkins Syndrome (PTHS) and gastrointestinal problems (constipation, bloating, abdominal pain). MTT involves a combination of 10 days of oral vancomycin (an antibiotic to kill pathogenic bacteria), followed by 1 day of bowel cleanse using magnesium citrate, followed by 4 days of high dose MTP-101P with an antacid, followed by 12 weeks of a lower maintenance dose of MTP-101P with an antacid.

Timeline

Start
2024-02-27
Primary completion
2025-02
Completion
2025-05

Drugs

EvaluationDrugModalityDoseRoute
Subject MTP-101P Other / unclassified
Subject Vancomycin Other / unclassified Oral
Background Aluminum hydroxide Unknown 200 mg
Background Calcium carbonate Other / unclassified
Background Magnesium Citrate Unknown
Background Simethicone Other / unclassified 20 mg
Background magnesium hydroxide Unknown 200 mg

Indications