Drugs / Efmoroctocog Alfa

Regulatory milestones approvals, filings & regulatory actions · 1 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved EU (EMA) Elocta 2015-11-18 europa.eu

Trials 14 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 01 trial
Phase 0 NCT03272568 Feb 2018 → Dec 2019 hemophilia, menstrual disorder Emory University Completed No outcome recorded
Phase 13 trials
Phase 1 NCT03364998 Nov 2017 → Jan 2018 hemophilia A Bayer Completed No outcome recorded
Phase 1 NCT02083965 Mar → Oct 2014 severe hemophilia A Bioverativ Therapeutics Inc. Completed No outcome recorded
Phase 1 NCT01027377 Dec 2009 → Jul 2010 severe hemophilia A Bioverativ Therapeutics Inc. Completed No outcome recorded
Phase 37 trials
Phase 3 NCT06137092 Jul → Sep 2023 severe hemophilia A AryoGen Pharmed Co. Completed No outcome recorded
Phase 3 NCT02196207 Aug 2020 → Jul 2027 severe hemophilia A Margaret Ragni Withdrawn No outcome recorded
Phase 3 NCT02502149 Aug 2015 → Apr 2017 severe hemophilia A Bioverativ Therapeutics Inc. Completed No outcome recorded
Phase 3 NCT02234323 Jan 2015 → Sep 2019 hemophilia A Bioverativ, a Sanofi company Completed No outcome recorded
Phase 3 NCT01458106 Nov 2012 → Dec 2013 hemophilia A Bioverativ Therapeutics Inc. Completed No outcome recorded
Phase 3 NCT01454739 Dec 2011 → Oct 2017 hemophilia A Bioverativ Therapeutics Inc. Completed No outcome recorded
Phase 3 NCT01181128 Nov 2010 → Aug 2012 severe hemophilia A Bioverativ Therapeutics Inc. Completed No outcome recorded
Phase 43 trials
Phase 4 NCT04728217 Apr 2021 → Feb 2023 hemophilia A The League of Clinical Research, Russia Completed No outcome recorded
Phase 4 NCT03093480 Dec 2017 → May 2020 hemophilia A Bioverativ, a Sanofi company Completed No outcome recorded
Phase 4 NCT03103542 Aug 2017 → Sep 2019 hemophilia A Swedish Orphan Biovitrum Completed No outcome recorded
Also used as a comparator or background therapy in 3 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 32 trials
Phase 3 NCT04303572 Background Nov 2021 → Jun 2022 severe hemophilia A Margaret Ragni Terminated No outcome recorded
Phase 3 NCT04303559 Comparator Oct 2021 → Apr 2022 hemophilia A Margaret Ragni Terminated No outcome recorded
Phase 41 trial
Phase 4 NCT04690322 Comparator Apr 2021 → Jul 2027 hemophilia A University of Texas Southwestern Medical Center Withdrawn No outcome recorded

Evidence & citations 16 cited values

Every value below carries the sentence it was read from. 21 sources stand behind the page.

FieldValueCited text
Known as efmoroctocog alfa “rescue ITI with efmoroctocog alfa, an extended half-life recombinant FVIII Fc fusion protein (herein rFVIIIFc)” PMID 39583653 Nov 2024
1

NCT04728217

Known as BIIB031 “Recombinant Coagulation Factor VIII Fc Fusion Protein, BIIB031, in the Prevention and Treatment of Bleeding Episodes in Pediatric Subjects With Hemophilia A” NCT01458106
Known as Efraloctocog alfa ChEMBL registry synonym — accepted as the source's own label CHEMBL4297945
Known as Elocta ClinicalTrials.gov intervention name — accepted as the source's own label NCT03364998
Known as Eloctate “Efmoroctocog Alfa Injection [Eloctate]” NCT04728217
4

NCT04690322

NCT04303559

NCT03272568

NCT02196207

Known as Eloctate ITI ClinicalTrials.gov intervention name — accepted as the source's own label NCT04303572
Known as ELOCTATE- antihemophilic factor (recombinant), fc fusion protein ELOCTATE- antihemophilic factor (recombinant), fc fusion proteinNCT04690322
Known as Factor VIII, recombinant human with Fc fusion Factor VIII, recombinant human with Fc fusion (rFVIII-Fc)” NCT06137092
Known as recombinant factor VIII Fc fusion protein Recombinant factor VIII Fc fusion protein for the treatment of severe haemophilia A: Final results from the ASPIRE extension study.” PMID 32227570 Mar 2020
Known as Recombinant Human Coagulation Factor VIII Fusion Protein “An Open-Label, Multicenter Evaluation of the Long-Term Safety and Efficacy of Recombinant Human Coagulation Factor VIII Fusion Protein (rFVIIIFc) in the Prevention and...” NCT01454739
Known as recombinant human Factor VIII Fc fusion protein “The primary objective of the study is to evaluate the long-term safety of recombinant human Factor VIII Fc fusion protein (rFVIIIFc) in participants with hemophilia A.” NCT01454739
Known as rFVIIIFc “Prevention Trial, Arm A: rFVIIIFc (Eloctate) 65 IU/kg weekly will be administered by intravenous infusion in previously untreated children with severe hemophilia A beginning...” NCT02196207
11

“randomized to preemptive weekly Eloctate (rFVIIIFc) vs. weekly Emicizumab (Hemlibra) to prevent inhibitor formation” NCT04303559

“rescue ITI with efmoroctocog alfa, an extended half-life recombinant FVIII Fc fusion protein (herein rFVIIIFc)” PMID 39583653 Nov 2024

NCT03093480

NCT01027377

NCT01458106

NCT02234323

NCT06137092

NCT01181128

NCT02083965

NCT01454739

NCT02502149

Action Restore “Prophylactic factor replacement” PMID 25912075 Apr 2015
Modality Protein / enzyme biologic “rFVIIIFc is a recombinant fusion protein composed of a single molecule of FVIII covalently linked to the Fc domain of human IgG(1) to extend circulating rFVIII t(1/2).” PMID 22223821 Jan 2012
Route Intravenous “single high dose intravenous injection of commercially available rFVIII with safety and PK assessments followed by a single high dose intravenous injection of rFVIIIFc with...” NCT01027377
Target F8 “Coagulation factor VIII exogenous protein” CHEMBL4297945