drugset / Trial / NCT04224558

Stem Cell Transplantation in Crohn's Disease

NCT04224558

Phase 1/2 Recruiting 15 enrolled Cedars-Sinai Medical Center
NaSingle-groupOpen-labelTreatment

Summary

Unfortunately, some patients with Crohn's disease (CD) fail to respond to the best clinical treatments and some only experience temporary benefit. For severe Crohn's disease, there is an experimental treatment called "high dose immunoablation" followed by autologous hematopoietic stem cell transplantation (HSCT). This study removes over active lymphocytes (immunoablation) and replaces them using blood stem cells that have been taken from the patient's own body. The aim of the study is to reset or reprogram the patient's immune system to its state prior to diagnosis.

Timeline

Start
2019-11-15
Primary completion
2027-09-30
Completion
2027-09-30

Drugs

EvaluationDrugModalityDoseRoute
Subject Peripheral Blood Stem Cell Infusion Cell therapy
Background 2-MERCAPTOETHANESULFONIC ACID Small molecule
Background ANTILYMPHOCYTE IMMUNOGLOBULIN (HORSE) Protein / enzyme biologic 25 mg/kg
Background Acetaminophen Small molecule
Background Cyclophosphamide Other / unclassified 25 mg/kg Intravenous
Background Cyclophosphamide Other / unclassified 50 mg/kg Intravenous
Background Diphenhydramine Unknown
Background Fludarabine Small molecule 30 mg/m2
Background Methylprednisolone Other / unclassified
Background Thymoglobulin Protein / enzyme biologic 2.5 mg/kg Intravenous
Background filgrastim Protein / enzyme biologic 5 ug/kg Subcutaneous
Background filgrastim Protein / enzyme biologic 10 ug/kg Subcutaneous

Indications