Drugs / Gemtuzumab Ozogamicin
last change Oct 2025 re-read 2 minutes ago

Gemtuzumab Ozogamicin

also known as Mylotarg · CMA-676 · gemtuzumab · CDP-771 · GTMZ · Mylotarg (GO)

Monoclonal antibody targets CD33

Developed for
acute myeloid leukemia · leukemia · myelodysplastic syndrome · acute promyelocytic leukemia · acute myeloid leukemia with 11q23 abnormalities · acute myeloid leukemia with abnormal bone marrow eosinophils inv(16)(p13q22) or t(16;16)(p13;q22) · acute myeloid leukemia with t(8;21)(q22;q22) translocation · acute megakaryoblastic leukemia in adult
+19 more · acute myeloblastic leukemia with maturation · acute myeloblastic leukemia without maturation · acute myeloid leukemia, inv(16)(p13.1;q22) · acute myeloid leukemia, t(16;16)(p13.1;q22) · acute myelomonocytic leukemia M4 · adult acute monocytic leukemia · acute myeloid leukemia with minimal differentiation · acute myeloid leukemia, t(8;21)(q22; q22.1) · childhood acute myeloid leukemia · erythroleukemia · juvenile myelomonocytic leukemia · acute erythroid leukemia · acute myeloid leukemia, t(9;11)(p21.3;q23.3) · chronic lymphocytic leukemia/small lymphocytic lymphoma · core binding factor acute myeloid leukemia · myelodysplastic syndrome with excess blasts · myeloid leukemia · acute myeloid leukemia with multilineage dysplasia · therapy related acute myeloid leukemia and myelodysplastic syndrome
Investigated by
National Cancer Institute (NCI) · Pfizer · M.D. Anderson Cancer Center · Wyeth is now a wholly owned subsidiary of Pfizer · European Organisation for Research and Treatment of Cancer - EORTC · Fred Hutchinson Cancer Center
+57 more · Children's Oncology Group · GIMEMA Foundation · Jazz Pharmaceuticals · New York Medical College · SWOG Cancer Research Network · University Hospital Heidelberg · Acute Leukemia French Association · Eastern Cooperative Oncology Group · Jonsson Comprehensive Cancer Center · University of Ulm · Versailles Hospital · Wake Forest University Health Sciences · Weill Medical College of Cornell University · AbbVie · Alliance for Clinical Trials in Oncology · Assistance Publique - Hôpitaux de Paris · Brown University · Cancer Research UK · Celgene Corporation · Columbia University · Eisai Inc. · Emory University · Genta Incorporated · German Cancer Research Center · H. Lee Moffitt Cancer Center and Research Institute · HOVON Foundation · Hematologics, Inc · Italian Association of Pediatric Hematology and Oncology · John Quigley · Kanisa Pharmaceuticals · Medical College of Wisconsin · National Cancer Institute, France · National Center for Tumor Diseases, Heidelberg · Novartis Pharmaceuticals · Rhode Island Hospital · Robert Redner, MD · Roswell Park Cancer Institute · Shaare Zedek Medical Center · Spanish Cooperative Group for the Study and Treatment of Acute Leukemias and Myelodysplasias · St. Jude Children's Research Hospital · Technical University Dresden · The Cleveland Clinic · The Miriam Hospital · The University of New South Wales · Uma Borate · University Hospital Carl Gustav Carus · University Hospital Dresden · University Hospital, Udine, Italy · University of Aarhus · University of Birmingham · University of California, Los Angeles · University of California, San Diego · University of Maryland, Baltimore · University of Michigan · University of Pittsburgh · University of Washington · Vor Biopharma

Regulatory milestones approvals, filings & regulatory actions · 4 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Label expansion US (FDA) MYLOTARG 2020-06-16 fda.gov
Approved EU (EMA) Mylotarg 2018-04-19 europa.eu
Approved US (FDA) MYLOTARG 2017-09-01 fda.gov
Refused (EMA) EU (EMA) Mylotarg 2008-04-14 europa.eu

Trials 85 · started per year

today
US approved 2017
EU approved 2018
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199719981999200020012002200320042005200620072008200920102011201220132014201520162017201820192020202120222023202420252026202720282029
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 113 trials
Phase 1 NCT05662904 Jan 2028 → Jan 2029 expected acute myeloid leukemia German Cancer Research Center Not yet recruiting No outcome recorded
Phase 1 NCT05558124 Feb 2023 → Apr 2027 expected acute myeloid leukemia H. Lee Moffitt Cancer Center and Research Institute Recruiting No outcome recorded
Phase 1 NCT04915612 May 2021 → Jan 2025 acute myeloid leukemia M.D. Anderson Cancer Center Completed No outcome recorded
Phase 1 NCT04207190 Oct 2020 → May 2024 acute myeloid leukemia Roswell Park Cancer Institute Completed No outcome recorded
Phase 1 NCT04070768 Sep 2019 → Oct 2023 acute myeloid leukemia John Quigley Completed No outcome recorded
Phase 1 NCT03878927 Aug 2019 → Aug 2022 acute myeloid leukemia Weill Medical College of Cornell University Terminated No outcome recorded
Phase 1 NCT03904251 Jul 2019 → Oct 2023 acute myeloid leukemia Jonsson Comprehensive Cancer Center Terminated No outcome recorded
Phase 1 NCT03848754 May 2019 → May 2021 acute myeloid leukemia Medical College of Wisconsin Completed No outcome recorded
Phase 1 NCT03900949 Mar 2019 → Aug 2024 acute myeloid leukemia Uma Borate Completed No outcome recorded
Phase 1 NCT00660036 Sep 2008 → Apr 2011 acute myeloid leukemia University of Pittsburgh Terminated No outcome recorded
Phase 1/210 trials
Phase 1/2 NCT04849910 Dec 2021 → May 2025 acute myeloid leukemia, myelodysplastic syndrome Vor Biopharma Terminated No outcome recorded
Phase 1/2 NCT04385290 Sep 2020 → Apr 2027 expected acute myeloid leukemia Technical University Dresden Recruiting No outcome recorded
Phase 1/2 NCT03531918 Sep 2018 → Jul 2021 acute myeloid leukemia Fred Hutchinson Cancer Center Completed No outcome recorded
Phase 1/2 NCT03390296 Dec 2017 → Feb 2022 acute myeloid leukemia M.D. Anderson Cancer Center Completed No outcome recorded
Phase 1/2 NCT00895934 May 2009 → Jul 2013 acute megakaryoblastic leukemia in adult, acute myeloblastic leukemia with maturation, acute myeloblastic leukemia without maturation, acute myeloid leukemia with 11q23 abnormalities +6 National Cancer Institute (NCI) Completed No outcome recorded
Phase 1/2 NCT02182596 Jun 2006 → Sep 2007 acute myeloid leukemia Acute Leukemia French Association Completed No outcome recorded
Phase 1/2 NCT00233909 Oct 2005 → Mar 2008 myeloid leukemia Kanisa Pharmaceuticals Completed No outcome recorded
Phase 1/2 NCT00766116 Jul 2005 → Sep 2014 acute myeloid leukemia University of California, San Diego Completed No outcome recorded
Phase 1/2 NCT00460447 Oct 2004 → ? acute myeloid leukemia University Hospital Carl Gustav Carus Unknown No outcome recorded
Phase 1/2 NCT00038831 May 2001 → Mar 2005 acute myeloid leukemia, chronic lymphocytic leukemia/small lymphocytic lymphoma, myelodysplastic syndrome M.D. Anderson Cancer Center Completed No outcome recorded
Phase 240 trials
Phase 2 NCT06917911 Feb → Nov 2027 expected core binding factor acute myeloid leukemia National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 2 NCT05599360 Aug 2022 → Sep 2028 expected acute myeloid leukemia Shaare Zedek Medical Center Active not recruiting No outcome recorded
Phase 2 NCT04326439 Jan 2020 → Mar 2022 childhood acute myeloid leukemia Emory University Terminated No outcome recorded
Phase 2 NCT03374332 Dec 2019 → Sep 2023 overdue acute myeloid leukemia Brown University Active not recruiting No outcome recorded
Phase 2 NCT04050280 Nov 2019 → Jun 2027 expected acute myeloid leukemia University of Maryland, Baltimore Recruiting No outcome recorded
Phase 2 NCT04173585 Oct 2019 → Feb 2023 acute myeloid leukemia University Hospital Heidelberg Completed No outcome recorded
Phase 2 NCT04793919 Oct 2019 → Oct 2025 overdue acute promyelocytic leukemia Italian Association of Pediatric Hematology and Oncology Recruiting No outcome recorded
Phase 2 NCT03839446 Feb 2019 → Feb 2023 acute myeloid leukemia Robert Redner, MD Completed No outcome recorded
Phase 2 NCT03737955 Nov 2018 → Dec 2026 expected acute myeloid leukemia University of Washington Recruiting No outcome recorded
Phase 2 NCT03672539 Nov 2018 → Nov 2027 expected acute myeloid leukemia, chronic myelomonocytic leukemia, myelodysplastic syndrome M.D. Anderson Cancer Center Active not recruiting No outcome recorded
Phase 2/35 trials
Phase 2/3 NCT02473146 Nov 2015 → Feb 2021 acute myeloid leukemia Versailles Hospital Completed No outcome recorded
Phase 2/3 NCT00909168 Mar 2008 → May 2009 acute myeloid leukemia University Hospital, Udine, Italy Completed No outcome recorded
Phase 2/3 NCT00454480 Aug 2006 → Aug 2012 leukemia, myelodysplastic syndrome The University of New South Wales Completed No outcome recorded
Phase 2/3 NCT00091234 Jun 2004 → Dec 2013 leukemia European Organisation for Research and Treatment of Cancer - EORTC Unknown No outcome recorded
Phase 2/3 NCT00038805 May 2001 → Nov 2004 leukemia M.D. Anderson Cancer Center Terminated No outcome recorded
Phase 313 trials
Phase 3 NCT04093505 Apr 2021 → Jun 2022 acute myeloid leukemia University Hospital Heidelberg Terminated No outcome recorded
Phase 3 NCT04168502 Sep 2020 → Apr 2025 overdue acute myeloid leukemia GIMEMA Foundation Recruiting No outcome recorded
Phase 3 NCT02724163 Apr 2016 → Dec 2031 expected acute myeloid leukemia University of Birmingham Active not recruiting No outcome recorded
Phase 3 NCT00893399 May 2010 → Sep 2021 acute myeloid leukemia University of Ulm Completed No outcome recorded
Phase 3 NCT00927498 Dec 2007 → Jul 2011 acute myeloid leukemia Acute Leukemia French Association Completed No outcome recorded
Phase 3 NCT00372593 Aug 2006 → Aug 2013 leukemia Children's Oncology Group Completed No outcome recorded
Phase 3 NCT00121303 Jan 2005 → Jan 2009 leukemia, myelodysplastic syndrome HOVON Foundation Completed No outcome recorded
Phase 3 NCT00085709 Jul 2004 → Mar 2010 leukemia SWOG Cancer Research Network Completed No outcome recorded
Phase 3 NCT00476541 Jan 2004 → Jan 2012 acute myeloid leukemia University of Aarhus Completed No outcome recorded
Phase 3 NCT00049517 Dec 2002 → Mar 2009 leukemia Eastern Cooperative Oncology Group Completed No outcome recorded
Phase 42 trials
Phase 4 NCT03727750 Jul 2019 → Apr 2021 Pfizer Completed No outcome recorded
Phase 4 NCT00304447 Apr 2002 → Jan 2004 acute myeloid leukemia Wyeth is now a wholly owned subsidiary of Pfizer Completed No outcome recorded
Phase not stated2 trials
NCT01869803 acute myeloid leukemia with 11q23 abnormalities, acute myeloid leukemia with abnormal bone marrow eosinophils inv(16)(p13q22) or t(16;16)(p13;q22), acute myeloid leukemia with t(8;21)(q22;q22) translocation, acute promyelocytic leukemia +1 Wake Forest University Health Sciences Approved for marketing No outcome recorded
NCT02312037 acute myeloid leukemia Pfizer No longer available No outcome recorded
Also used as a comparator or background therapy in 12 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 01 trial
Phase 0 NCT03568994 Background Jul 2018 → Sep 2020 acute myeloid leukemia Baylor College of Medicine Completed No outcome recorded
Phase 11 trial
Phase 1 NCT00577694 Background Nov 2007 → Jul 2010 leukemia UNC Lineberger Comprehensive Cancer Center Terminated No outcome recorded
Phase 26 trials
Phase 2 NCT05564390 Comparator Jun 2024 → May 2029 expected acute myeloid leukemia with multilineage dysplasia, myelodysplastic syndrome, therapy related acute myeloid leukemia and myelodysplastic syndrome National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 2 NCT05904106 Comparator Apr 2024 → Sep 2028 expected acute myeloid leukemia Technical University Dresden Recruiting No outcome recorded
Phase 2 NCT05955261 Background Jul 2023 → Dec 2026 acute myeloid leukemia St. Jude Children's Research Hospital Suspended No outcome recorded
Phase 2 NCT03589729 Background Sep 2018 → Dec 2027 expected Philadelphia-positive myelogenous leukemia, blast phase chronic myelogenous leukemia, BCR-ABL1 positive, myelodysplastic syndrome, myeloid sarcoma M.D. Anderson Cancer Center Recruiting No outcome recorded
Phase 2 NCT00798213 Comparator Jan 2009 → Apr 2010 acute lymphoblastic leukemia, acute myeloid leukemia Merck Sharp & Dohme LLC Terminated No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT02272478 Comparator Oct 2014 → Feb 2021 acute myeloid leukemia, myelodysplastic syndrome Cardiff University Unknown No outcome recorded
Phase 33 trials
Phase 3 NCT05183035 Background Oct 2022 → Feb 2027 expected acute myeloid leukemia PedAL BCU, LLC Recruiting No outcome recorded
Phase 3 NCT04293562 Background Jul 2020 → Jun 2029 expected acute myeloid leukemia Children's Oncology Group Recruiting No outcome recorded
Phase 3 NCT02665065 Comparator Jun 2016 → Jun 2022 overdue acute myeloid leukemia Actinium Pharmaceuticals Active not recruiting No outcome recorded

Press releases naming this drug 4 releases

DateIssuerRelease
2018-04-23 Pfizer MYLOTARG™ Approved In The EU For The Treatment Of Previously Untreated, De Novo, CD33-positive Acute Myeloid Leukemia In Combination With Chemotherapy pfizer.com
2018-02-23 Pfizer Pfizer Receives Positive CHMP Opinion for Two Hematology Medicines, MYLOTARG™ and BOSULIF® pfizer.com
2017-09-01 Pfizer Pfizer Receives FDA Approval for MYLOTARG™ (gemtuzumab ozogamicin) pfizer.com
2017-07-11 Pfizer FDA Advisory Committee Votes in Favor of Pfizer’s MYLOTARG (gemtuzumab ozogamicin) for Acute Myeloid Leukemia pfizer.com

Evidence & citations 11 cited values

Every value below carries the sentence it was read from. 99 sources stand behind the page.

FieldValueCited text
Known as Gemtuzumab-Ozogamicin “We tested MCMs and standard statistical models using data from a clinical trial comparing gemtuzumab ozogamicin (GO) + standard chemotherapy against standard chemotherapy alone...” PMID 33858190 Apr 2021
90

“Gemtuzumab Ozogamicin (GO) is a therapeutic CD33 antibody linked to a strong cytostatic drug (calicheamicin) which causes apoptosis of cancer cells upon internalization.” NCT04385290

“Gemtuzumab ozogamicin (GO) remained available to US clinicians through an open-label expanded-access protocol (NCT02312037) until GO was reapproved.” PMID 32432489 May 2020

“Upon HSC engraftment, patients will be treated with escalating doses of the anti-CD33 antibodydrug conjugate Gemtuzumab-Ozogamicin (GO).” NCT05662904

“Gemtuzumab ozogamicin (Mylotarg ®) is an immunoconjugate between anti-CD33 antibody and a cytotoxic antitumor antibiotic, calicheamicin.” NCT01698879

“GEMTUZUMAB OZOGAMICIN (Mylotarg): 5 mg, single dose 500 FS in 4 h - 6” NCT00909168

“Gemtuzumab ozogamicin (GO) 3 mg/m2 IV on day 1.” NCT00136084

“Mylotarg (gemtuzumab ozogamicin, or GO)” NCT02272478

“gemtuzumab ozogamicin” NCT04849910

“Gemtuzumab ozogamicin” NCT02665065

NCT00660036

NCT01039363

NCT00089050

NCT00049179

NCT03589729

NCT01020539

NCT03727750

NCT00895934

NCT05662904

NCT04050280

NCT00006265

NCT03531918

NCT04173585

NCT00454480

NCT03904251

NCT05558124

NCT00460447

NCT00669890

NCT06917911

NCT03878927

NCT00005962

NCT04168502

NCT00372593

NCT05955261

NCT03737955

NCT00017589

NCT00577694

NCT00551460

NCT03568994

NCT00274781

NCT03839446

NCT00037596

NCT00658814

NCT00037583

NCT00143975

NCT00003131

NCT00085709

NCT00476541

NCT04915612

NCT05564390

NCT00766116

NCT02473146

NCT01548911

NCT02117297

NCT05183035

NCT00893399

NCT03390296

NCT04070768

NCT00049517

NCT00801489

NCT00882102

NCT03672539

NCT00052299

NCT04207190

NCT00413166

NCT00022321

NCT03374332

NCT04093505

NCT00962767

NCT05904106

NCT00121303

NCT00673153

NCT00006122

NCT00233909

NCT00968071

NCT00003673

NCT03900949

NCT04326439

NCT00077116

NCT03848754

NCT04293562

NCT02221310

NCT00070174

NCT01409161

NCT00798213

NCT01869803

NCT00091234

NCT00008151

NCT02724163

NCT00044733

NCT00028899

Known as CDP-771 CDP-771NCT00801489
Known as CMA-676 “Gemtuzumab Ozogamicin (CMA-676) is a chemotherapeutic agent consisting of a recombinant humanized anti-CD33 antibody conjugated with calicheamicin, a highly potent cytotoxic...” NCT01020539
3

“Gemtuzumab Ozogamicin (CMA-676) is a chemotherapeutic agent consisting of recombinant humanized anti-CD33 antibody conjugated with calicheamicin, a highly potent cytotoxic...” NCT00669890

“A Dose Escalation And Phase II Study Of Gemtuzumab Ozogamicin (CMA-676; Mylotarg) With High-Dose Cytarabine For Patients With Refractory Or Relapsed Acute Myeloid Leukemia (AML)” NCT00006265

“gemtuzumab ozogamicin (CMA-676) with or without mitoxantrone, etoposide, cytarabine, and idarubicin in elderly patients with acute myeloid leukemia.” NCT00006122

Known as gemtuzumab Gemtuzumab ozogamicin is a monoclonal antibody, called gemtuzumab, linked to a antitumor drug, called calicheamicin” NCT00801489
1

Gemtuzumab (GO) added to the standard induction regimen of 7 days of Ara-C and 3 days of daunomycin” NCT00085709

Known as GTMZ “While gemtuzumab ozogamicin (GTMZ) is commonly used in the treatment of acute myeloid leukemia (AML) in combination with standard chemotherapy agents” PMID 18467731 May 2008
Known as Mylotarg “Phase II Study of Genasense (Bcl-2 Antisense) Combined With Mylotarg (Gemtuzumab Ozogamicin) in Elderly Patients With Relapsed Acute Myeloid Leukemia” NCT00017589
14

“GEMTUZUMAB OZOGAMICIN (MYLOTARG (TRADEMARKER)) AS A SINGLE-AGENT REGIMEN” NCT03727750

“GEMTUZUMAB OZOGAMICIN (Mylotarg): 5 mg, single dose 500 FS in 4 h - 6” NCT00909168

Mylotarg (gemtuzumab ozogamicin) Injection” NCT00044733

“Gemtuzumab Ozogamicin (Mylotarg)” NCT00893399

NCT00038831

NCT00038805

NCT04849910

NCT04793919

NCT02182596

NCT05599360

NCT01698879

NCT02272478

NCT00195000

NCT00304447

Known as Mylotarg (GO) Mylotarg (GO)NCT02272478
Action Deplete “can locate cancer cells and either kill them or deliver cancer-killing substances to them without harming normal cells” NCT00049179
Modality Monoclonal antibody “anti-CD33 monoclonal antibodyPMID 30062662 Mar 2019
Route Intravenous “Arm I: Patients receive cytarabine IV over 2 hours on days 1-4 and gemtuzumab ozogamicin IV over 2 hours on day 5.” NCT00005962
Target CD33 “anti-CD33 monoclonal antibody” PMID 30062662 Mar 2019