Drugs / CPX-351
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CPX-351

Other / unclassified

Developed for
acute myeloid leukemia · myelodysplastic syndrome · therapy related acute myeloid leukemia and myelodysplastic syndrome · acute lymphoblastic leukemia · acute myeloid leukemia with multilineage dysplasia · acute myelomonocytic leukemia M4 · childhood acute myeloid leukemia · chronic myelomonocytic leukemia
+16 more · acute biphenotypic leukemia · acute erythroid leukemia · acute megakaryoblastic leukemia in adult · acute myeloblastic leukemia with maturation · acute myeloblastic leukemia without maturation · acute myeloid leukemia with 11q23 abnormalities · acute myeloid leukemia with minimal differentiation · acute myeloid leukemia with t(8;21)(q22;q22) translocation · acute myeloid leukemia, del(5q31-q32) · acute myeloid leukemia, FLT3 internal tandem duplication · acute myeloid leukemia, inv(16)(p13.1;q22) · acute myeloid leukemia, t(16;16)(p13.1;q22) · adult acute monocytic leukemia · leukemia · myelodysplastic syndrome with excess blasts-2 · myeloid neoplasm
Investigated by
Jazz Pharmaceuticals · National Cancer Institute (NCI) · M.D. Anderson Cancer Center · Weill Medical College of Cornell University · Fred Hutchinson Cancer Center · H. Lee Moffitt Cancer Center and Research Institute
+34 more · Pfizer · Acute Leukemia French Association · Case Comprehensive Cancer Center · Children's Oncology Group · Jonsson Comprehensive Cancer Center · The Leukemia and Lymphoma Society · Adienne SA · Centre Hospitalier Universitaire de Nice · Children's Hospital Medical Center, Cincinnati · Eastern Cooperative Oncology Group · French Innovative Leukemia Organisation · French Intergroup of Myeloproliferative syndromes · GWT-TUD GmbH · Gilead Sciences · Groupe Francophone des Myelodysplasies · Guenther Koehne · Masonic Cancer Center, University of Minnesota · Ohio State University Comprehensive Cancer Center · Pennsylvania Department of Health · Princess Maxima Center for Pediatric Oncology · Rondeep Brar · Roswell Park Cancer Institute · Shaare Zedek Medical Center · St. Jude Children's Research Hospital · Sudipto Mukherjee, MD, PhD, MPH · Thomas Jefferson University · University of Birmingham · University of California, Irvine · University of California, Los Angeles · University of California, San Diego · University of Nebraska · University of Ulm · Uwe Platzbecker · Washington University School of Medicine

Regulatory milestones approvals, filings & regulatory actions · 1 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved US (FDA) VYXEOS 2017-08-03 fda.gov

Trials 58 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 115 trials
Phase 1 NCT05627232 Aug 2023 → Jan 2028 expected acute myeloid leukemia Thomas Jefferson University Recruiting No outcome recorded
Phase 1 NCT05558124 Feb 2023 → Apr 2027 expected acute myeloid leukemia H. Lee Moffitt Cancer Center and Research Institute Recruiting No outcome recorded
Phase 1 NCT05024552 Feb 2022 → Feb 2027 expected acute myeloid leukemia, FLT3 internal tandem duplication H. Lee Moffitt Cancer Center and Research Institute Recruiting No outcome recorded
Phase 1 NCT04915612 May 2021 → Jan 2025 acute myeloid leukemia M.D. Anderson Cancer Center Completed No outcome recorded
Phase 1 NCT07156435 Nov 2020 → Dec 2026 expected childhood acute myeloid leukemia Princess Maxima Center for Pediatric Oncology Recruiting No outcome recorded
Phase 1 NCT04075747 Dec 2019 → Feb 2022 acute myeloid leukemia Jazz Pharmaceuticals Completed No outcome recorded
Phase 1 NCT04038437 Oct 2019 → Apr 2022 acute myeloid leukemia Jazz Pharmaceuticals Completed No outcome recorded
Phase 1 NCT03878927 Aug 2019 → Aug 2022 acute myeloid leukemia Weill Medical College of Cornell University Terminated No outcome recorded
Phase 1 NCT03904251 Jul 2019 → Oct 2023 acute myeloid leukemia Jonsson Comprehensive Cancer Center Terminated No outcome recorded
Phase 1 NCT03896269 May 2019 → Dec 2027 expected chronic myelomonocytic leukemia, myelodysplastic syndrome M.D. Anderson Cancer Center Recruiting No outcome recorded
Phase 1/27 trials
Phase 1/2 NCT07008638 Jul 2025 → Dec 2027 expected acute myeloid leukemia Masonic Cancer Center, University of Minnesota Recruiting No outcome recorded
Phase 1/2 NCT04982354 Jul 2022 → Aug 2031 acute myeloid leukemia Guenther Koehne Withdrawn No outcome recorded
Phase 1/2 NCT04049539 Jan 2021 → Dec 2026 expected acute myeloid leukemia Ohio State University Comprehensive Cancer Center Recruiting No outcome recorded
Phase 1/2 NCT04128748 May 2020 → Dec 2027 expected acute myeloid leukemia, myelodysplastic syndrome M.D. Anderson Cancer Center Active not recruiting No outcome recorded
Phase 1/2 NCT04273802 Apr 2020 → Aug 2021 myelodysplastic syndrome Groupe Francophone des Myelodysplasies Completed No outcome recorded
Phase 1/2 NCT03844997 Jun 2019 → Jan 2024 acute myeloid leukemia Sudipto Mukherjee, MD, PhD, MPH Completed No outcome recorded
Phase 1/2 NCT02642965 May 2016 → Dec 2018 childhood acute myeloid leukemia, therapy related acute myeloid leukemia and myelodysplastic syndrome Children's Oncology Group Completed No outcome recorded
Phase 230 trials
Phase 2 NCT05554419 Jul → Aug 2026 overdue therapy related acute myeloid leukemia and myelodysplastic syndrome National Cancer Institute (NCI) Not yet recruiting No outcome recorded
Phase 2 NCT05628623 Oct 2024 → Feb 2026 overdue acute myeloid leukemia Eastern Cooperative Oncology Group Not yet recruiting No outcome recorded
Phase 2 NCT05554406 Sep 2024 → Mar 2027 expected acute myeloid leukemia with multilineage dysplasia, therapy related acute myeloid leukemia and myelodysplastic syndrome National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 2 NCT05564390 Jun 2024 → May 2029 expected acute myeloid leukemia with multilineage dysplasia, myelodysplastic syndrome, therapy related acute myeloid leukemia and myelodysplastic syndrome National Cancer Institute (NCI) Recruiting No outcome recorded
Phase 2 NCT05829434 Mar 2024 → Aug 2028 acute myeloid leukemia, myelodysplastic syndrome Uwe Platzbecker Withdrawn No outcome recorded
Phase 2 NCT05260528 May 2023 → Aug 2028 expected acute myeloid leukemia Centre Hospitalier Universitaire de Nice Recruiting No outcome recorded
Phase 2 NCT05656248 Jan 2023 → Aug 2025 overdue myeloid neoplasm St. Jude Children's Research Hospital Active not recruiting No outcome recorded
Phase 2 NCT05599360 Aug 2022 → Sep 2028 expected acute myeloid leukemia Shaare Zedek Medical Center Active not recruiting No outcome recorded
Phase 2 NCT04992949 Mar 2022 → Oct 2023 acute myeloid leukemia French Innovative Leukemia Organisation Completed No outcome recorded
Phase 2 NCT04526288 Aug 2021 → Aug 2023 acute myeloid leukemia, myelodysplastic syndrome with excess blasts-2 Fred Hutchinson Cancer Center Terminated No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT04217278 Jan 2020 → May 2026 overdue acute myeloid leukemia, myelodysplastic syndrome University of Birmingham Active not recruiting No outcome recorded
Phase 33 trials
Phase 3 NCT04293562 Jul 2020 → Jun 2029 expected acute myeloid leukemia Children's Oncology Group Recruiting No outcome recorded
Phase 3 NCT03897127 Sep 2019 → Jun 2027 expected acute myeloid leukemia University of Ulm Active not recruiting No outcome recorded
Phase 3 NCT01696084 Dec 2012 → Dec 2015 acute myeloid leukemia Jazz Pharmaceuticals Completed No outcome recorded
Phase not applicable1 trial
NCT01804101 May 2013 → Jan 2017 acute biphenotypic leukemia, myelodysplastic syndrome Fred Hutchinson Cancer Center Completed No outcome recorded
Phase not stated1 trial
NCT02533115 acute myeloid leukemia Jazz Pharmaceuticals Approved for marketing No outcome recorded
Also used as a comparator or background therapy in 4 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 1/21 trial
Phase 1/2 NCT05320380 Background Aug → Sep 2023 B-cell acute lymphoblastic leukemia, T-cell acute lymphoblastic leukemia, mixed phenotype acute leukemia Children's Oncology Group Withdrawn No outcome recorded
Phase 21 trial
Phase 2 NCT04802161 Background Aug 2022 → Nov 2024 overdue acute myeloid leukemia with multilineage dysplasia, chronic myelomonocytic leukemia, myelodysplastic syndrome, therapy related acute myeloid leukemia and myelodysplastic syndrome National Cancer Institute (NCI) Active not recruiting No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT02272478 Comparator Oct 2014 → Feb 2021 acute myeloid leukemia, myelodysplastic syndrome Cardiff University Unknown No outcome recorded
Phase 41 trial
Phase 4 NCT03988205 Background Aug 2019 → Dec 2021 acute myeloid leukemia Medical College of Wisconsin Terminated No outcome recorded

Evidence & citations 9 cited values

Every value below carries the sentence it was read from. 64 sources stand behind the page.

FieldValueCited text
Known as CPX-351 “This phase II trial studies the effect of CPX-351 followed by donor stem cell transplantation versus immediate donor stem cell transplantation in treating patients with...” NCT04526288
48

“We aimed to evaluate the safety and preliminary activity of lower doses of CPX-351, a liposomal encapsulation of cytarabine and daunorubicin, in a single-centre, phase 1/2...” PMID 37946611 Nov 2023

“This phase II trial studies the best dose and how well liposomal cytarabine-daunorubicin CPX-351 (CPX-351) works in treating patients with newly diagnosed acute myeloid leukemia” NCT02286726

“A Phase 1/2 Study of CPX-351 (NSC# 775341) Alone Followed by Fludarabine, Cytarabine, and G-CSF (FLAG) for Children With Relapsed Acute Myeloid Leukemia (AML).” NCT02642965

“This phase II trial studies how well liposome-encapsulated daunorubicin-cytarabine (CPX-351) works in treating patients with secondary acute myeloid leukemia” NCT04269213

“This phase Ib trial studies the best dose of gemtuzumab ozogamicin when given together with CPX-351 in treating patients with acute myeloid leukemia” NCT03904251

“Patients receive CPX-351 intravenously (IV) over 90 minutes on days 1, 3, and 5 in the absence of disease progression or unacceptable toxicity.” NCT04195945

“Induction 1:CPX-351 44 mg/m2 daunorubicin / 100 mg/m2 cytarabine i.v. (90 min) d1,3,5” NCT05260528

“The liposomal formulation of Vyxeos®/CPX-351 may be a suitable replacement for DNX” NCT07156435

“Patients receive CPX-351 intravenously (IV) over 90 minutes on days 1, 3, and 5” NCT04493164

“A Phase 2 Trial of CPX-351 Combined With Venetoclax in Relapsed or Refractory” PMID 40401707 May 2025

“Liposomal Cytarabine and Daunorubicin (CPX-351) and Quizartinib” NCT04128748

“liposome-encapsulated daunorubicin-cytarabine (CPX-351)” NCT03825796

“Vyxeos (CPX-351, cytarabine and daunorubicin liposome)” NCT03826992

CPX-351 is made up of daunorubicin and cytarabine” NCT04293562

“liposomal cytarabine and daunorubicin (CPX-351)” NCT03672539

“liposomal cytarabine and daunorubicin (CPX-351)” NCT04915612

CPX-351NCT02019069

NCT03878927

NCT02019069

NCT05829434

NCT04075747

NCT04992949

NCT04231851

NCT03572764

NCT00875693

NCT02272478

NCT03988205

NCT00788892

NCT03555955

NCT03575325

NCT04982354

NCT03844997

NCT02269579

NCT02533115

NCT05656248

NCT04061239

NCT04038437

NCT03897127

NCT01696084

NCT04273802

NCT05628623

NCT00822094

NCT07008638

NCT03335267

NCT03393611

NCT03957876

NCT02238925

NCT04668885

Known as liposomal cytarabine-daunorubicin “This phase 2 clinical trial studies how well CPX-351 (liposomal cytarabine-daunorubicin) works in treating patients with relapsed or refractory acute myeloid leukemia or...” NCT02019069
Known as Liposomal Cytarabine-Daunorubicin CPX-351 ClinicalTrials.gov intervention name — accepted as the source's own label NCT01804101
Known as liposome-encapsulated daunorubicin-cytarabine “PRIMARY OBJECTIVES: I. To determine the phase II dose of the combination liposome-encapsulated daunorubicin-cytarabine (CPX-351) plus gemtuzumab ozogamicin (GO) by means of...” NCT03904251
7

NCT03226418

NCT05564390

NCT05627232

NCT04802161

NCT05320380

NCT05554406

NCT05554419

Known as NSC# 775341 “A Phase 1/2 Study of CPX-351 (NSC# 775341) Alone Followed by Fludarabine, Cytarabine, and G-CSF (FLAG) for Children With Relapsed Acute Myeloid Leukemia (AML).” NCT02642965
Known as VYXEOS “CPX-351 (Europe: Vyxeos® liposomal; United States: Vyxeos®) is a dual-drug liposomal encapsulation of daunorubicin and cytarabine in a synergistic 1:5 molar ratio.” PMID 36289532 Oct 2022
10

Vyxeos is a combination of both chemotherapy drugs cytarabine and daunorubicin contained in a liposome.” NCT04049539

“CPX-351 (Vyxeos™) for Transplant Eligible, Higher Risk Patients With Myelodysplastic Syndrome” NCT03572764

“The liposomal formulation of Vyxeos®/CPX-351 may be a suitable replacement for DNX” NCT07156435

“EAP of CPX-351 (VYXEOS) for Patients 60-75 Years of Age With Secondary AML” NCT02533115

NCT05024552

NCT04425655

NCT04217278

NCT05599360

NCT03826992

NCT05558124

Known as Vyxeos liposomal “CPX-351 (Europe: Vyxeos® liposomal; United States: Vyxeos®) is a dual-drug liposomal encapsulation of daunorubicin and cytarabine in a synergistic 1:5 molar ratio.” PMID 36289532 Oct 2022
Modality Other / unclassified “CPX-351 is a liposomal formulation of cytarabine:daunorubicin designed to deliver synergistic drug ratios to leukemia cells.” PMID 24687088 Mar 2014
Route Intravenous “by 90-minute IV infusion” NCT00822094