drugset / Trial / NCT06395285

Evaluating the Safety and Tolerability of Orally Administered DF-003 in ROSAH Syndrome Patients

NCT06395285 ↗

Phase 1 Recruiting 12 enrolled Shanghai Yao Yuan Biotechnology Ltd.
NaSingle-groupOpen-labelTreatment

Summary

The purpose of this study is to evaluate the safety and tolerability of DF-003 in retinal dystrophy, optic nerve edema, splenomegaly, anhidrosis, and migraine headache (ROSAH) syndrome patients.

Timeline

Start
2025-05-27
Primary completion
2026-07
Completion
2026-11

Drugs

EvaluationDrugModalityDoseRoute
Subject DF-003 Small molecule 45 mg Oral