drugset / Trial / NCT07575308

HMBeacon: A Phase 2 Study to Evaluate ALN-6400 in Adult and Adolescent Female Patients With VWD and HMB

NCT07575308 ↗

Phase 2 Not yet recruiting 24 enrolled Alnylam Pharmaceuticals
RandomizedParallel-groupTriple-blindTreatment

Summary

The purpose of this study is to evaluate the safety, tolerability, efficacy, and pharmacodynamics (PD) of multiple doses of ALN-6400 in adult and adolescent patients with VWD and HMB

Timeline

Start
2026-07-31
Primary completion
2027-06-30
Completion
2028-11-29

Drugs

EvaluationDrugModalityDoseRoute
Subject ALN-6400 Unknown — Subcutaneous