Drugs / bryostatin 1
last change Mar 2025 re-read 2 minutes ago

bryostatin 1

also known as NSC 339555 · bryostatin · BRYO

Small molecule

Developed for
lymphoma · leukemia · cancer of unknown primary site · Alzheimer disease · diffuse large B-cell lymphoma · kidney cancer · Burkitt lymphoma · esophageal cancer
+43 more · gastric cancer · mantle cell lymphoma · myelodysplastic syndrome · plasma cell myeloma · renal cell carcinoma · acute myeloid leukemia · acute myeloid leukemia with 11q23 abnormalities · acute myeloid leukemia with t(8;21)(q22;q22) translocation · acute myeloid leukemia, del(5q31-q32) · acute myeloid leukemia, inv(16)(p13.1;q22) · acute myeloid leukemia, t(16;16)(p13.1;q22) · B-cell chronic lymphocytic leukemia · blast phase chronic myelogenous leukemia, BCR-ABL1 positive · breast cancer · cervical cancer · chronic lymphocytic leukemia/small lymphocytic lymphoma · chronic myelomonocytic leukemia · colorectal cancer · cutaneous melanoma · fallopian tube cancer · gastric carcinoma · head and neck cancer · immunodeficiency-associated lymphoproliferative disease · large-cell immunoblastic lymphoma · leukemia, myeloid, accelerated-phase · lung cancer · lymphoblastic lymphoma · MALT lymphoma · metastatic melanoma · multiple sclerosis · myelodysplastic syndrome with ring sideroblasts · nodal marginal zone B-cell lymphoma · ovarian cancer · ovarian carcinoma · pancreatic acinar cell carcinoma · pancreatic ductal adenocarcinoma · paroxysmal nocturnal hemoglobinuria · peritoneum cancer · prostate cancer · small intestine cancer · splenic marginal zone lymphoma · thrombocytopenia · HIV infectious disease
Investigated by
National Cancer Institute (NCI) · Barbara Ann Karmanos Cancer Institute · Virginia Commonwealth University · Memorial Sloan Kettering Cancer Center · National Institute on Aging (NIA) · Neurotrope Bioscience, Inc.
+15 more · Blanchette Rockefeller Neurosciences Insitute · Brigham and Women's Hospital · Cancer Research UK · Dana-Farber Cancer Institute · Icahn School of Medicine at Mount Sinai · Lombardi Comprehensive Cancer Center · M.D. Anderson Cancer Center · NYU Langone Health · Robert Fox · Synaptogenix, Inc. · University of Chicago · University of Colorado, Denver · University of Glasgow · University of Maryland, Baltimore · Worldwide Clinical Trials

Trials 40 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 113 trials
Phase 1 NCT06190912 Jun 2024 → Mar 2025 multiple sclerosis Robert Fox Terminated No outcome recorded
Phase 1 NCT00112476 Mar 2005 → Jul 2010 metastatic melanoma, renal cell carcinoma National Cancer Institute (NCI) Completed No outcome recorded
Phase 1 NCT00022555 Nov 2001 → Jul 2003 Burkitt lymphoma, diffuse large B-cell lymphoma, immunodeficiency-associated lymphoproliferative disease National Cancer Institute (NCI) Completed No outcome recorded
Phase 1 NCT00012376 Mar 2001 → Jan 2010 acute myeloid leukemia with 11q23 abnormalities, acute myeloid leukemia with t(8;21)(q22;q22) translocation, acute myeloid leukemia, del(5q31-q32), acute myeloid leukemia, inv(16)(p13.1;q22) +7 National Cancer Institute (NCI) Completed No outcome recorded
Phase 1 NCT00006022 Sep 2000 → Oct 2003 cutaneous melanoma, kidney cancer Virginia Commonwealth University Completed No outcome recorded
Phase 1 NCT00004144 May 2000 → Dec 2006 cancer of unknown primary site Barbara Ann Karmanos Cancer Institute Completed No outcome recorded
Phase 1 NCT00003993 Sep 1999 → Jul 2008 lymphoma, small intestine cancer National Institute on Aging (NIA) Completed No outcome recorded
Phase 1 NCT00005580 Sep 1998 → Aug 2006 leukemia, lymphoma Virginia Commonwealth University Completed No outcome recorded
Phase 1 NCT00003166 May 1998 → Jul 2001 B-cell chronic lymphocytic leukemia, Burkitt lymphoma, diffuse large B-cell lymphoma, large-cell immunoblastic lymphoma +3 National Cancer Institute (NCI) Completed No outcome recorded
Phase 1 NCT00003242 Feb 1998 → Oct 2001 cancer of unknown primary site Memorial Sloan Kettering Cancer Center Completed No outcome recorded
Phase 227 trials
Phase 2 NCT03560245 Jun 2018 → Jul 2019 Alzheimer disease Neurotrope Bioscience, Inc. Completed No outcome recorded
Phase 2 NCT02431468 Nov 2015 → Feb 2017 Alzheimer disease Neurotrope Bioscience, Inc. Completed No outcome recorded
Phase 2 NCT00606164 Apr → Dec 2008 Alzheimer disease Blanchette Rockefeller Neurosciences Insitute Unknown No outcome recorded
Phase 2 NCT00087425 Jul 2004 → Oct 2007 leukemia, lymphoma National Institute on Aging (NIA) Completed No outcome recorded
Phase 2 NCT00058305 Mar 2003 → Dec 2007 MALT lymphoma, chronic lymphocytic leukemia/small lymphocytic lymphoma, diffuse large B-cell lymphoma, mantle cell lymphoma +2 National Cancer Institute (NCI) Completed No outcome recorded
Phase 2 NCT00031694 Mar 2002 → Apr 2010 pancreatic acinar cell carcinoma, pancreatic ductal adenocarcinoma National Cancer Institute (NCI) Completed No outcome recorded
Phase 2 NCT00032188 Jan 2002 → Jun 2006 renal cell carcinoma National Cancer Institute (NCI) Completed No outcome recorded
Phase 2 NCT00017342 Jul 2001 → Sep 2004 leukemia Virginia Commonwealth University Completed No outcome recorded
Phase 2 NCT00006389 Oct 2000 → Mar 2010 gastric carcinoma National Cancer Institute (NCI) Completed No outcome recorded
Phase 2 NCT00006942 Oct 2000 → Mar 2004 fallopian tube cancer, ovarian carcinoma, peritoneum cancer National Cancer Institute (NCI) Completed No outcome recorded
Also used as a comparator or background therapy in 4 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 12 trials
Phase 1 NCT02269605 Comparator Sep 2014 → Jan 2015 HIV infectious disease Fundacion para la Investigacion Biomedica del Hospital Universitario Ramon y Cajal Completed No outcome recorded
Phase 1 NCT00003174 Background May 1998 → Nov 2005 leukemia Barbara Ann Karmanos Cancer Institute Completed No outcome recorded
Phase 1/21 trial
Phase 1/2 NCT02221947 Comparator Jun → Dec 2014 Alzheimer disease Neurotrope Bioscience, Inc. Terminated No outcome recorded
Phase 21 trial
Phase 2 NCT04538066 Comparator Aug 2020 → Nov 2022 Alzheimer disease Neurotrope Bioscience, Inc. Completed No outcome recorded

Evidence & citations 7 cited values

Every value below carries the sentence it was read from. 50 sources stand behind the page.

FieldValueCited text
Known as Bryostatin-1 “BACKGROUND: We sought to determine the response rate and toxicity profile of sequential paclitaxel and bryostatin-1, a novel, selective inhibitor of protein kinase C, in...” PMID 18270704 Feb 2008
51

Bryostatin-1 is a macrocyclic lactone that has been shown to regulate protein kinase C (PKC) activity and thereby potentially inhibit tumor invasion, angiogenesis, cell...” PMID 15047228 Apr 2004

“BACKGROUND: Bryostatin-1 is a macrocyclic lactone, which exhibits pleiotropic biological effects via protein kinase C and has shown preclinical synergy with paclitaxel for...” PMID 12581572 Feb 2003

“A Phase lb Trial of the Combination of Bryostatin-1 and Low Dose Interleukin-2: Evaluation of the Functional and Molecular Status of Human Monocytes as Antigen Presenting Cells” NCT00003993

“An Open-Label, Non-Randomized Phase I Study of the Protein Kinase C Inhibitor Bryostatin-1 Administered in Combination With Paclitaxel in Patients With Advanced Solid Tumors” NCT00003242

“The protein kinase C (PKC) agonist bryostatin-1 has shown significant ex-vivo potency to revert HIV-1 latency, compared with other latency reversing agents (LRA).” PMID 26891037 Jun 2016

“Preclinical data suggested that bryostatin-1 (bryo) could potentiate the cytotoxicity of cisplatin when given prior to this drug.” PMID 19221754 Feb 2009

“The main purpose of this study is find out how safe a single dose of bryostatin 1 is in patients with Alzheimer's Disease (AD).” NCT00606164

“A Phase II Trial of Bryostatin-1 In Patients With Metastatic or Recurrent Squamos Cell Carcinoma of the Head and Neck” NCT00003443

“Phase II study of paclitaxel plus the protein kinase C inhibitor bryostatin-1 in advanced pancreatic carcinoma.” PMID 19738452 Apr 2010

“A Phase II Trial of Bryostatin-1 for the Treatment of Stage IV Breast Cancer” NCT00003205

NCT00003242

NCT00005028

NCT00003936

NCT00003205

NCT00112476

NCT02269605

NCT00032188

NCT00058305

NCT00005849

NCT00087425

NCT00003220

NCT00006022

NCT00002908

NCT00003993

NCT00022555

NCT00006942

NCT00002725

NCT00017342

NCT00006389

NCT00002907

NCT00003166

NCT00005599

NCT00136461

NCT00003079

NCT00003174

NCT04538066

NCT00004008

NCT00003443

NCT00003171

NCT00003132

NCT02431468

NCT00006081

NCT06190912

NCT00012376

NCT00004144

NCT00031694

NCT02221947

NCT00005056

NCT00003108

NCT00005580

NCT00003968

Known as BRYO “Preclinical data suggested that bryostatin-1 (bryo) could potentiate the cytotoxicity of cisplatin when given prior to this drug.” PMID 19221754 Feb 2009
2

“Single-Agent Chemotherapy/Differentiation Therapy. Bryostatin 1, BRYO, NSC-339555.” NCT00002725

Bryostatin 1 (BRYO; NSC 339555)” NCT00006022

Known as bryostatin “The investigational drug product, bryostatin, is a sterile, pyrogen-free, lyophilized powder intended for IV infusion upon reconstitution and dilution.” NCT02431468
3

“Eligible participants will be treated with bryostatin over a 26-week period.” NCT06190912

bryostatin 1 (hereafter referred to as bryostatin)” NCT04538066

NCT03560245

Known as NSC 339555 “A Phase II Study of Bryostatin-1 (NSC 339555) Plus Paclitaxel in Patients With Metastatic or Unresectable Locally Advanced Adenocarcinoma of the Stomach or Gastroesophageal Junction” NCT00006081
4

“Phase I Study of Bryostatin 1 (NSC 339555) and Fludarabine in Patients With Chronic Lymphocytic Leukemia and Indolent Non-Hodgkin's Lymphoma” NCT00005580

“Phase I Study of Bryostatin 1 (NSC 339555) and High-Dose 1-Beta-D-Arabinofuranosylcytosine (HiDAC) in Patients With Refractory Leukemia” NCT00003079

“Single-Agent Chemotherapy/Differentiation Therapy. Bryostatin 1, BRYO, NSC-339555.” NCT00002725

“Bryostatin 1 (BRYO; NSC 339555)” NCT00006022

Action Inhibit “Consistent inhibition of PKC isoform eta (eta) in peripheral blood mononuclear cells was observed following bryo.” PMID 19221754 Feb 2009
Modality Small molecule “Bryostatin 1 is a macrocyclic lactone” PMID 17145828 Dec 2006
Route Intravenous “bryostatin 1 IV over 24 hours on day 1” NCT00003132