drugset / Trial / NCT02845596

Unrelated Donor Transplant Versus Immune Therapy in Pediatric Severe Aplastic Anemia

NCT02845596

Completed 40 enrolled Michael Pulsipher
RandomizedParallel-groupOpen-labelOther

Summary

The purpose of this study is to determine the feasibility of comparing outcomes of patients treated de novo with immunosuppressive therapy (IST) versus matched unrelated donor (MUD) hematopoietic stem cell transplant (HSCT) for pediatric acquired severe aplastic anemia.

Timeline

Start
2016-08
Primary completion
2020-11-03
Completion
2023-07-19

Drugs

EvaluationDrugModalityDoseRoute
Comparator ANTILYMPHOCYTE IMMUNOGLOBULIN (HORSE) Protein / enzyme biologic
Comparator Cyclophosphamide Other / unclassified
Comparator Cyclosporine Peptide
Comparator Fludarabine Small molecule
Comparator Methotrexate Small molecule
Comparator Thymoglobulin Protein / enzyme biologic