Phase 1 6 trials
Phase 1
NCT01163097
Jul 2010 → Jan 2011
mucositis
Swedish Orphan Biovitrum
Completed
No outcome recorded
Phase 1
NCT00701688
Sep 2007 → Sep 2011
mouth disorder
St. Jude Children's Research Hospital
Completed
No outcome recorded
Phase 1
NCT00482846
Jun 2007 → Oct 2011
mucositis , plasma cell myeloma
Barbara Ann Karmanos Cancer Institute
Completed
No outcome recorded
Phase 1
NCT00460421
Aug 2006 → May 2011
leukemia
Swedish Orphan Biovitrum
Completed
No outcome recorded
Phase 1
NCT00361348
Dec 2005 → Jul 2006
—
Swedish Orphan Biovitrum
Completed
No outcome recorded
Phase 1
NCT00070616
Dec 2001 → Mar 2005
leukemia , plasma cell myeloma
Swedish Orphan Biovitrum
Completed
No outcome recorded
Phase 1/2 5 trials · 1 missed
Phase 1/2
NCT02356159
Sep 2015 → Dec 2024
Hodgkins lymphoma , acute leukemia , myelodysplastic syndrome , non-Hodgkin lymphoma +1
National Cancer Institute (NCI)
Completed
Missed primary
Phase 1/2
NCT01712945
Jun 2012 → Aug 2017
multiple sclerosis
Cambridge University Hospitals NHS Foundation Trust
Terminated
No outcome recorded
Phase 1/2
NCT02037347
Oct 2010 → Dec 2014
Stevens-Johnson syndrome
Brett King
Terminated
No outcome recorded
Stop: Enrollment
Phase 1/2
NCT00540332
Oct 2007 → Sep 2008
head and neck cancer
Swedish Orphan Biovitrum
Withdrawn
No outcome recorded
Phase 1/2
NCT00626639
Jul 2005 → May 2007
head and neck cancer , mucositis
Swedish Orphan Biovitrum
Completed
No outcome recorded
Phase 2 11 trials · 1 met primary · 3 missed
Phase 2
NCT01746849
Dec 2012 → Dec 2026 expected
leukemia , myelodysplastic syndrome , non-Hodgkin lymphoma , plasma cell myeloma
Memorial Sloan Kettering Cancer Center
Active not recruiting
No outcome recorded
Phase 2
NCT00728585
Mar 2008 → May 2009
cancer , gastrointestinal mucositis
Children's Oncology Group
Withdrawn
No outcome recorded
Phase 2
NCT00629798
Feb 2008 → Oct 2020
acute myeloid leukemia , myelodysplastic syndrome
Memorial Sloan Kettering Cancer Center
Completed
No outcome recorded
Phase 2
NCT00570999
Feb 2008 → Jan 2013
acute leukemia , chronic myeloid leukemia , lymphoma , myelodysplastic syndrome +1
European Society for Blood and Marrow Transplantation
Withdrawn
No outcome recorded
Phase 2
NCT00593554
Aug 2007 → Aug 2016
acute lymphoblastic leukemia , acute myeloid leukemia , chronic myeloid leukemia , myelodysplastic syndrome
Sherif S. Farag
Terminated
No outcome recorded
Stop: Enrollment
Phase 2
NCT00376935
Dec 2006 → Jul 2008
HIV infectious disease
National Institute of Allergy and Infectious Diseases (NIAID)
Completed
Missed primary
Phase 2
NCT00189488
Dec 2005 → Nov 2008
acute graft versus host disease , hematopoietic and lymphoid cell neoplasm
Swedish Orphan Biovitrum
Completed
Missed primary
Phase 2
NCT00267046
Dec 2005 → Jul 2009
chemotherapy-induced oral mucositis , sarcoma
M.D. Anderson Cancer Center
Completed
Met primary
Phase 2
NCT00094861
Jan 2005 → Dec 2007
non-small cell lung carcinoma
Swedish Orphan Biovitrum
Completed
Missed primary
Phase 2
NCT00004132
Jan 2000 → May 2004
chemotherapy-induced oral mucositis , leukemia , plasma cell neoplasm , poisoning +1
Jonsson Comprehensive Cancer Center
Completed
No outcome recorded
Phase 2
NCT00004061
May 1999 → May 2003
chemotherapy-induced oral mucositis , leukemia , lymphoma
Memorial Sloan Kettering Cancer Center
Completed
No outcome recorded
Show 1 more trial
Phase 2/3 1 trial
Phase 2/3
NCT00393822
Aug 2005 → Dec 2007
colon carcinoma
Amgen
Completed
No outcome recorded
Phase 3 4 trials · 1 met primary
Phase 3
NCT00360971
Jul 2006 → May 2008
head and neck cancer , mucositis , radiation-induced disorder
Radiation Therapy Oncology Group
Terminated
No outcome recorded
Phase 3
NCT00101582
Aug 2005 → Sep 2007
chemotherapy-induced oral mucositis , head and neck cancer , squamous cell carcinoma
Swedish Orphan Biovitrum
Completed
Met primary
Phase 3
NCT00131638
Jan 2005 → Nov 2007
head and neck cancer
Amgen
Completed
No outcome recorded
Phase 3
NCT00109031
Jan 2005 → Feb 2006
cancer , leukemia , lymphoma
Swedish Orphan Biovitrum
Completed
No outcome recorded
Phase not applicable 1 trial
—
NCT01233921
Sep 2010 → Jul 2012
Burkitt lymphoma , Hodgkins lymphoma , MALT lymphoma , acute myeloid leukemia with 11q23 abnormalities +26
Martin, Paul
Completed
No outcome recorded
Phase not stated 1 trial · 1 missed
—
NCT01085617
Dec 2010 → Feb 2025
leukemia , mouth disorder , mucositis
University College, London
Completed
Missed primary
Comparator or background therapy 23 trials
Phase 0
NCT00881556 Background
Aug 2009 → Sep 2015
epidermolysis bullosa
Columbia University
Terminated
No outcome recorded
Phase 1
NCT05139004 Background
Jul 2022 → Jun 2027 expected
acute lymphoblastic leukemia , acute myeloid leukemia , myelodysplastic syndrome
City of Hope Medical Center
Active not recruiting
No outcome recorded
Phase 1
NCT04177004 Background
Apr 2021 → Dec 2025 overdue
disease related to hematopoietic stem cell transplant , hematopoietic and lymphoid cell neoplasm
City of Hope Medical Center
Active not recruiting
No outcome recorded
Phase 1
NCT03531281 Background
Dec 2018 → Dec 2022
disease related to hematopoietic stem cell transplant , hematopoietic and lymphoid cell neoplasm
City of Hope Medical Center
Withdrawn
No outcome recorded
Phase 1
NCT01421173 Background
Aug 2011 → Sep 2015
lymphoma
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1
NCT00410982 Background
Dec 2006 → Sep 2012
leukemia , plasma cell myeloma
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 1/2
NCT07775313 Background
Oct 2026 → Dec 2031 expected
WHIM syndrome , dysgammaglobulinemia , myeloid hemopathy , skin disorder caused by infection
National Institute of Allergy and Infectious Diseases (NIAID)
Enrolling by invitation
No outcome recorded
Phase 1/2
NCT06959771 Background
Jul 2025 → Oct 2027 expected
hyper-IgM syndrome type 1
National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
No outcome recorded
Phase 1/2
NCT06986382 Background
Jul 2025 → Jul 2037 expected
Crohn disease
Stanford University
Not yet recruiting
No outcome recorded
Phase 1/2
NCT06851767 Background
May 2025 → Dec 2034 expected
T-B+ severe combined immunodeficiency due to gamma chain deficiency
National Institute of Allergy and Infectious Diseases (NIAID)
Enrolling by invitation
No outcome recorded
Phase 1/2
NCT06325709 Background
Apr 2024 → Dec 2032 expected
granulomatous disease, chronic, X-linked
National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
No outcome recorded
Phase 1/2
NCT03100877 Background
Jan 2018 → May 2020
plasma cell leukemia , plasma cell myeloma
City of Hope Medical Center
Withdrawn
No outcome recorded
Phase 1/2
NCT02589145 Background
Jun 2016 → Apr 2019
lymphoma
M.D. Anderson Cancer Center
Terminated
No outcome recorded
Stop: Enrollment
Phase 1/2
NCT01306019 Background
Sep 2012 → Dec 2032 expected
T-B+ severe combined immunodeficiency due to gamma chain deficiency
National Institute of Allergy and Infectious Diseases (NIAID)
Recruiting
No outcome recorded
Phase 1/2
NCT03315078 Background
Apr 2012 → Dec 2022
combined immunodeficiency, X-linked
National Institute of Allergy and Infectious Diseases (NIAID)
Unknown
No outcome recorded
Phase 2
NCT07582172 Background
Nov 2026 → Nov 2031 expected
acute myeloid leukemia , chronic myelomonocytic leukemia , myelodysplastic syndrome
City of Hope Medical Center
Recruiting
No outcome recorded
Phase 2
NCT02961816 Background
Jun 2017 → Jun 2021
lymphoma
M.D. Anderson Cancer Center
Withdrawn
No outcome recorded
Stop: Business
Phase 2
NCT02114502 Background
Sep 2014 → Sep 2018
plasma cell myeloma
M.D. Anderson Cancer Center
Withdrawn
No outcome recorded
Phase 2
NCT01746173 Background
Jul 2013 → Oct 2014
T-cell non-Hodgkin lymphoma
Dana-Farber Cancer Institute
Terminated
No outcome recorded
Stop: Enrollment
Phase 2
NCT01200329 Background
Jun 2011 → Dec 2018
lymphoma
M.D. Anderson Cancer Center
Completed
No outcome recorded
Phase 2
NCT01237951 Background
Nov 2010 → Sep 2017
plasma cell myeloma
M.D. Anderson Cancer Center
Completed
Met primary
Phase 3
NCT02313792 Comparator
Jan → Mar 2015
mucositis
The Catholic University of Korea
Unknown
No outcome recorded
Phase 3
NCT00434161 Comparator
Dec 2006 → Mar 2009
plasma cell myeloma
Swedish Orphan Biovitrum
Completed
No outcome recorded
Show 18 more trials