Drugs / Taurursodiol
last change Jul 2026 re-read 2 minutes ago

Taurursodiol

Small molecule

Developed for
amyotrophic lateral sclerosis · hepatocellular carcinoma · amyloidosis · cholestasis · type 1 diabetes mellitus · arterial disorder · asthma · chronic progressive multiple sclerosis
+10 more · cirrhosis of liver · cystic fibrosis · hereditary amyloidosis · hypertensive disorder · isoproterenol-mediated vasodilatation · metabolic dysfunction-associated steatotic liver disease · obesity disorder · primary biliary cholangitis · ulcerative colitis · Alzheimer disease
Investigated by
Amylyx Pharmaceuticals Inc. · Beijing Trendful Kangjian Medical Information Consulting Limited Company · Bruschettini S.r.l. · Children's Hospital Medical Center, Cincinnati · Fondazione IRCCS Policlinico San Matteo di Pavia · Fudan University
+32 more · Humanitas Mirasole SpA · Italian National Institute of Health · KU Leuven · Motor Neurone Disease Association · UMC Utrecht · University Hospital, Tours · University of Dublin, Trinity College · University of Sheffield · University of Ulm · Washington University School of Medicine · Beijing Friendship Hospital · Breakthrough T1D · Brigham and Women's Hospital · Colorado State University · Crohn's and Colitis Foundation · Dallas VA Medical Center · European Commission · Federico II University · Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta · Johns Hopkins University · Juvenile Diabetes Research Foundation · Massachusetts General Hospital · Peking University First Hospital · Robin Goland, MD · Second Affiliated Hospital of Bengbu Medical College · The First Affiliated Hospital with Nanjing Medical University · Tongji Hospital · Tsinghua University · University of North Texas Health Science Center · University of Palermo · University of Vermont · University of Washington

Regulatory milestones approvals, filings & regulatory actions · 1 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved US (FDA) RELYVRIO 2022-09-29 fda.gov

Trials 29 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 02 trials
Phase 0 NCT04727320 Mar → Jul 2021 cirrhosis of liver The First Affiliated Hospital with Nanjing Medical University Unknown No outcome recorded
Phase 0 NCT04001647 Jun 2019 → Aug 2022 arterial disorder, isoproterenol-mediated vasodilatation Colorado State University Terminated No outcome recorded
Phase 12 trials
Phase 1 NCT04114292 Jan 2019 → Jun 2022 ulcerative colitis Washington University School of Medicine Completed No outcome recorded
Phase 1 NCT03878654 Jan → Sep 2019 asthma University of Vermont Terminated No outcome recorded
Phase 1/24 trials
Phase 1/2 NCT06025630 Aug 2023 → Dec 2028 expected hypertensive disorder University of North Texas Health Science Center Recruiting No outcome recorded
Phase 1/2 NCT04987671 Aug 2021 → May 2022 amyotrophic lateral sclerosis Amylyx Pharmaceuticals Inc. Unknown No outcome recorded
Phase 1/2 NCT03423121 Jun 2018 → Apr 2022 chronic progressive multiple sclerosis Johns Hopkins University Completed No outcome recorded
Phase 1/2 NCT01855360 Jun 2013 → May 2015 amyloidosis Brigham and Women's Hospital Completed No outcome recorded
Phase 210 trials
Phase 2 NCT07699380 Jun 2026 → Dec 2029 expected type 1 diabetes mellitus University of Washington Recruiting No outcome recorded
Phase 2 NCT07517276 Apr → May 2026 overdue metabolic dysfunction-associated steatotic liver disease Peking University First Hospital Not yet recruiting No outcome recorded
Phase 2 NCT07328009 Jan 2026 → Jan 2029 expected hepatocellular carcinoma Fudan University Recruiting No outcome recorded
Phase 2 NCT07100392 Aug 2025 → Aug 2027 expected hepatocellular carcinoma Fudan University Recruiting No outcome recorded
Phase 2 NCT07064668 Jul 2025 → Jun 2027 expected hepatocellular carcinoma Tongji Hospital Not yet recruiting No outcome recorded
Phase 2 NCT04244630 Nov 2023 → Dec 2025 overdue amyotrophic lateral sclerosis Dallas VA Medical Center Recruiting No outcome recorded
Phase 2 NCT03488524 Mar 2018 → Mar 2021 amyotrophic lateral sclerosis Amylyx Pharmaceuticals Inc. Completed No outcome recorded
Phase 2 NCT02218619 Aug 2015 → Dec 2019 type 1 diabetes mellitus Robin Goland, MD Completed No outcome recorded
Phase 2 NCT01171859 Jul 2010 → Apr 2015 hereditary amyloidosis Fondazione IRCCS Policlinico San Matteo di Pavia Completed No outcome recorded
Phase 2 NCT00877604 Jun 2008 → Jul 2011 amyotrophic lateral sclerosis Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta Completed No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT04516096 Nov 2020 → Dec 2022 amyotrophic lateral sclerosis Amylyx Pharmaceuticals Inc. Completed No outcome recorded
Phase 36 trials
Phase 3 NCT05619783 Dec 2022 → Oct 2024 amyotrophic lateral sclerosis Amylyx Pharmaceuticals Inc. Completed No outcome recorded
Phase 3 NCT05753852 Oct 2021 → Mar 2025 amyotrophic lateral sclerosis Humanitas Mirasole SpA Unknown No outcome recorded
Phase 3 NCT03800524 Feb 2019 → Dec 2023 amyotrophic lateral sclerosis Humanitas Mirasole SpA Unknown No outcome recorded
Phase 3 NCT03481972 Apr 2018 → Jan 2023 amyloidosis Fondazione IRCCS Policlinico San Matteo di Pavia Completed No outcome recorded
Phase 3 NCT01857284 Sep 2009 → Jan 2013 primary biliary cholangitis Beijing Friendship Hospital Completed No outcome recorded
Phase 3 NCT01829698 Aug 2009 → Jan 2013 cholestasis Beijing Trendful Kangjian Medical Information Consulting Limited Company Completed No outcome recorded
Phase not applicable4 trials
NCT06827873 Feb → May 2025 overdue Tsinghua University Not yet recruiting No outcome recorded
NCT00771901 Feb 2008 → Dec 2014 obesity disorder, type 2 diabetes mellitus Washington University School of Medicine Completed No outcome recorded
NCT00004410 Jun 1998 → Mar 2002 cholestasis Children's Hospital Medical Center, Cincinnati Completed No outcome recorded
NCT00004441 Sep 1997 → Sep 2001 cystic fibrosis Children's Hospital Medical Center, Cincinnati Completed No outcome recorded
Also used as a comparator or background therapy in 3 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 21 trial
Phase 2 NCT03533257 Comparator Sep 2018 → Oct 2020 Alzheimer disease Amylyx Pharmaceuticals Inc. Completed No outcome recorded
Phase 41 trial
Phase 4 NCT01998451 Background Dec 2012 → Dec 2018 gallstones The First Affiliated Hospital of Guangzhou Medical University Unknown No outcome recorded
Phase not applicable1 trial
NCT01877551 Comparator Sep 2013 → May 2018 Washington University School of Medicine Completed No outcome recorded

Evidence & citations 14 cited values

Every value below carries the sentence it was read from. 35 sources stand behind the page.

FieldValueCited text
Known as taurursodiol “Sodium Phenylbutyrate (PB) and Taurursodiol (TURSO, also known as Ursodoxicoltaurine or Tauroursodeoxycholic Acid [TUDCA])” NCT03488524
5

“Over-the-counter anti-oxidants, namely vitamin E, NAc cysteine, L-cystine, Nicotinamide and Taurursodiol at defined doses” NCT04244630

“AMX0035 twice daily--a combination of Sodium Phenylbutyrate (3g) and Taurursodiol (1g)” NCT03533257

“oral AMX0035 (sodium phenylbutyrate + taurursodiol) versus placebo” NCT07699380

“Fixed dose combination of Sodium Phenylbutyrate and taurursodiol.” NCT04987671

“Combination of 3 g phenylbutyrate and 1 g taurursodiolNCT05619783

Known as tauroursodeoxycholate “The more hydrophilic bile acid tauroursodeoxycholate (TUDCA) is the active ingredients of UDCA” NCT01857284
Known as Tauroursodeoxycholic Acid Tauroursodeoxycholic acid (TUDCA), a naturally occurring bile acid, acts as a chemical chaperone to reduce protein aggregation and colitis severity in preclinical models.” PMID 40236400 Apr 2025
26

“Sodium Phenylbutyrate (PB) and Taurursodiol (TURSO, also known as Ursodoxicoltaurine or Tauroursodeoxycholic Acid [TUDCA])” NCT03488524

“Testing arm: tauroursodeoxycholic acid, 750mg , divided into three times, each time 250mg, oral administration, after meal” NCT01829698

“Oral Double Wood brand TUDCA (Tauroursodeoxycholic Acid) dietary supplement capsules, dosage 1000 mg/person/day.” NCT06827873

“the chemical chaperone tauroursodeoxycholic acid (TUDCA), an established inhibitor of ER stress” NCT04001647

Tauroursodeoxycholic Acid and Sodium Phenylbutyrate orally given twice a day” NCT04516096

Tauroursodeoxycholic Acid (TUDCA): 250 mg orally twice daily.” NCT07328009

“TUDCA (Tauroursodeoxycholic Acid) Supplementation” NCT07064668

tauroursodeoxycholic acid (TUDCA; 1,750 mg/day)” NCT06025630

NCT00771901

NCT01855360

NCT02218619

NCT01857284

NCT01171859

NCT03423121

NCT05753852

NCT00004441

NCT07100392

NCT00877604

NCT07517276

NCT04727320

NCT00004410

NCT01877551

NCT03481972

NCT01998451

NCT03800524

NCT03878654

Known as Tauroursodeoxycholic Acid [TUDCA] “Sodium Phenylbutyrate (PB) and Taurursodiol (TURSO; also known as Tauroursodeoxycholic Acid [TUDCA])” NCT03533257
Known as Tauroursodesoxycholic acid ChEMBL registry synonym — accepted as the source's own label CHEMBL272427
Known as Taurursodiol component of relyvrio ChEMBL registry synonym — accepted as the source's own label CHEMBL272427
Known as TUDCA “Tauroursodeoxycholic acid (TUDCA), a naturally occurring bile acid, acts as a chemical chaperone to reduce protein aggregation and colitis severity in preclinical models.” PMID 40236400 Apr 2025
14

“Determine the optimum dose of tauroursodeoxycholic acid (TUDCA) required to achieve maximal bioavailability for patients with cystic fibrosis-associated liver disease.” NCT00004441

“Given all of this information, the investigators propose that a specific bile acid called tauroursodeoxycholic acid (TUDCA) may be helpful in patients with asthma.” NCT03878654

“Tauroursodeoxycholic acid (TUDCA) is a hydrophilic bile acid that is produced in the liver and used for treatment of chronic cholestatic liver diseases.” PMID 25664595 Feb 2015

“Sodium Phenylbutyrate (PB) and Taurursodiol (TURSO, also known as Ursodoxicoltaurine or Tauroursodeoxycholic Acid [TUDCA])” NCT03488524

“Half of the participants will receive the bile acid tauroursodeoxycholic acid (TUDCA) and half will receive placebo.” NCT03423121

“the chemical chaperone tauroursodeoxycholic acid (TUDCA), an established inhibitor of ER stress” NCT04001647

“The more hydrophilic bile acid tauroursodeoxycholate (TUDCA) is the active ingredients of UDCA” NCT01857284

“infants treated with tauroursodeoxycholic acid (TUDCA) have a lower peak direct bilirubin” NCT00004410

“Tauroursodeoxycholic Acid (TUDCA): 250 mg orally twice daily.” NCT07328009

“tauroursodeoxycholic acid (TUDCA).” NCT03481972

“tauroursodeoxycholic acid (TUDCA)” NCT07100392

NCT06827873

NCT06025630

NCT07064668

Known as TURSO “Sodium phenylbutyrate and taurursodiol (PB and TURSO) is hypothesized to mitigate endoplasmic reticulum stress and mitochondrial dysfunction, two of many mechanisms implicated...” PMID 39131742 Aug 2024
1

“Sodium Phenylbutyrate (PB) and Taurursodiol (TURSO, also known as Ursodoxicoltaurine or Tauroursodeoxycholic Acid [TUDCA])” NCT03488524

Known as Ur-906 ChEMBL registry synonym — accepted as the source's own label CHEMBL272427
Known as Ursodeoxycholyltaurine ChEMBL registry synonym — accepted as the source's own label CHEMBL272427
Known as Ursodoxicoltaurine “Sodium Phenylbutyrate (PB) and Taurursodiol (TURSO, also known as Ursodoxicoltaurine or Tauroursodeoxycholic Acid [TUDCA])” NCT03488524
Action Inhibit “the chemical chaperone tauroursodeoxycholic acid (TUDCA), an established inhibitor of ER stress” NCT04001647
Modality Small molecule “Tauroursodeoxycholic acid (TUDCA), a naturally occurring bile salt” NCT01877551
Route Oral “TUDCA is administered by mouth” NCT00004410