Drugs / fenretinide
last change Jul 2026 re-read 2 minutes ago

fenretinide

Small molecule

Developed for
neuroblastoma · cancer of unknown primary site · head and neck cancer · breast cancer · cystic fibrosis · ovarian cancer · peripheral T-cell lymphoma, not otherwise specified · primary peritoneal carcinoma
+44 more · acute lymphoblastic leukemia · acute myeloid leukemia · adult glioblastoma · adult nodular lymphocyte predominant Hodgkin lymphoma · angioimmunoblastic T-cell lymphoma · Burkitt lymphoma · cancer · central nervous system neoplasm · cervical cancer · childhood malignant neoplasm · chronic lymphocytic leukemia/small lymphocytic lymphoma · COVID-19 · cutaneous melanoma · dengue disease · diffuse large B-cell lymphoma · dysplasia of cervix · giant cell glioblastoma · gliosarcoma · hereditary neoplastic syndrome · kidney cancer · leukemia · long COVID-19 · lung cancer · lymphoma · malignant epithelial tumor of ovary · mantle cell lymphoma · mycosis fungoides · myeloproliferative neoplasm · nodal marginal zone B-cell lymphoma · Nodal T-follicular helper cell lymphoma, follicular type · obesity disorder · oral mucosa leukoplakia · ovarian carcinoma · plasma cell neoplasm · prostate adenocarcinoma · prostate cancer · schizophrenia · Sezary syndrome · small cell lung carcinoma · splenic marginal zone lymphoma · urinary bladder cancer · Waldenstrom macroglobulinemia · diffuse secondary choroid atrophy · dry age related macular degeneration
Investigated by
National Cancer Institute (NCI) · South Plains Oncology Consortium · M.D. Anderson Cancer Center · Laurent Pharmaceuticals Inc. · Barbara Ann Karmanos Cancer Institute · California Cancer Consortium
+23 more · Eastern Cooperative Oncology Group · New Approaches to Neuroblastoma Therapy Consortium · Ohio State University Comprehensive Cancer Center · SWOG Cancer Research Network · SciTech Development, Inc. · Beersheva Mental Health Center · Cancer Therapeutics Research Group · Cancer and Leukemia Group B · Case Comprehensive Cancer Center · CerRx, Inc. · Cystic Fibrosis Foundation · Elias Matouk · European Institute of Oncology · Gynecologic Oncology Group · Island Pharmaceuticals · National Institutes of Health Clinical Center (CC) · North Central Cancer Treatment Group · Schering-Plough · Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins · The Evan Foundation · University of Alabama at Birmingham · University of Arizona · University of California, San Diego

Trials 46 · a red edge is where a trial was stopped

PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 118 trials
Phase 1 NCT06922539 Dec 2025 → May 2027 expected small cell lung carcinoma SciTech Development, Inc. Recruiting No outcome recorded
Phase 1 NCT07149220 Oct 2025 → Jun 2026 overdue oral mucosa leukoplakia Ohio State University Comprehensive Cancer Center Active not recruiting No outcome recorded
Phase 1 NCT04234048 Dec 2023 → Dec 2026 expected Nodal T-follicular helper cell lymphoma, follicular type, Sezary syndrome, angioimmunoblastic T-cell lymphoma, mycosis fungoides +1 SciTech Development, Inc. Recruiting No outcome recorded
Phase 1 NCT01553071 Nov 2016 → Dec 2020 cancer South Plains Oncology Consortium Terminated No outcome recorded
Phase 1 NCT02163356 May 2014 → May 2018 neuroblastoma South Plains Oncology Consortium Terminated No outcome recorded
Phase 1 NCT02141958 Apr 2014 → Feb 2015 cystic fibrosis Elias Matouk Completed No outcome recorded
Phase 1 NCT01187810 Aug 2010 → Apr 2018 acute lymphoblastic leukemia, acute myeloid leukemia South Plains Oncology Consortium Terminated No outcome recorded
Phase 1 NCT00589381 Aug 2007 → Dec 2010 cancer of unknown primary site, lymphoma National Institutes of Health Clinical Center (CC) Completed No outcome recorded
Phase 1 NCT00646230 Dec 2006 → Mar 2012 neuroblastoma New Approaches to Neuroblastoma Therapy Consortium Completed No outcome recorded
Phase 1 NCT00387504 Nov 2006 → Jul 2013 cancer of unknown primary site California Cancer Consortium Completed No outcome recorded
Phase 1/22 trials
Phase 1/2 NCT01535157 Feb 2012 → Jun 2017 ovarian cancer, primary peritoneal carcinoma South Plains Oncology Consortium Terminated No outcome recorded
Phase 1/2 NCT00288067 Oct 2005 → Jul 2013 Burkitt lymphoma, Waldenstrom macroglobulinemia, adult nodular lymphocyte predominant Hodgkin lymphoma, chronic lymphocytic leukemia/small lymphocytic lymphoma +4 National Cancer Institute (NCI) Terminated No outcome recorded
Phase 216 trials
Phase 2 NCT06528457 Sep 2024 → May 2025 dengue disease Island Pharmaceuticals Completed No outcome recorded
Phase 2 NCT03265288 Nov 2018 → Sep 2021 cystic fibrosis Laurent Pharmaceuticals Inc. Completed No outcome recorded
Phase 2 NCT02495415 Dec 2016 → Jul 2021 peripheral T-cell lymphoma, not otherwise specified CerRx, Inc. Unknown No outcome recorded
Phase 2 NCT00546455 Dec 2007 → Jan 2012 obesity disorder University of California, San Diego Suspended No outcome recorded
Phase 2 NCT00080899 Jun 2004 → Jan 2009 prostate adenocarcinoma National Cancer Institute (NCI) Completed No outcome recorded
Phase 2 NCT00075491 Dec 2003 → Mar 2005 adult glioblastoma, giant cell glioblastoma, gliosarcoma National Cancer Institute (NCI) Terminated No outcome recorded
Phase 2 NCT00077402 Nov 2003 → Jan 2011 prostate cancer Cancer Therapeutics Research Group Completed No outcome recorded
Phase 2 NCT00053326 May 2003 → Mar 2006 neuroblastoma National Cancer Institute (NCI) Completed No outcome recorded
Phase 2 NCT00026091 Sep 2001 → Mar 2004 malignant epithelial tumor of ovary, primary peritoneal carcinoma National Cancer Institute (NCI) Completed No outcome recorded
Phase 2 NCT00011973 Dec 2000 → Oct 2005 kidney cancer Barbara Ann Karmanos Cancer Institute Completed No outcome recorded
Phase 2/32 trials
Phase 2/3 NCT05999435 Nov 2023 → Aug 2024 long COVID-19 Laurent Pharmaceuticals Inc. Completed No outcome recorded
Phase 2/3 NCT04417257 Aug 2020 → Feb 2024 COVID-19 Laurent Pharmaceuticals Inc. Terminated No outcome recorded
Phase 35 trials
Phase 3 NCT01479192 Dec 2009 → Dec 2015 hereditary neoplastic syndrome European Institute of Oncology Terminated No outcome recorded
Phase 3 NCT00004154 Jul 1998 → Mar 2005 urinary bladder cancer M.D. Anderson Cancer Center Completed No outcome recorded
Phase 3 NCT00002646 Oct 1995 → Feb 2004 breast cancer Eastern Cooperative Oncology Group Completed No outcome recorded
Phase 3 NCT00003075 Mar 1993 → May 2001 cervical cancer, dysplasia of cervix M.D. Anderson Cancer Center Completed No outcome recorded
Phase 3 NCT00534898 schizoaffective disorder, schizophrenia Beersheva Mental Health Center Withdrawn No outcome recorded
Phase not applicable2 trials
NCT00098800 Oct 2004 → Aug 2006 BRCA1-related cancer predisposition, BRCA2-related cancer predisposition, ovarian cancer University of Arizona Completed No outcome recorded
NCT00017134 Sep 2002 → Dec 2006 ovarian carcinoma Gynecologic Oncology Group Terminated No outcome recorded
Phase not stated1 trial
NCT02075177 neuroblastoma South Plains Oncology Consortium No longer available No outcome recorded
Also used as a comparator or background therapy in 3 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 11 trial
Phase 1 NCT06181760 Comparator Nov 2023 → Feb 2024 Island Pharmaceuticals Completed No outcome recorded
Phase 22 trials
Phase 2 NCT00429936 Comparator Dec 2006 → May 2010 diffuse secondary choroid atrophy, dry age related macular degeneration Sirion Therapeutics, Inc. Completed No outcome recorded
Phase 2 NCT00003099 Comparator May 1996 → Jun 2000 breast cancer M.D. Anderson Cancer Center Completed No outcome recorded

Evidence & citations 19 cited values

Every value below carries the sentence it was read from. 54 sources stand behind the page.

FieldValueCited text
Known as fenretinide Fenretinide is an anticancer agent that may work differently than standard chemotherapy medicines.” NCT02075177
45

“Active drug fenretinide (as LAU-7b capsules)” NCT03265288

NCT00011973

NCT00077402

NCT06181760

NCT02495415

NCT00009932

NCT00001378

NCT00098800

NCT02163356

NCT00006080

NCT00646230

NCT00295919

NCT00053326

NCT00003223

NCT00429936

NCT00026091

NCT00005819

NCT01187810

NCT04234048

NCT00004161

NCT00387504

NCT00004154

NCT00009971

NCT07149220

NCT00102635

NCT00075491

NCT00534898

NCT00288067

NCT00006471

NCT00589381

NCT00003601

NCT06922539

NCT00003250

NCT00002646

NCT00017134

NCT01535157

NCT00546455

NCT00080899

NCT00104923

NCT00003191

NCT00003099

NCT00003075

NCT02141958

NCT01479192

NCT01553071

Known as 4-HPR “Induction of apoptosis is a unique feature of fenretinide (4-hydroxyphenylretinamide, 4-HPR),(2) the most widely studied retinoid in clinical trials of breast cancer...” NCT01479192
10

“A Multicenter Randomized Double-Blinded Trial for Chemoprevention of Ovarian Cancer: Modulation of Biomarkers and Spectral Properties Using Contrast Enhanced Ultrasound in...” NCT00098800

“The synthetic retinoid fenretinide (N-(4-hydroxyphenyl)retinamide, 4-HPR) has shown promising anticancer activity in preclinical studies, but its limited oral bioavailability...” PMID 21498721 Mar 2011

“A Randomized, Double Blind, Placebo-Controlled Phase II Clinical Trial of N(4-Hydroxy-phenyl)Retinamide (Fenretinide, 4HPR) in Oral Leukoplakia” NCT00004161

“Phase I Study of Fenretinide (4-HPR, NSC 374551) Lym-X-Sorb™ (LXS) Oral Powder in Patients With Recurrent or Resistant Neuroblastoma” NCT00295919

“To evaluate the efficacy of fenretinide (4-HPR) in patients with recurrent ovarian cancer or primary peritoneal carcinoma.” NCT00026091

“Fenretinide (4-HPR) is a synthetic retinoid that induces cytotoxicity through dihydroceramide production.” PMID 37199745 May 2023

4-HPR (Fenretinide) is given as a continuous intravenous infusion (CIV) for five consecutive days.” NCT00387504

“A Phase II Trial of Fenretinide (4-HPR) in Biochemically Recurrent, Hormone Naive Prostate Cancer” NCT00080899

“Phase I Trial of Intravenous Fenretinide (4-HPR) for Patients With Hematologic Malignancies” NCT00104923

“Fenretinide (4-HPR)” NCT00102635

Known as 4-hydroxyphenylretinamide “Induction of apoptosis is a unique feature of fenretinide (4-hydroxyphenylretinamide, 4-HPR),(2) the most widely studied retinoid in clinical trials of breast cancer...” NCT01479192
Known as All-trans-4'-hydroxyretinanilide ChEMBL registry synonym — accepted as the source's own label CHEMBL7301
Known as Dihydroceramide N-(4-Hydroxyphenyl retinamide) “fenretinide (Dihydroceramide N-(4-Hydroxyphenyl retinamide) on severity” NCT00534898
Known as Fenretinida ChEMBL registry synonym — accepted as the source's own label CHEMBL7301
Known as FMS “The goal of this clinical trial is to determine the effect of a mucoadhesive system that releases the vitamin A derivative, fenretinide (FMS), on precancerous surface...” NCT07149220
Known as HPR “Determine the maximum tolerated dose of fenretinide (HPR) in children with high risk solid tumors.” NCT00003191
Known as IND-40, 294 “Phase II Trial Of Fenretinide (NSC-374551; IND-40, 294) In Patients With Relapsed Small Cell Lung Cancer” NCT00009971
Known as ISLA101 ClinicalTrials.gov intervention name — accepted as the source's own label NCT06528457
Known as LAU-7b ClinicalTrials.gov intervention name — accepted as the source's own label NCT05999435
2

NCT04417257

NCT03265288

Known as LXS “The purpose of this study is to determine the effectiveness of fenretinide (4-HPR/LXS) plus ketoconazole in the treatment of recurrent ovarian cancer or primary peritoneal carcinoma.” NCT01535157
Known as MCN-R-1967 ChEMBL registry synonym — accepted as the source's own label CHEMBL7301
Known as N-(4-hydroxyphenyl)retinamide “The synthetic retinoid fenretinide (N-(4-hydroxyphenyl)retinamide, 4-HPR) has shown promising anticancer activity in preclinical studies, but its limited oral bioavailability...” PMID 21498721 Mar 2011
1

“A Randomized, Double Blind, Placebo-Controlled Phase II Clinical Trial of N(4-Hydroxy-phenyl)Retinamide (Fenretinide, 4HPR) in Oral Leukoplakia” NCT00004161

Known as NSC-374551 “Phase II study of fenretinide (NSC 374551) in adults with recurrent malignant gliomas: A North American Brain Tumor Consortium study.” PMID 15514370 Nov 2004
4

“Fenretinide (4-HPR, NSC 374551) Lym-X-Sorb (LXS) Oral Powder Plus Ketoconazole in Patients With Recurrent or Resistant Neuroblastoma” NCT02075177

“Phase I Study of Fenretinide (4-HPR, NSC 374551) Lym-X-Sorb™ (LXS) Oral Powder in Patients With Recurrent or Resistant Neuroblastoma” NCT00295919

“Phase II Trial Of Fenretinide (NSC-374551; IND-40, 294) In Patients With Relapsed Small Cell Lung Cancer” NCT00009971

“A Phase I Study of Fenretinide (NSC #374551) in Children With High Risk Solid Tumors” NCT00003191

Known as NSC-760419 ChEMBL registry synonym — accepted as the source's own label CHEMBL7301
Known as Rii retinamide ChEMBL registry synonym — accepted as the source's own label CHEMBL7301
Modality Small molecule “Fenretinide, a synthetic form of retinoid” PMID 15744595 Mar 2005
Route Oral “Patients also receive either oral fenretinide or oral placebo daily for 5 years, beginning within 2 weeks after completion of any radiotherapy, or within 2 weeks of...” NCT00002646