drugset / Trial / NCT00481013
Valproic Acid in Ambulant Adults With Spinal Muscular Atrophy
Phase 2
Completed
33 enrolled
University of Utah
Abbott · collabFamilies of Spinal Muscular Atrophy · collab
RandomizedCrossoverQuadruple-blindTreatment
Summary
The primary objective of this proposal is to determine whether oral VPA is effective in treating SMA in adult patients.
Timeline
- Start
- 2007-07
- Primary completion
- 2009-12
- Completion
- 2010-11
Drugs
| Evaluation | Drug | Modality | Dose | Route |
|---|---|---|---|---|
| Comparator | Valproic Acid | Small molecule | — | — |
| Comparator | L-carnitine | Other / unclassified | — | — |