drugset / Trial / NCT05088356

Reduced Intensity Allogeneic HCT in Advanced Hematologic Malignancies w/T-Cell Depleted Graft

NCT05088356

Phase 1 Active not recruiting 66 enrolled Stanford University Orca Biosystems, Inc. · collab
Non-randomizedParallel-groupOpen-labelTreatment

Summary

Reduced intensity conditioning (RIC) has emerged and been increasingly adopted as a modality to allow preparative conditioning pre transplant to be tolerated by older adults or those patients that are otherwise unfit for myeloablative conditioning. In this study, we aim to use RIC followed by matched related/unrelated donor, 7/8 matched related/unrelated donor, or haploidentical donor peripheral blood stem cell transplantation. Standard strategies to control the alloreactivity following HCT utilize immunosuppressive or cytotoxic medications. In this study, we explore donor graft engineering to enrich for immmunoregulatory populations to facilitate post transplantation immune reconstitution while minimizing graft versus host disease (GVHD) with post-transplant immunosuppressive agents.

Timeline

Start
2021-09-07
Primary completion
2028-05
Completion
2028-05

Drugs

EvaluationDrugModalityDoseRoute
Subject Melphalan Small molecule 50 mg/m2
Subject Melphalan Small molecule 100 mg/m2
Subject Purified regulatory T-cells Cell therapy 1e+06 cells/kg
Subject Purified regulatory T-cells Cell therapy 3e+06 cells/kg
Subject Thiotepa Other / unclassified 5 mg/kg
Subject Thiotepa Other / unclassified 7.5 mg/kg
Subject Thiotepa Other / unclassified 10 mg/kg
Background CD34+ HSPC Cell therapy
Background Cyclophosphamide Other / unclassified 40 mg/kg
Background Fludarabine Small molecule 160 mg/m2
Background Mycophenolate Mofetil Small molecule 1000 mg
Background Plerixafor Small molecule 0.24 mg/kg
Background Ruxolitinib Small molecule 5 mg
Background Sirolimus Small molecule 5 ng/ml
Background Sirolimus Small molecule 8 ng/ml
Background Tacrolimus Small molecule 4 ng/ml
Background Tacrolimus Small molecule 6 ng/ml
Background filgrastim Protein / enzyme biologic 300 ug
Background filgrastim Protein / enzyme biologic 480 ug