drugset / Trial / NCT07514338

Open Label Extension to Assess Long Term Safety and Efficacy of KL1333 in Patients With Primary Mitochondrial Disease

NCT07514338

Phase 2 Not yet recruiting 140 enrolled Pharming Technologies B.V. ICON plc · collab
NaSingle-groupOpen-labelTreatment

Summary

The purpose of this study is to investigate if the study medicine, KL1333, is safe, well-tolerated and effective long-term in improving the symptoms of fatigue and impacts on daily living and functional capacity (physical abilities) in people with PMD.

Timeline

Start
2026-06-09
Primary completion
2029-03-31
Completion
2029-03-31

Drugs

EvaluationDrugModalityDoseRoute
Subject Napazimone Small molecule 50 mg Oral

Indications