Drugs / Deferasirox
last change Jun 2026 re-read 2 minutes ago

Deferasirox

Developed for
disorder of iron metabolism and transport · myelodysplastic syndrome · hemosiderosis · beta-thalassemia major · sickle cell disease · thalassemia · beta thalassemia · anemia
+14 more · acute myeloid leukemia · Diamond-Blackfan anemia · hereditary hemochromatosis · aplastic anemia · myelofibrosis · porphyria cutanea tarda · acute lymphoblastic leukemia · beta-thalassemia and related diseases · disease related to hematopoietic stem cell transplant · Fanconi renotubular syndrome · inherited hemoglobinopathy · metabolic dysfunction-associated steatohepatitis · postmenopausal osteoporosis · Zygomycosis
Investigated by
Novartis Pharmaceuticals · Novartis · National Cancer Institute (NCI) · Abramson Cancer Center at Penn Medicine · Academic Medical Center - University of Amsterdam · Ann & Robert H Lurie Children's Hospital of Chicago
+39 more · Assistance Publique - Hôpitaux de Paris · Association pour l'Etude des Fonctions Digestives (AEFD) · Astellas Pharma Inc · Boston Children's Hospital · Children's Hospital Los Angeles · Children's Hospital of Philadelphia · China Medical University Hospital · City of Hope Medical Center · Crolll Gmbh · Elizabeth Henry · Elliott Vichinsky · Estimate, GmbH · Fondazione Italiana Sindromi Mielodisplastiche-ETS · Fred Hutchinson Cancer Center · GIMEMA Foundation · Gilead Sciences · Groupe Francophone des Myelodysplasies · Hadassah Medical Organization · Hormozgan University of Medical Sciences · Inova Health Care Services · Isfahan University of Medical Sciences · Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center · Masonic Cancer Center, University of Minnesota · RESnTEC, Institute of Research · Second Affiliated Hospital of Soochow University · Sheba Medical Center · Soroka University Medical Center · Sunnybrook Health Sciences Centre · Tel-Aviv Sourasky Medical Center · The Cooley's Anemia Foundation, · The First Affiliated Hospital of Zhejiang Chinese Medical University · University Hospital, Grenoble · University of Erlangen-Nürnberg Medical School · University of Magdeburg · University of Michigan Rogel Cancer Center · University of Texas Southwestern Medical Center · Wake Forest University Health Sciences · Weill Medical College of Cornell University · Wolfson Medical Center

Regulatory milestones approvals, filings & regulatory actions · 10 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Label expansions (5) US (FDA) JADENU SPRINKLE 2018-05-11 – 2020-07-23 fda.gov
Label expansion US (FDA) JADENU 2019-07-26 fda.gov
Label expansions (2) US (FDA) EXJADE 2013-01-23 – 2019-07-24 fda.gov
Approved EU (EMA) Exjade 2006-08-28 europa.eu
Approved US (FDA) EXJADE 2005-11-02 fda.gov

Trials 83 · started per year

today
US approved 2005
EU approved 2006
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20022003200420052006200720082009201020112012201320142015201620172018201920202021202220232024202520262027
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 01 trial
Phase 0 NCT02233504 Aug 2014 → Oct 2017 acute myeloid leukemia Abramson Cancer Center at Penn Medicine Completed No outcome recorded
Phase 15 trials
Phase 1 NCT02413021 May → Aug 2016 acute lymphoblastic leukemia, acute myeloid leukemia Isfahan University of Medical Sciences Unknown No outcome recorded
Phase 1 NCT00560820 Sep 2007 → Apr 2012 beta thalassemia, disorder of iron metabolism and transport Novartis Pharmaceuticals Completed No outcome recorded
Phase 1 NCT00419172 Jan 2007 → ? Novartis Completed No outcome recorded
Phase 1 NCT00432627 Dec 2006 → Aug 2010 Novartis Pharmaceuticals Completed No outcome recorded
Phase 1 NCT00427505 Jul 2006 → ? Novartis Completed No outcome recorded
Phase 1/25 trials
Phase 1/2 NCT01718366 Feb 2013 → Feb 2019 myelodysplastic syndrome Groupe Francophone des Myelodysplasies Unknown No outcome recorded
Phase 1/2 NCT01709032 Sep 2012 → Aug 2015 beta-thalassemia major Children's Hospital of Philadelphia Completed No outcome recorded
Phase 1/2 NCT01278056 Mar 2010 → Mar 2012 disorder of iron metabolism and transport, metabolic dysfunction-associated steatohepatitis Crolll Gmbh Completed No outcome recorded
Phase 1/2 NCT00738413 Aug 2008 → Sep 2009 thalassemia Weill Medical College of Cornell University Unknown No outcome recorded
Phase 1/2 NCT00395629 Aug 2006 → Dec 2007 hereditary hemochromatosis Novartis Pharmaceuticals Completed No outcome recorded
Phase 240 trials
Phase 2 NCT06784336 Oct 2025 → Oct 2028 expected disease related to hematopoietic stem cell transplant University of Michigan Rogel Cancer Center Recruiting No outcome recorded
Phase 2 NCT07023666 Oct 2025 → Jun 2026 overdue sickle cell disease Inova Health Care Services Recruiting No outcome recorded
Phase 2 NCT05392101 Jul 2021 → Aug 2022 sickle cell disease Academic Medical Center - University of Amsterdam Completed No outcome recorded
Phase 2 NCT03920657 Oct 2019 → Oct 2020 myelodysplastic syndrome Fondazione Italiana Sindromi Mielodisplastiche-ETS Terminated No outcome recorded
Phase 2 NCT03387475 Feb 2018 → Oct 2024 myelodysplastic syndrome University Hospital, Grenoble Completed No outcome recorded
Phase 2 NCT02854722 Jan 2018 → Jun 2019 postmenopausal osteoporosis Second Affiliated Hospital of Soochow University Unknown No outcome recorded
Phase 2 NCT03203850 Jan 2018 → Apr 2023 hereditary hemochromatosis Novartis Pharmaceuticals Terminated No outcome recorded
Phase 2 NCT02993224 Jul 2017 → Jan 2020 inherited hemoglobinopathy Novartis Pharmaceuticals Completed No outcome recorded
Phase 2 NCT02943668 Mar 2017 → Dec 2018 anemia, myelodysplastic syndrome Fred Hutchinson Cancer Center Terminated No outcome recorded
Phase 2 NCT02663752 May → Jul 2016 myelodysplastic syndrome Novartis Pharmaceuticals Terminated No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT01033747 Feb 2003 → Jan 2008 disorder of iron metabolism and transport Novartis Pharmaceuticals Completed No outcome recorded
Phase 39 trials
Phase 3 NCT02720536 Aug 2016 → Jul 2019 disorder of iron metabolism and transport Novartis Pharmaceuticals Completed No outcome recorded
Phase 3 NCT00981370 Apr 2009 → Oct 2010 hemosiderosis, sickle cell disease Children's Hospital Los Angeles Terminated No outcome recorded
Phase 3 NCT00599326 Jan 2008 → Apr 2010 porphyria cutanea tarda University of Texas Southwestern Medical Center Completed No outcome recorded
Phase 3 NCT00469560 Jun 2007 → Mar 2010 hemosiderosis, myelodysplastic syndrome GIMEMA Foundation Completed No outcome recorded
Phase 3 NCT00235391 Oct 2005 → Oct 2008 Diamond-Blackfan anemia, myelofibrosis, sickle cell disease, thalassemia Novartis Pharmaceuticals Completed No outcome recorded
Phase 3 NCT00171821 Apr 2005 → May 2009 disorder of iron metabolism and transport Novartis Pharmaceuticals Completed No outcome recorded
Phase 3 NCT00171210 Oct 2004 → Apr 2008 beta-thalassemia and related diseases Novartis Pharmaceuticals Completed No outcome recorded
Phase 3 NCT00171171 May 2004 → Nov 2006 beta thalassemia, hemosiderosis Novartis Completed No outcome recorded
Phase 3 NCT00061750 May 2003 → Nov 2004 beta thalassemia Novartis Pharmaceuticals Completed No outcome recorded
Phase 418 trials
Phase 4 NCT03372083 Jan 2018 → Dec 2019 hemosiderosis Novartis Pharmaceuticals Completed No outcome recorded
Phase 4 NCT02069886 Dec 2014 → Dec 2018 thalassemia Novartis Pharmaceuticals Withdrawn No outcome recorded
Phase 4 NCT01818726 Jun 2014 → Oct 2016 aplastic anemia Novartis Pharmaceuticals Terminated No outcome recorded
Phase 4 NCT01610297 Sep 2013 → Oct 2015 beta-thalassemia major Novartis Pharmaceuticals Completed No outcome recorded
Phase 4 NCT01724138 Jun 2013 → Apr 2014 beta-thalassemia major Novartis Pharmaceuticals Withdrawn No outcome recorded
Phase 4 NCT01709838 Dec 2012 → Jan 2015 thalassemia Novartis Pharmaceuticals Completed No outcome recorded
Phase 4 NCT01326845 Dec 2011 → Sep 2012 disorder of iron metabolism and transport, myelodysplastic syndrome Novartis Pharmaceuticals Terminated No outcome recorded
Phase 4 NCT01250951 Dec 2009 → Jul 2011 myelodysplastic syndrome, thalassemia Novartis Pharmaceuticals Completed No outcome recorded
Phase 4 NCT00845871 May 2009 → Aug 2010 hemosiderosis Novartis Pharmaceuticals Completed No outcome recorded
Phase 4 NCT01335035 Dec 2008 → May 2011 disorder of iron metabolism and transport Novartis Pharmaceuticals Completed No outcome recorded
Phase not applicable4 trials
NCT06964971 May 2025 → May 2027 expected aplastic anemia The First Affiliated Hospital of Zhejiang Chinese Medical University Not yet recruiting No outcome recorded
NCT06468423 Jan → Sep 2023 beta-thalassemia major RESnTEC, Institute of Research Completed No outcome recorded
NCT01369719 Feb 2010 → Jan 2011 disorder of iron metabolism and transport, thalassemia Hormozgan University of Medical Sciences Completed No outcome recorded
NCT02198508 Jul 2007 → Jul 2008 beta-thalassemia major China Medical University Hospital Completed No outcome recorded
Also used as a comparator or background therapy in 12 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 25 trials
Phase 2 NCT07292259 Background Jan 2024 → Dec 2025 beta-thalassemia major Pakistan Blood and Marrow Transplant (PBMT) Group Completed No outcome recorded
Phase 2 NCT03637556 Comparator Aug 2019 → Jun 2021 beta-thalassemia major DisperSol Technologies, LLC Completed No outcome recorded
Phase 2 NCT01927913 Comparator Nov 2014 → Oct 2015 beta thalassemia, disorder of iron metabolism and transport, hemosiderosis Shire Withdrawn No outcome recorded
Phase 2 NCT02125877 Comparator Jul 2014 → Feb 2016 disorder of iron metabolism and transport Novartis Pharmaceuticals Completed No outcome recorded
Phase 2 NCT01892644 Comparator May 2013 → Jan 2017 hereditary hemochromatosis, myelodysplastic syndrome Haukeland University Hospital Withdrawn No outcome recorded
Phase 2/32 trials
Phase 2/3 NCT02065492 Background Feb 2014 → Oct 2015 thalassemia Aga Khan University Completed No outcome recorded
Phase 2/3 NCT01511848 Comparator Feb 2012 → Feb 2013 beta-thalassemia major, hemosiderosis, sickle cell disease Ain Shams University Unknown No outcome recorded
Phase 32 trials
Phase 3 NCT07157722 Comparator Aug → Dec 2025 overdue beta thalassemia Tanta University Not yet recruiting No outcome recorded
Phase 3 NCT01825512 Comparator Mar 2014 → Sep 2017 disorder of iron metabolism and transport Consorzio per Valutazioni Biologiche e Farmacologiche Completed No outcome recorded
Phase not applicable3 trials
NCT02761395 Background Nov 2015 → May 2017 beta-thalassemia major Tanta University Unknown No outcome recorded
NCT02474420 Background Jun 2015 → Jun 2017 beta thalassemia, disorder of iron metabolism and transport Kevin H.M. Kuo, MD, MSc, FRCPC Unknown No outcome recorded
NCT01349699 Comparator Feb → May 2010 anemia, autoinflammatory syndrome Radboud University Medical Center Completed No outcome recorded

Press releases naming this drug 1 release

DateIssuerRelease
2019-03-22 Teva Branded Pharmaceutical Products R&D, Inc. Teva Announces Launch of a Generic Version of EXJADE® (deferasirox) Tablets For Oral Suspension in the United States tevapharm.com

Evidence & citations 12 cited values

Every value below carries the sentence it was read from. 101 sources stand behind the page.

FieldValueCited text
Known as Deferasirox “Patients will receive Iron chelation with deferasirox (Jadenu 7 mg/kg/day preferred versus Exjade 10 mg/kg/day) beginning on day -14 and continuing through day +100” NCT06784336
83

“This will comprise of standard chelation drugs (Deferasirox or Deferoxamine or Combination of Deferoxamine and Deferiprone).” NCT02065492

“Patients will also continue the iron chelation therapy (Deferasirox, Deferiprone or Deferoxamine) in case of iron overload.” NCT07292259

“oral iron chelator Deferasirox -Exjade” NCT00452660

NCT02341495

NCT01868477

NCT00599326

NCT00419172

NCT06468423

NCT00560820

NCT00171171

NCT01033747

NCT02069886

NCT01709838

NCT01159067

NCT00879242

NCT00110266

NCT02474420

NCT01892644

NCT00981370

NCT01709032

NCT00110617

NCT02943668

NCT00395629

NCT01459718

NCT00469560

NCT03203850

NCT00564941

NCT00845871

NCT02663752

NCT00481143

NCT00427505

NCT07023666

NCT01058369

NCT01718366

NCT00235391

NCT00901199

NCT00171301

NCT01326845

NCT01349699

NCT00602446

NCT02993224

NCT00419770

NCT02720536

NCT01273766

NCT00600938

NCT00940602

NCT02854722

NCT02435212

NCT01250951

NCT01927913

NCT03387475

NCT00749515

NCT02198508

NCT00873041

NCT02413021

NCT00117507

NCT02159040

NCT01724138

NCT00654589

NCT01825512

NCT00738413

NCT03372083

NCT01511848

NCT02233504

NCT01948817

NCT00390858

NCT00631163

NCT00447694

NCT00171210

NCT05392101

NCT00673608

NCT06964971

NCT01254227

NCT00379483

NCT03920657

NCT02125877

NCT00303329

NCT02038816

NCT01335035

NCT00061763

NCT02761395

NCT00432627

NCT00171821

Known as Deferasirox dispersible tablet Deferasirox dispersible tablet (DFX-DT)” NCT02125877
Known as Deferasirox film-coated tablet Deferasirox film-coated tablet (DFX-FCT)” NCT02125877
Known as Deferasirox, (Exjade) Deferasirox, (Exjade)NCT00901199
Known as DFX “Comparison of safety, efficacy, compliance, treatment satisfaction, and quality of life (QoL) of two regimens: deferiprone (DFP) and deferoxamine (DFO) versus DFP and...” PMID 25600572 Mar 2015
5

“Deferasirox (DFX) monotherapy is effective for reducing myocardial and liver iron concentrations (LIC), although some patients may require intensive chelation for a limited duration.” PMID 25934475 May 2015

“combined therapy with deferasirox (DFX, 20-30 mg/kg daily) and deferoxamine (DFO, 35-50mg/kg on 3-7 days/week)” PMID 23151373 Nov 2012

“Deferasirox DFX, DT” NCT01868477

“Deferasirox (DFX)” NCT06468423

DFX(Deferasirox)” NCT02198508

Known as DFX-DT “Deferasirox dispersible tablet (DFX-DT)” NCT02125877
Known as DFX-FCT “Deferasirox film-coated tablet (DFX-FCT)” NCT02125877
Known as Exjade “Background Following a clinical evaluation of deferasirox (Exjade) it was concluded that, in addition to baseline body iron burden, ongoing transfusional iron intake should be...” PMID 19951979 Nov 2009
8

“The THALASSA (assessment of Exjade(®) in non-transfusion-dependent THALASSemiA patients) study assessed the efficacy and safety of deferasirox in iron-overloaded NTDT patients” PMID 25212456 Sep 2014

“Patients will receive Iron chelation with deferasirox (Jadenu 7 mg/kg/day preferred versus Exjade 10 mg/kg/day) beginning on day -14 and continuing through day +100” NCT06784336

“Patient-reported outcomes of once-daily oral deferasirox (Exjade) in iron-overloaded patients with beta-thalassemia” PMID 20424435 Apr 2010

Exjade® (deferasirox, ICL670)” NCT02233504

NCT03637556

NCT01284946

NCT01278056

NCT00452660

Known as ICL670 “The study will have 2 treatment groups and will compare the safety and efficacy of chelation therapy with a medicine called deferasirox (ICL670) with another medicine called...” NCT00600938
16

“Open Label, Multicenter Study to Evaluate Safety/Tolerability and Efficacy of Deferasirox (ICL670) in Myelodysplastic Syndrome Patients With Chronic Transfusional Hemosiderosis.” NCT00469560

“Safety of Deferasirox (ICL670) and Deferoxamine (Desferal or DFO) Combined Chelation Therapy in Patients With Transfusion Dependent Thalassemia and Iron Overload” NCT00901199

“An Extension Study of Iron Chelation Therapy With Deferasirox (ICL670) in β-thalassemia Patients With Transfusional Iron Overload” NCT00171210

“Drug: Deferasirox will be orally administered at a dose of 20 mg/kg once daily at evening for 5 days. Other Name: ICL670NCT01511848

“An Open Label Trial Evaluating Cardiac T2* in Beta-thalassemia Patients on Deferasirox (ICL670) Treatment for 18 Months” NCT00447694

“Deferasirox (Exjade, ICL670) is an oral chelator with high iron-binding potency and selectivity.” NCT00171301

“Exjade® (deferasirox, ICL670)” NCT02233504

“Deferasirox (ICL670)” NCT00631163

“Deferasirox (ICL670)” NCT00395629

“Deferasirox (ICL670)” NCT00110617

NCT01610297

NCT01044186

NCT01090323

NCT00061750

NCT01818726

NCT00067080

Known as Jadenu “Patients will receive Iron chelation with deferasirox (Jadenu 7 mg/kg/day preferred versus Exjade 10 mg/kg/day) beginning on day -14 and continuing through day +100” NCT06784336
2

JADENU is indicated for the treatment of chronic iron overload due to blood transfusions.” NCT07157722

NCT03637556

Known as osveral ClinicalTrials.gov intervention name — accepted as the source's own label NCT01369719
Route Oral “The purpose of this study is to deterimine if the new orally active iron chelator, ICL670, is as effective and as safe as deferoxamine in preventing accumulation of iron in the...” NCT00061750