Phase 0 1 trial
Phase 0
NCT05343572
Nov 2023 → Dec 2026 expected
Asherman syndrome , infertility disorder , uterine disorder
Hugh Taylor
Recruiting
No outcome recorded
Phase 1 24 trials
Phase 1
NCT07585136
Jun 2026 → Dec 2028 expected
bone marrow failure syndrome
St. Jude Children's Research Hospital
Not yet recruiting
No outcome recorded
Phase 1
NCT03932864
Apr 2019 → Feb 2020
—
Ensoma
Completed
No outcome recorded
Phase 1
NCT03664830
Sep 2018 → Aug 2026 overdue
sickle cell disease
City of Hope Medical Center
Active not recruiting
No outcome recorded
Phase 1
NCT03277209
Jul 2017 → Dec 2019
malignant pancreatic neoplasm
Weill Medical College of Cornell University
Terminated
No outcome recorded
Phase 1
NCT03226691
Jul 2017 → Feb 2019
sickle cell disease
National Heart, Lung, and Blood Institute (NHLBI)
Completed
No outcome recorded
Phase 1
NCT02989701
Jan → Dec 2017
sickle cell disease
Alessandra Biffi
Completed
No outcome recorded
Phase 1
NCT02179970
Jun 2015 → Dec 2018
colorectal cancer , ovarian serous adenocarcinoma , pancreatic adenocarcinoma
CCTU- Cancer Theme
Completed
No outcome recorded
Phase 1
NCT02193191
Sep 2014 → Mar 2025
sickle cell disease
Memorial Sloan Kettering Cancer Center
Completed
No outcome recorded
Phase 1
NCT01916577
Aug 2013 → Oct 2017
chronic obstructive pulmonary disease , cystic fibrosis , pulmonary fibrosis
University of Colorado, Denver
Completed
No outcome recorded
Phase 1
NCT01610999
Jul 2013 → Jun 2014
B-cell chronic lymphocytic leukemia , plasma cell myeloma
Tufts Medical Center
Terminated
No outcome recorded
Phase 1
NCT01711073
Oct 2012 → Sep 2013
liver failure
Proteonomix, Inc.
Unknown
No outcome recorded
Phase 1
NCT01373229
Jan 2012 → Mar 2014
B-cell chronic lymphocytic leukemia
David Rizzieri, MD
Completed
No outcome recorded
Phase 1
NCT01455025
Jan 2012 → Mar 2015
acute myeloid leukemia
French Innovative Leukemia Organisation
Terminated
No outcome recorded
Phase 1
NCT01339039
Dec 2011 → Apr 2014
anaplastic astrocytoma , anaplastic oligoastrocytoma , anaplastic oligodendroglioma , gliosarcoma
Patrick Y. Wen, MD
Terminated
No outcome recorded
Phase 1
NCT01579149
Sep 2011 → Feb 2012
—
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 1
NCT01319864
Mar 2011 → Jun 2013
acute leukemia of ambiguous lineage , precursor lymphoblastic lymphoma/leukemia , therapy related acute myeloid leukemia and myelodysplastic syndrome
Seattle Children's Hospital
Completed
No outcome recorded
Phase 1
NCT01058993
Oct 2010 → Mar 2011
neutropenia
University of Washington
Completed
No outcome recorded
Phase 1
NCT01065129
Sep 2010 → Jul 2014
myelodysplastic syndrome
Washington University School of Medicine
Completed
No outcome recorded
Phase 1
NCT01068301
May 2010 → Oct 2013
acute lymphoblastic leukemia , acute myeloid leukemia , chronic myeloid leukemia , myelodysplastic syndrome
St. Jude Children's Research Hospital
Completed
No outcome recorded
Phase 1
NCT01027923
May → Jul 2010
acute myeloid leukemia
Washington University School of Medicine
Terminated
No outcome recorded
Phase 1
NCT01074060
Apr 2010 → Feb 2013
plasma cell myeloma
City of Hope Medical Center
Completed
No outcome recorded
Phase 1
NCT00990054
Dec 2009 → Mar 2012
acute myeloid leukemia
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 1
NCT00694590
Jun 2008 → Nov 2010
chronic lymphocytic leukemia/small lymphocytic lymphoma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 1
NCT00445302
Jan 2006 → Aug 2007
impaired renal function disease
Genzyme, a Sanofi Company
Completed
No outcome recorded
Show 14 more trials
Phase 1/2 15 trials
Phase 1/2
NCT07341022
Jun 2026 → Dec 2027 expected
sickle cell disease
Hospital Israelita Albert Einstein
Not yet recruiting
No outcome recorded
Phase 1/2
NCT05470491
Jan 2023 → Jul 2026 overdue
HIV infectious disease , hematopoietic and lymphoid cell neoplasm
National Cancer Institute (NCI)
Recruiting
No outcome recorded
Phase 1/2
NCT03182426
Aug 2017 → Jul 2024
type 1 diabetes mellitus
University of Alberta
Completed
No outcome recorded
Phase 1/2
NCT02678533
Feb 2017 → Nov 2018
Fanconi anemia
Assistance Publique - Hôpitaux de Paris
Completed
No outcome recorded
Phase 1/2
NCT02212535
Jan 2016 → Apr 2017
sickle cell disease
Assistance Publique - Hôpitaux de Paris
Completed
No outcome recorded
Phase 1/2
NCT02522572
Aug 2015 → Sep 2020
—
E. Steve Woodle
Unknown
No outcome recorded
Phase 1/2
NCT01977677
Nov 2014 → Nov 2017
adult glioblastoma , adult medulloblastoma , adult pineoblastoma , ependymoblastoma +4
Lawrence Recht
Completed
No outcome recorded
Phase 1/2
NCT01288573
Mar 2014 → May 2017
brain neoplasm , neuroblastoma , sarcoma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 1/2
NCT01435343
Jul 2012 → May 2016
acute myeloid leukemia
PETHEMA Foundation
Completed
No outcome recorded
Phase 1/2
NCT01280955
Dec 2011 → Sep 2014
bone marrow failure syndrome
Mitchell Horwitz, MD
Completed
No outcome recorded
Phase 1/2
NCT01236144
Apr 2011 → Dec 2013
acute myeloid leukemia , myelodysplastic syndrome
Cardiff University
Completed
No outcome recorded
Phase 1/2
NCT00906945
Feb 2011 → Nov 2012
acute myeloid leukemia
Washington University School of Medicine
Completed
No outcome recorded
Phase 1/2
NCT01160354
Aug 2010 → Mar 2016
acute myeloid leukemia
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Phase 1/2
NCT00903968
Jun 2009 → Jun 2016
plasma cell myeloma
Dana-Farber Cancer Institute
Completed
No outcome recorded
Phase 1/2
NCT00822770
Jan 2009 → Oct 2012
disease related to hematopoietic stem cell transplant , leukemia
M.D. Anderson Cancer Center
Completed
No outcome recorded
Show 5 more trials
Phase 2 48 trials
Phase 2
NCT07188090
Oct 2025 → Dec 2027 expected
Hodgkins lymphoma , non-Hodgkin lymphoma , plasma cell myeloma
Thomas Jefferson University
Recruiting
No outcome recorded
Phase 2
NCT06872333
Nov 2024 → Jun 2030 expected
disease related to hematopoietic stem cell transplant , sickle cell disease
Masonic Cancer Center, University of Minnesota
Recruiting
No outcome recorded
Phase 2
NCT06141304
Sep 2023 → Jan 2025
acute myeloid leukemia , adult acute lymphoblastic leukemia
The First Hospital of Jilin University
Unknown
No outcome recorded
Phase 2
NCT04817345
Apr 2023
sickle cell disease
St. Jude Children's Research Hospital
Withdrawn
No outcome recorded
Phase 2
NCT05411575
Jul → Oct 2022
COVID-19 , acute respiratory distress syndrome
4Living Biotech
Withdrawn
No outcome recorded
Phase 2
NCT05445128
Jun → Dec 2022
sickle cell disease
Ensoma
Terminated
No outcome recorded
Phase 2
NCT04762875
Jun → Sep 2021
acute lymphoblastic leukemia , acute myeloid leukemia , myelodysplastic syndrome
Ensoma
Terminated
No outcome recorded
Phase 2
NCT04177810
Nov 2020 → Mar 2023
malignant pancreatic neoplasm
Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins
Completed
No outcome recorded
Phase 2
NCT04552743
Oct 2020 → Jul 2021
plasma cell myeloma
Surbhi Sidana, MD
Completed
No outcome recorded
Phase 2
NCT04362293
Apr 2020 → Aug 2026
sickle cell disease
St. Jude Children's Research Hospital
Suspended
No outcome recorded
Phase 2
NCT03547830
Apr 2019 → Jan 2023
chronic granulomatous disease
Federal Research Institute of Pediatric Hematology, Oncology and Immunology
Unknown
No outcome recorded
Phase 2
NCT03746080
Dec 2018 → May 2022
gliosarcoma , mixed neuronal-glial tumor , oligodendroglial tumor
Lawrence D Recht
Completed
No outcome recorded
Phase 2
NCT03244930
May 2017 → May 2018
Hodgkins lymphoma , disease related to hematopoietic stem cell transplant , non-Hodgkin lymphoma , plasma cell myeloma
Hospital Universitario Dr. Jose E. Gonzalez
Unknown
No outcome recorded
Phase 2
NCT03019809
Jun 2016 → Dec 2018
Wiskott-Aldrich syndrome , disease related to hematopoietic stem cell transplant , transplant rejection
Federal Research Institute of Pediatric Hematology, Oncology and Immunology
Unknown
No outcome recorded
Phase 2
NCT02790957
Jun 2016 → Aug 2019
diabetes mellitus , limb ischemia
Gian Paolo Fadini
Terminated
No outcome recorded
Phase 2
NCT02221492
Nov 2014 → Mar 2016
lymphoma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT02221479
Oct 2014 → Jul 2015
plasma cell myeloma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT02200380
Jul 2014 → Mar 2016
B-cell chronic lymphocytic leukemia , Hodgkins lymphoma , acute myeloid leukemia , chronic myeloid leukemia +1
Celldex Therapeutics
Terminated
No outcome recorded
Phase 2
NCT02605460
Feb 2014 → Nov 2020
acute lymphoblastic leukemia , acute myeloid leukemia
National Institute of Medical Sciences and Nutrition Salvador Zubiran
Unknown
No outcome recorded
Phase 2
NCT02015013
Jan 2014 → Oct 2026 expected
idiopathic CD4-positive T-lymphocytopenia
National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
No outcome recorded
Phase 2
NCT01954914
Dec 2013 → Jan 2016
bone marrow failure syndrome
Technical University Dresden
Completed
No outcome recorded
Phase 2
NCT01818284
Oct 2013 → Jun 2016
disease related to hematopoietic stem cell transplant
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT02931071
Sep 2013 → Oct 2018
Fanconi anemia
Hospital Universitari Vall d'Hebron Research Institute
Completed
No outcome recorded
Phase 2
NCT01753453
Jun 2013 → Sep 2016
plasma cell myeloma
Sanofi
Completed
No outcome recorded
Phase 2
NCT01696461
May 2013 → Aug 2016
Hodgkins lymphoma , acute myeloid leukemia , chronic lymphocytic leukemia/small lymphocytic lymphoma , chronic myeloid leukemia +1
Center for International Blood and Marrow Transplant Research
Completed
No outcome recorded
Phase 2
NCT01547806
Feb 2012 → Jun 2014
plasma cell myeloma
National Cancer Institute (NCI)
Completed
No outcome recorded
Phase 2
NCT01158118
Apr 2011 → Jan 2014
B-cell chronic lymphocytic leukemia , Hodgkins lymphoma , acute myeloid leukemia , myelodysplastic syndrome +1
Washington University School of Medicine
Completed
No outcome recorded
Phase 2
NCT01339572
Apr 2011 → Nov 2015
non-Hodgkin lymphoma , plasma cell myeloma
University of Florida
Completed
No outcome recorded
Phase 2
NCT01097057
Nov 2010 → Sep 2013
non-Hodgkin lymphoma
Fred Hutchinson Cancer Center
Completed
No outcome recorded
Phase 2
NCT01225419
Sep 2010 → May 2011
childhood malignant neoplasm
University Hospital, Clermont-Ferrand
Completed
No outcome recorded
Phase 2
NCT01182675
Aug 2010 → Sep 2013
severe combined immunodeficiency
University of California, San Francisco
Terminated
No outcome recorded
Phase 2
NCT01164345
Jun 2010 → May 2015
Hodgkins lymphoma , non-Hodgkin lymphoma
Sheba Medical Center
Completed
No outcome recorded
Phase 2
NCT01149863
Jun 2010 → Dec 2011
—
Emory University
Completed
No outcome recorded
Phase 2
NCT01220375
Apr 2010 → Jan 2012
plasma cell myeloma
Insel Gruppe AG, University Hospital Bern
Completed
No outcome recorded
Phase 2
NCT01095757
Mar 2010 → May 2012
plasma cell myeloma
Emory University
Completed
No outcome recorded
Phase 2
NCT01037517
Jan 2010 → Aug 2013
plasma cell myeloma
CancerCare Manitoba
Completed
No outcome recorded
Phase 2
NCT00998049
Dec 2009 → Nov 2011
plasma cell myeloma
Mayo Clinic
Completed
No outcome recorded
Phase 2
NCT00901225
May 2009 → Aug 2010
Hodgkins lymphoma , non-Hodgkin lymphoma , plasma cell myeloma
Duke University
Completed
No outcome recorded
Phase 2
NCT00665314
Nov 2007 → Apr 2008
Hodgkins lymphoma , non-Hodgkin lymphoma , plasma cell myeloma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00444912
Feb 2006 → Jun 2009
Hodgkins lymphoma , non-Hodgkin lymphoma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00396331
Oct 2005 → Dec 2009
disease related to hematopoietic stem cell transplant
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00395967
Apr → Jul 2005
non-Hodgkin lymphoma , plasma cell myeloma
Genzyme, a Sanofi Company
Terminated
No outcome recorded
Phase 2
NCT00396266
Jan 2005 → Dec 2007
non-Hodgkin lymphoma , plasma cell myeloma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00396201
Nov 2004 → Oct 2006
Hodgkins lymphoma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00396383
Nov 2004 → May 2007
plasma cell myeloma
Genzyme, a Sanofi Company
Terminated
No outcome recorded
Phase 2
NCT00322842
Sep 2004 → Feb 2007
non-Hodgkin lymphoma , plasma cell myeloma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00322387
Apr 2004 → Jul 2006
non-Hodgkin lymphoma , plasma cell myeloma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 2
NCT00322491
Mar 2004 → Jun 2006
non-Hodgkin lymphoma , plasma cell myeloma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Show 38 more trials
Phase 3 6 trials
Phase 3
NCT01767714
Apr 2013 → Nov 2014
non-Hodgkin lymphoma
Sanofi
Completed
No outcome recorded
Phase 3
NCT01301963
Jul 2011 → Jun 2013
refractory plasma cell neoplasm
Case Comprehensive Cancer Center
Terminated
No outcome recorded
Phase 3
NCT01146834
Mar 2011 → Feb 2019
plasma cell myeloma
Weill Medical College of Cornell University
Completed
No outcome recorded
Phase 3
NCT00838357
Sep 2008 → Nov 2010
disease related to transplantation , non-Hodgkin lymphoma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 3
NCT00103662
Jan 2005 → Oct 2006
plasma cell myeloma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 3
NCT00103610
Jan 2005 → Jul 2006
non-Hodgkin lymphoma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase 4 4 trials
Phase 4
NCT05510544
Dec 2022 → Dec 2023
lymphoma
Peking University
Unknown
No outcome recorded
Phase 4
NCT05087212
Oct 2021 → Dec 2022
disease related to hematopoietic stem cell transplant
Sanofi
Completed
No outcome recorded
Phase 4
NCT02006225
Feb 2014 → Feb 2019
disease related to hematopoietic stem cell transplant
Tel-Aviv Sourasky Medical Center
Unknown
No outcome recorded
Phase 4
NCT01164475
Oct 2010 → Feb 2013
non-Hodgkin lymphoma
Genzyme, a Sanofi Company
Completed
No outcome recorded
Phase not applicable 4 trials
—
NCT01408043
Oct 2011 → May 2016
Burkitt lymphoma , MALT lymphoma , T-cell large granular lymphocyte leukemia , Waldenstrom macroglobulinemia +18
Case Comprehensive Cancer Center
Terminated
No outcome recorded
—
NCT01076270
Jun 2010 → Jan 2011
Burkitt lymphoma , Hodgkins lymphoma , MALT lymphoma , acute myeloid leukemia with 11q23 abnormalities +19
Fred Hutchinson Cancer Center
Terminated
No outcome recorded
—
NCT01186224
May 2010 → Jun 2015
lymphoproliferative syndrome , plasma cell myeloma
University of Liverpool
Completed
No outcome recorded
—
NCT01042717
Feb 2010 → Dec 2011
non-Hodgkin lymphoma , plasma cell myeloma
Shi, Patricia, M.D.
Unknown
No outcome recorded