Drugs / Danazol
last change Dec 2025 re-read 2 minutes ago

Danazol

also known as Danatrol · Danocrine · Danol · NSC-270916 · Optina · VML-0501 · WIN 17,757

Other / unclassified targets AR, PGR via activation

Developed for
autoimmune thrombocytopenia · diabetic macular edema · endometriosis · aplastic anemia · breast fibrocystic disease · cirrhosis of liver · dyskeratosis congenita · endometrial cancer
+9 more · Fanconi anemia · infertility disorder · myelodysplastic syndrome · myelofibrosis · ovarian dysfunction · primary myelofibrosis · telomere syndrome · thrombotic thrombocytopenic purpura · pulmonary fibrosis
Investigated by
Peking University People's Hospital · Beijing Hospital · Beijing Friendship Hospital · China-Japan Friendship Hospital · Navy General Hospital, Beijing · Beijing Luhe Hospital
+35 more · Beijing Tsinghua Changgeng Hospital · Chinese PLA General Hospital · National Cancer Institute (NCI) · Peking University First Hospital · Peking University Third Hospital · Ain Shams University · Ampio Pharmaceuticals. Inc. · Assistance Publique - Hôpitaux de Paris · Beijing Municipal Science & Technology Commission · Beijing Tongren Hospital · Beth Israel Medical Center · Blood Cancer UK · Boston Children's Hospital · Dudley Group NHS Foundation Trust · FemmePharma Global Healthcare, Inc. · First Affiliated Hospital of Chongqing Medical University · Gynecologic Oncology Group · IVI Madrid · Icahn School of Medicine at Mount Sinai · King's College Hospital NHS Trust · Kyowa Kirin Co., Ltd. · Lumara Health, Inc. · Mayo Clinic · National Heart, Lung, and Blood Institute (NHLBI) · Parc de Salut Mar · Prof. Janet Dunn · Qilu Hospital of Shandong University · Seoul National University Hospital · Shanxi Bethune Hospital · The First Affiliated Hospital of Zhengzhou University · Unity Health Toronto · University of Birmingham · University of Manchester · University of Southern California · Viramal Limited

Regulatory milestones approvals, filings & regulatory actions · 3 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Label expansions (2) US (FDA) DANOCRINE 1980-09-02 – 1981-05-18 fda.gov
Approved US (FDA) DANOCRINE 1976-06-21 fda.gov

Trials 27 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT04757532 Dec 2020 → Mar 2021 Parc de Salut Mar Completed No outcome recorded
Phase 1/24 trials
Phase 1/2 NCT03710356 Oct 2018 → Oct 2021 telomere syndrome Assistance Publique - Hôpitaux de Paris Unknown No outcome recorded
Phase 1/2 NCT03460808 Mar 2018 → Jan 2020 autoimmune thrombocytopenia Peking University People's Hospital Unknown No outcome recorded
Phase 1/2 NCT01441037 Jul 2011 → Nov 2016 aplastic anemia National Heart, Lung, and Blood Institute (NHLBI) Completed No outcome recorded
Phase 1/2 NCT01001598 Nov 2009 → May 2014 Fanconi anemia, dyskeratosis congenita Boston Children's Hospital Terminated No outcome recorded
Phase 220 trials
Phase 2 NCT04873102 Aug 2024 → Aug 2027 expected cirrhosis of liver University of Southern California Recruiting No outcome recorded
Phase 2 NCT06176911 Dec 2023 → Dec 2024 autoimmune thrombocytopenia Peking University People's Hospital Unknown No outcome recorded
Phase 2 NCT05852847 May 2023 → Nov 2024 autoimmune thrombocytopenia Peking University People's Hospital Unknown No outcome recorded
Phase 2 NCT05494307 Sep 2022 → Sep 2023 autoimmune thrombocytopenia Peking University People's Hospital Unknown No outcome recorded
Phase 2 NCT05471050 Mar 2022 → Mar 2023 autoimmune thrombocytopenia Peking University People's Hospital Unknown No outcome recorded
Phase 2 NCT04997811 Dec 2021 → Jan 2025 myelodysplastic syndrome Prof. Janet Dunn Unknown No outcome recorded
Phase 2 NCT05281068 Sep 2021 → Sep 2023 autoimmune thrombocytopenia Peking University People's Hospital Unknown No outcome recorded
Phase 2 NCT05353673 Jun 2021 → Dec 2022 autoimmune thrombocytopenia, blood coagulation disease Peking University People's Hospital Unknown No outcome recorded
Phase 2 NCT04481282 Jul 2020 → Mar 2021 autoimmune thrombocytopenia Peking University People's Hospital Unknown No outcome recorded
Phase 2 NCT04289207 Mar → Sep 2020 autoimmune thrombocytopenia Seoul National University Hospital Unknown No outcome recorded
Phase 31 trial
Phase 3 NCT03563664 Aug 2015 → Aug 2017 infertility disorder Ain Shams University Completed No outcome recorded
Phase not applicable1 trial
NCT04058678 Jan 2020 → Dec 2021 ovarian dysfunction IVI Madrid Completed No outcome recorded
Also used as a comparator or background therapy in 11 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/21 trial
Phase 1/2 NCT04807309 Comparator Jan → Nov 2021 telomere syndrome Brigham and Women's Hospital Withdrawn No outcome recorded
Phase 24 trials
Phase 2 NCT04638517 Comparator Sep 2021 → Jan 2025 dyskeratosis congenita, pulmonary fibrosis, telomere syndrome The University of Queensland Terminated No outcome recorded
Phase 2 NCT07183787 Comparator Apr → Oct 2019 endometriosis Sidra Salman Completed No outcome recorded
Phase 2 NCT03312400 Comparator Feb 2018 → Oct 2025 telomere syndrome National Heart, Lung, and Blood Institute (NHLBI) Completed No outcome recorded
Phase 2 NCT00744276 Comparator Jan 2007 → Apr 2009 breast fibrocystic disease FemmePharma Global Healthcare, Inc. Completed No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT04324060 Comparator Mar 2020 → Mar 2022 myelodysplastic syndrome Peking Union Medical College Hospital Unknown No outcome recorded
Phase 34 trials
Phase 3 NCT05697471 Comparator Feb 2023 → Dec 2025 endometriosis Far Eastern Memorial Hospital Unknown No outcome recorded
Phase 3 NCT04576156 Comparator Apr 2021 → Jun 2028 expected myelofibrosis Geron Corporation Active not recruiting No outcome recorded
Phase 3 NCT04173494 Comparator Feb 2020 → Dec 2021 myelofibrosis, primary myelofibrosis Sierra Oncology LLC - a GSK company Completed No outcome recorded
Phase 3 NCT03165734 Comparator Jun 2017 → Oct 2026 expected myelofibrosis, primary myelofibrosis Swedish Orphan Biovitrum Active not recruiting No outcome recorded
Phase 41 trial
Phase 4 NCT01779232 Comparator Oct 2012 → Aug 2015 endometriosis, infertility disorder, ovarian cyst Centre for Endocrinology and Reproductive Medicine, Italy Completed No outcome recorded

Evidence & citations 14 cited values

Every value below carries the sentence it was read from. 39 sources stand behind the page.

FieldValueCited text
Known as danazol “which may include but is not limited to hydroxyurea, thalidomide or an analog of thalidomide, interferon, danazol, hypomethylating agents, chemotherapy or radiotherapy.” NCT04576156
37

“corticosteroids, hydroxyurea, danazol, or low-dose ruxolitinib” NCT03165734

NCT01732445

NCT06176911

NCT03563664

NCT03352076

NCT04481282

NCT07183787

NCT03460808

NCT00744276

NCT05697471

NCT04997811

NCT00758953

NCT01441037

NCT05852847

NCT00953771

NCT00003946

NCT04873102

NCT04058678

NCT01105793

NCT01001598

NCT04807309

NCT05494307

NCT03909763

NCT01821677

NCT04324060

NCT01779232

NCT03312400

NCT04638517

NCT05353673

NCT01667263

NCT04289207

NCT03710356

NCT02002403

NCT04173494

NCT05281068

NCT04757532

NCT05471050

Known as Danatrol “Danazol treatment administered as an oral capsule (Danatrol)” NCT03352076
Known as Danocrine ChEMBL registry synonym — accepted as the source's own label CHEMBL1479
Known as Danol “Participants were treated with danazol (Danol® 200mg capsules, Sanofi, Guildford, UK) in daily dosage of 400 mg for 12 weeks.” NCT03563664
Known as NSC-270916 ChEMBL registry synonym — accepted as the source's own label CHEMBL1479
Known as Optina “The drug being tested in this study is low doses of Optina (formerly known as Danazol)” NCT02002403
Known as VML-0501 VML-0501 (100 mg Danazol)” NCT03352076
Known as WIN 17,757 ChEMBL registry synonym — accepted as the source's own label CHEMBL1479
Action Activate “Progesterone receptor agonist” CHEMBL1479
1

“Androgen Receptor agonist” CHEMBL1479

Action Inhibit “It suppresses the pituitary-ovarian axis by inhibiting the pituitary output of gonadotropins.” NCT04873102
Modality Other / unclassified “Danazol is a synthetic steroid hormone structurally resembling a group of natural hormones (androgens)found in the body.” NCT00953771
Route Oral “Patients receive oral danazol 4 times per day for at least 4 weeks.” NCT00003946
Target AR “Androgen Receptor agonist” CHEMBL1479
Target PGR “Progesterone receptor agonist” CHEMBL1479