Drugs / Lonafarnib
last change Mar 2026 re-read 2 minutes ago

Lonafarnib

also known as SCH66336 · SARASAR · LNF · SCH 066336 · SCH 663366 · SCH 6636 · Zokinvy

Small molecule

Developed for
hepatitis D virus infection · breast cancer · Hutchinson-Gilford progeria syndrome · central nervous system neoplasm · chronic myeloid leukemia · gliosarcoma · head and neck cancer · myelodysplastic syndrome
+26 more · neoplasm · anaplastic astrocytoma · blast phase chronic myelogenous leukemia, BCR-ABL1 positive · cancer of unknown primary site · chronic myelomonocytic leukemia · colorectal cancer · gastric cancer · glioblastoma · head and neck squamous cell carcinoma · liver cancer · lung cancer · lymphoid leukemia · lymphoma · malignant epithelial tumor of ovary · metastatic malignant neoplasm · metastatic neoplasm · non-small cell lung carcinoma · ovarian cancer · prostate cancer · renal pelvis/ureter urothelial carcinoma · squamous cell carcinoma · supratentorial cancer · urethra cancer · urinary bladder cancer · colorectal carcinoma · soft tissue sarcoma
Investigated by
Merck Sharp & Dohme LLC · Eiger BioPharmaceuticals · M.D. Anderson Cancer Center · Schering-Plough · National Cancer Institute (NCI) · National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
+15 more · European Organisation for Research and Treatment of Cancer - EORTC · Boston Children's Hospital · AGO Study Group · Ankara University · Brigham and Women's Hospital · Dana-Farber Cancer Institute · Duke University · George Sledge · Hannover Medical School · Hoosier Cancer Research Network · Jonsson Comprehensive Cancer Center · Memorial Sloan Kettering Cancer Center · Monica E. Kleinman · Pediatric Brain Tumor Consortium · Soroka University Medical Center

Regulatory milestones approvals, filings & regulatory actions · 2 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved EU (EMA) Zokinvy 2022-07-18 europa.eu
Approved US (FDA) ZOKINVY 2020-11-20 fda.gov

Trials 37 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 112 trials
Phase 1 NCT00612651 Oct 2005 → Jan 2009 anaplastic astrocytoma, gliosarcoma Duke University Completed No outcome recorded
Phase 1 NCT00102635 Jan 2005 → Jan 2006 head and neck cancer M.D. Anderson Cancer Center Terminated No outcome recorded
Phase 1 NCT00102648 Dec 2004 → Mar 2025 overdue gliosarcoma, supratentorial cancer M.D. Anderson Cancer Center Active not recruiting No outcome recorded
Phase 1 NCT00083096 Mar 2004 → Jun 2009 central nervous system neoplasm European Organisation for Research and Treatment of Cancer - EORTC Unknown No outcome recorded
Phase 1 NCT00068757 Aug 2003 → Nov 2007 breast cancer European Organisation for Research and Treatment of Cancer - EORTC Completed No outcome recorded
Phase 1 NCT00047502 Nov 2002 → Apr 2006 chronic myeloid leukemia M.D. Anderson Cancer Center Completed No outcome recorded
Phase 1 NCT00015899 Jan 2002 → Sep 2005 central nervous system neoplasm Pediatric Brain Tumor Consortium Completed No outcome recorded
Phase 1 NCT00040547 Jun 2001 → Feb 2004 neoplasm Merck Sharp & Dohme LLC Completed No outcome recorded
Phase 1 NCT00040534 Jan 2001 → Jul 2004 neoplasm Merck Sharp & Dohme LLC Terminated No outcome recorded
Phase 1 NCT00005030 Sep 1999 → Sep 2000 colorectal cancer, metastatic malignant neoplasm M.D. Anderson Cancer Center Withdrawn No outcome recorded
Phase 1/22 trials
Phase 1/2 NCT00539968 Jun 2007 → Dec 2009 breast cancer, gastric cancer, lung cancer, ovarian cancer +1 Merck Sharp & Dohme LLC Terminated No outcome recorded
Phase 1/2 NCT00034684 Jul 2001 → Oct 2003 blast phase chronic myelogenous leukemia, BCR-ABL1 positive, lymphoid leukemia, myelodysplastic syndrome Merck Sharp & Dohme LLC Completed No outcome recorded
Phase 218 trials
Phase 2 NCT05953545 May 2024 hepatitis D virus infection National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) Withdrawn No outcome recorded
Phase 2 NCT03600714 Aug 2018 → Feb 2020 hepatitis D virus infection National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) Completed No outcome recorded
Phase 2 NCT02527707 Sep 2015 → Aug 2016 hepatitis D virus infection Eiger BioPharmaceuticals Completed No outcome recorded
Phase 2 NCT02511431 Jul 2015 → Feb 2017 hepatitis D virus infection National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) Completed No outcome recorded
Phase 2 NCT02430194 Dec 2014 → Apr 2017 hepatitis D virus infection Eiger BioPharmaceuticals Completed No outcome recorded
Phase 2 NCT02430181 Nov 2014 → Sep 2015 hepatitis D virus infection Eiger BioPharmaceuticals Completed No outcome recorded
Phase 2 NCT01495585 Dec 2011 → Apr 2015 hepatitis D virus infection National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) Completed No outcome recorded
Phase 2 NCT00916747 Aug 2009 → Feb 2022 Hutchinson-Gilford progeria syndrome Boston Children's Hospital Unknown No outcome recorded
Phase 2 NCT00879034 Mar → Apr 2009 Hutchinson-Gilford progeria syndrome Boston Children's Hospital Completed No outcome recorded
Phase 2 NCT00773474 Oct 2008 → Nov 2010 breast cancer George Sledge Terminated No outcome recorded
Phase 34 trials
Phase 3 NCT05229991 May 2021 → Feb 2025 hepatitis D virus infection Soroka University Medical Center Completed No outcome recorded
Phase 3 NCT03719313 Dec 2018 → Oct 2022 hepatitis D virus infection Eiger BioPharmaceuticals Completed No outcome recorded
Phase 3 NCT00109538 May 2005 → Aug 2008 chronic myelomonocytic leukemia, myelodysplastic syndrome Merck Sharp & Dohme LLC Terminated No outcome recorded
Phase 3 NCT00050336 Dec 2002 → Feb 2004 metastatic neoplasm, non-small cell lung carcinoma Merck Sharp & Dohme LLC Terminated No outcome recorded
Phase not stated1 trial
NCT03895528 Hutchinson-Gilford progeria syndrome Eiger BioPharmaceuticals Approved for marketing No outcome recorded
Also used as a comparator or background therapy in 4 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT00288444 Comparator Jan 2006 → May 2008 breast cancer, colorectal carcinoma, lung cancer, prostate cancer +1 Emory University Terminated No outcome recorded
Phase 1/21 trial
Phase 1/2 NCT02579044 Background Dec 2015 → Mar 2027 expected Hutchinson-Gilford progeria syndrome Boston Children's Hospital Enrolling by invitation No outcome recorded
Phase 22 trials
Phase 2 NCT06775041 Background Jan 2025 → Mar 2026 overdue Hutchinson-Gilford progeria syndrome PRG Science & Technology Co., Ltd. Active not recruiting No outcome recorded
Phase 2 NCT02968641 Comparator ? → Feb 2021 hepatitis D virus infection Eiger BioPharmaceuticals Withdrawn No outcome recorded

Evidence & citations 11 cited values

Every value below carries the sentence it was read from. 45 sources stand behind the page.

FieldValueCited text
Known as Lonafarnib “A phase I safety, pharmacological, and biological study of the farnesyl protein transferase inhibitor, lonafarnib (SCH 663366), in combination with cisplatin and gemcitabine in...” PMID 18058098 Dec 2007
32

“This is an open-label clinical trial treating 30 adult patients with chronic delta hepatitis with peginterferon lambda and lonafarnib boosted with ritonavir for 48 weeks.” NCT05953545

“A phase II study of Lonafarnib (SCH66336) in patients with chemorefractory, advanced squamous cell carcinoma of the head and neck.” PMID 19433965 Jun 2009

NCT03895528

NCT00050336

NCT00068757

NCT00425607

NCT00006351

NCT03719313

NCT00020774

NCT00916747

NCT02579044

NCT02511431

NCT02968641

NCT00773474

NCT02430181

NCT02527707

NCT00081510

NCT00281515

NCT00109538

NCT00288444

NCT00083096

NCT03600714

NCT01495585

NCT00015899

NCT02430194

NCT00003956

NCT00102648

NCT06775041

NCT00879034

NCT00539968

NCT00047502

NCT05229991

Known as LNF “We propose to treat 21 adult patients with chronic delta hepatitis using the combination of the farnesyltransferase inhibitor (FTI) lonafarnib (LNF) and the protease inhibitor...” NCT02511431
Known as SARASAR “Docetaxel (Taxotere®); lonafarnib (SCH 066336, Sarasar®)” NCT00539968
1

“Lonafarnib (SARASAR)” NCT00050336

Known as SCH 066336 “Docetaxel (Taxotere®); lonafarnib (SCH 066336, Sarasar®)” NCT00539968
Known as SCH 663366 “A phase I safety, pharmacological, and biological study of the farnesyl protein transferase inhibitor, lonafarnib (SCH 663366), in combination with cisplatin and gemcitabine in...” PMID 18058098 Dec 2007
Known as SCH 6636 “Farnesyl Protein Transferase Inhibitor (Lonafarnib/SCH 6636)” NCT00073450
Known as SCH66336 “The purpose of this study is to determine the safety and tolerability of an oral Farnesyl Protein Transferase Inhibitor (SCH 66336) as a single agent in patients with Advanced...” NCT00034684
11

“The purpose of this study is to determine the safety and tolerability of an oral Farnesyl Protein Transferase Inhibitor (SCH 66336) when given in combination with intravenous...” NCT00040547

“A phase II study of Lonafarnib (SCH66336) in patients with chemorefractory, advanced squamous cell carcinoma of the head and neck.” PMID 19433965 Jun 2009

“Phase I Study of Lonafarnib (SCH66336) in Combination With Herceptin Plus Paclitaxel in HER 2 NEU Overexpressing Breast Cancer” NCT00068757

“Phase I Study Of SCH66336 (Lonafarnib), A Farnesyl Protein Transferase Inhibitor In Combination With Temozolomide In Gliomas” NCT00083096

“Lonafarnib/SCH 66336” NCT00050336

NCT00038597

NCT00038584

NCT00005030

NCT00038493

NCT00612651

NCT00102635

Known as Zokinvy “FDA approval summary for lonafarnib (Zokinvy) for the treatment of Hutchinson-Gilford progeria syndrome and processing-deficient progeroid laminopathies.” PMID 36507973 Dec 2022
Action Inhibit “the farnesyl transferase inhibitor SCH66336” PMID 15911238 May 2005
Modality Small molecule “SCH66336, A Farnesyltransferase Inhibitor” NCT00038597
1

CHEMBL298734

Route Oral “Patients receive oral SCH 66336 twice daily for 7-14 days prior to exploratory laparotomy and/or resection of hepatic metastases.” NCT00005030