Drugs / Mexiletine
last change Apr 2026 re-read 2 minutes ago

Mexiletine

Small molecule

Developed for
myotonic dystrophy · nondystrophic myotonia · ventricular fibrillation · ventricular tachycardia · cardiac arrest · Charcot-Marie-Tooth disease · chronic pain syndrome · diabetic neuropathy
+10 more · dystonic disorder · idiopathic progressive polyneuropathy · irritable bowel syndrome · myotonic syndrome · paramyotonia congenita of Von Eulenburg · peripheral nervous system disorder · sudden cardiac arrest · amyotrophic lateral sclerosis · bulbospinal muscular atrophy · sporadic amyotrophic lateral sclerosis
Investigated by
Lupin Ltd. · National Heart, Lung, and Blood Institute (NHLBI) · Assistance Publique - Hôpitaux de Paris · Boehringer Ingelheim · Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) · First Affiliated Hospital Xi'an Jiaotong University
+13 more · IRCCS Ospedale San Raffaele · Lupin Atlantis Holdings S.A. · Mayo Clinic · National Center for Research Resources (NCRR) · National Institute of Allergy and Infectious Diseases (NIAID) · National Institute of Neurological Disorders and Stroke (NINDS) · Patient-Centered Outcomes Research Institute · Richard Barohn, MD · University of Kansas Medical Center · University of Rochester · University of Tennessee · University of Utah · University of Washington

Regulatory milestones approvals, filings & regulatory actions · 3 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved EU (EMA) Namuscla 2018-12-18 europa.eu
Label expansion US (FDA) MEXITIL 1991-10-21 fda.gov
Approved US (FDA) MEXITIL 1985-12-30 fda.gov

Trials 16 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT01717404 Oct → Nov 2012 irritable bowel syndrome Mayo Clinic Completed No outcome recorded
Phase 25 trials
Phase 2 NCT02561702 Sep 2015 → Dec 2016 Charcot-Marie-Tooth disease University of Rochester Completed No outcome recorded
Phase 2 NCT00832000 Dec 2008 → Mar 2011 nondystrophic myotonia Richard Barohn, MD Completed No outcome recorded
Phase 2 NCT00001784 Jul 1998 → Jul 2002 dystonic disorder National Institute of Neurological Disorders and Stroke (NINDS) Completed No outcome recorded
Phase 2 NCT00383682 Jul 1997 → Apr 2003 chronic pain syndrome Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) Completed No outcome recorded
Phase 2 NCT00000793 ? → Oct 1997 HIV infectious disease, peripheral nervous system disorder National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 36 trials
Phase 3 NCT06549400 Sep 2025 → May 2028 expected myotonic dystrophy Lupin Ltd. Enrolling by invitation No outcome recorded
Phase 3 NCT04624750 Sep 2021 → Jun 2024 myotonic dystrophy Lupin Ltd. Completed No outcome recorded
Phase 3 NCT02336477 Jun 2011 → Jan 2014 nondystrophic myotonia, paramyotonia congenita of Von Eulenburg Assistance Publique - Hôpitaux de Paris Completed No outcome recorded
Phase 3 NCT00004647 Mar 1993 → Feb 1999 diabetic neuropathy National Center for Research Resources (NCRR) Completed No outcome recorded
Phase 3 NCT00000464 Apr 1987 → Dec 1992 cardiac arrest, myocardial infarction, ventricular fibrillation University of Washington Completed No outcome recorded
Phase 3 NCT00000518 Jul 1985 → Dec 1992 sudden cardiac arrest, ventricular fibrillation, ventricular tachycardia University of Utah Completed No outcome recorded
Phase 41 trial
Phase 4 NCT02260388 Oct 2014 → Sep 2017 idiopathic progressive polyneuropathy University of Kansas Medical Center Completed No outcome recorded
Phase not applicable3 trials
NCT06669299 Jun 2025 → Dec 2027 expected ventricular tachycardia IRCCS Ospedale San Raffaele Recruiting No outcome recorded
NCT05619120 Jan 2023 → Jun 2025 First Affiliated Hospital Xi'an Jiaotong University Unknown No outcome recorded
NCT04622553 Nov 2021 → Jan 2026 overdue myotonic syndrome Lupin Ltd. Active not recruiting No outcome recorded
Also used as a comparator or background therapy in 14 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT02308748 Comparator May → Jun 2014 Food and Drug Administration (FDA) Completed No outcome recorded
Phase 24 trials
Phase 2 NCT02781454 Comparator Oct 2016 → Sep 2018 sporadic amyotrophic lateral sclerosis University of Washington Completed No outcome recorded
Phase 2 NCT02045667 Comparator Jan 2014 → Jun 2015 nondystrophic myotonia Radboud University Medical Center Completed No outcome recorded
Phase 2 NCT01849770 Comparator Jul 2013 → Aug 2014 sporadic amyotrophic lateral sclerosis University of Washington Completed No outcome recorded
Phase 2 NCT01406873 Comparator Jun 2011 → Feb 2017 myotonic dystrophy University of Rochester Completed No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT06862596 Comparator Feb 2025 → Dec 2027 expected bulbospinal muscular atrophy Masahisa Katsuno Recruiting No outcome recorded
Phase 34 trials
Phase 3 NCT07097701 Comparator Sep 2025 → Jan 2027 expected myotonic syndrome Lupin Ltd. Recruiting No outcome recorded
Phase 3 NCT06523400 Comparator Feb 2025 → Mar 2026 overdue myotonic dystrophy Lupin Ltd. Recruiting No outcome recorded
Phase 3 NCT04700046 Comparator Sep 2021 → Jul 2024 myotonic dystrophy Lupin Ltd. Withdrawn No outcome recorded
Phase 3 NCT05017155 Comparator Aug 2021 → Aug 2023 nondystrophic myotonia University College, London Unknown No outcome recorded
Phase 43 trials
Phase 4 NCT02114528 Comparator Oct 2014 → Nov 2015 ventricular tachycardia Ottawa Heart Institute Research Corporation Terminated No outcome recorded
Phase 4 NCT01811355 Comparator May 2013 → Mar 2016 amyotrophic lateral sclerosis Bjorn Oskarsson, MD Completed No outcome recorded
Phase 4 NCT00905853 Comparator May 2009 → Dec 2015 ventricular tachycardia John Sapp Completed No outcome recorded
Phase not applicable1 trial
NCT05639257 Comparator Dec 2022 → Apr 2024 nondystrophic myotonia Grete Andersen, MD Unknown No outcome recorded

Evidence & citations 17 cited values

Every value below carries the sentence it was read from. 32 sources stand behind the page.

FieldValueCited text
Known as Mexiletine “Patients who 'failed' amiodarone (greater or equal to 300mg/day) will be prescribed: Amiodarone at the current dose with the addition of mexiletine 400 to 800 mg/day” NCT00905853
28

“Either one or more of the following antiarrhythmic drugs: sotalol, mexiletine, procainamide, or amiodarone.” NCT02114528

NCT06549400

NCT02260388

NCT04700046

NCT06862596

NCT01849770

NCT00383682

NCT05619120

NCT00000518

NCT02781454

NCT01811355

NCT06523400

NCT01406873

NCT00001784

NCT00004647

NCT02045667

NCT00000793

NCT06669299

NCT01717404

NCT05017155

NCT04624750

NCT07097701

NCT00832000

NCT02336477

NCT02308748

NCT04622553

NCT02561702

NCT00000464

Known as (rs)-mexiletine ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Known as Dl-mexiletine ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Known as Katen ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Known as KO 1173 CL ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Known as KO-1173 ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Known as Mexiletina ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Known as mexiletine HCl “Mexiletine 167 mg (equivalent to mexiletine HCl 200 mg) immediate release, oral capsules.” NCT04700046
Known as Mexiletine hydrochloride Mexiletine hydrochloride 300 mg is administered orally divided into three times a day after meals for 12 weeks.” NCT06862596
Known as Mexiletine PR Mexiletine PR 167 mg (mexiletine HCl 200 mg) Mexiletine PR 333 mg (mexiletine HCl 400 mg) OR Mexiletine PR 500 mg (mexiletine HCl 600 mg)” NCT06523400
Known as Mexitil ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Known as Mexitil p.l. ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Known as Namuscla ClinicalTrials.gov intervention name — accepted as the source's own label NCT05639257
Known as NSC-758639 ChEMBL registry synonym — accepted as the source's own label CHEMBL558
Action Restore “Incubation of cells that expressed this variant with mexiletine restored their sodium current” PMID 24613995 Mar 2014
Modality Small molecule “Mexiletine is a lidocaine-derivate and belongs to the class of 1B antiarrhythmic agents (Vaughan-Williams Classification of Antiarrhytmica).” NCT02045667
Route Oral “can be taken by mouth” NCT00001784