Drugs / Topotecan
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Topotecan

Small molecule targets HIF1A, TOP1 via inhibition

Developed for
ovarian cancer · small cell lung carcinoma · neuroblastoma · fallopian tube cancer · leukemia · primary peritoneal carcinoma · cervical cancer · cancer
+177 more · cancer of unknown primary site · lung cancer · retinoblastoma · ovarian carcinoma · central nervous system neoplasm · peritoneum cancer · lymphoma · endometrial cancer · myelodysplastic syndrome · sarcoma · Ewing sarcoma · neoplasm · non-small cell lung carcinoma · childhood malignant neoplasm · childhood medulloblastoma · fallopian tube carcinoma · ovarian neoplasm · cervical adenosquamous carcinoma · gliosarcoma · metastatic malignant neoplasm · plasma cell myeloma · proliferative vitreoretinopathy · refractory malignant neoplasm · rhabdomyosarcoma · acute lymphoblastic leukemia · acute myeloid leukemia · atypical teratoid rhabdoid tumor · brain glioma · brain neoplasm · childhood ependymoma · diffuse intrinsic pontine glioma · embryonal tumor with multilayered rosettes · esophageal cancer · Ewing sarcoma of bone · extraskeletal Ewing sarcoma · female reproductive system neoplasm · glioma · kidney cancer · malignant epithelial tumor of ovary · malignant glioma · medulloblastoma · metastatic neoplasm · myeloproliferative neoplasm · neoplastic meningitis · non-Hodgkin lymphoma · osteosarcoma · ovarian clear cell cystadenocarcinoma · ovarian endometrioid adenocarcinoma · ovarian mucinous cystadenocarcinoma · ovarian serous cystadenocarcinoma · pineoblastoma · rhegmatogenous retinal detachment · supratentorial primitive neuroectodermal tumor · undifferentiated ovarian carcinoma · acute erythroid leukemia · acute leukemia of ambiguous lineage · acute megakaryoblastic leukemia in adult · acute myeloblastic leukemia with maturation · acute myeloblastic leukemia without maturation · acute myeloid leukemia with 11q23 abnormalities · acute myeloid leukemia with abnormal bone marrow eosinophils inv(16)(p13q22) or t(16;16)(p13;q22) · acute myeloid leukemia with minimal differentiation · acute myeloid leukemia with t(8;21)(q22;q22) translocation · acute myeloid leukemia, t(16;16)(p13.1;q22) · acute myelomonocytic leukemia M4 · adult acute monocytic leukemia · adult central nervous system germ cell tumor · adult liposarcoma · adult malignant mesenchymoma · AIDS-related primary central nervous system lymphoma · alveolar rhabdomyosarcoma · anaplastic astrocytoma · atypical choroid plexus papilloma · brain cancer · brain stem glioma · breast cancer · Brenner tumor · Burkitt lymphoma · cervical adenocarcinoma · cervical small cell carcinoma · cervical squamous cell carcinoma · childhood acute lymphoblastic leukemia · childhood acute myeloid leukemia · childhood botryoid rhabdomyosarcoma · childhood brain stem glioma · childhood central nervous system germ cell tumor · childhood cerebellar astrocytic neoplasm · childhood cerebral astrocytoma · childhood germ cell tumor · childhood malignant mesenchymoma · cholangiocarcinoma · choroid plexus carcinoma · colon carcinoma · COVID-19 · cutaneous neuroendocrine carcinoma · diffuse large B-cell lymphoma · endometrioid tumor · ependymoblastoma · extragonadal germ cell tumor · extragonadal nonseminomatous germ cell tumor · female breast carcinoma · ganglioneuroblastoma · gastric cancer · head and neck cancer · high grade malignant neoplasm · HIV infectious disease · Hodgkins lymphoma · immunodeficiency-associated lymphoproliferative disease · intraocular retinoblastoma · kidney Wilms tumor · large cell neuroendocrine carcinoma · large-cell immunoblastic lymphoma · liver cancer · malignant childhood germ cell neoplasm · malignant leptomeningeal tumor · malignant ovarian serous tumor · malignant pancreatic neoplasm · malignant testicular germ cell tumor · malignant tumor of meninges · medulloblastoma non-WNT/non-SHH group 3 · medulloblastoma non-WNT/non-SHH group 4 · medulloepithelioma · metastatic malignant neoplasm in the brain · myelodysplastic/myeloproliferative disease · neoplasm of mediastinum · neuroendocrine carcinoma · optic pathway glioma · ovarian epithelial tumor · ovarian mixed germ cell neoplasm · pancreatic adenocarcinoma · pediatric lymphoma · pediatric meningioma · peripheral primitive neuroectodermal tumor of bone · peripheral primitive neuroectodermal tumor of soft tissues · peritoneal carcinoma · peritoneal neoplasm · plasma cell neoplasm · pleuropulmonary blastoma · precancerous condition · primary brain neoplasm · progressive multifocal leukoencephalopathy · prostate cancer · rectal neoplasm · rhabdoid tumor · serous adenocarcinoma · small cell carcinoma · small intestine cancer · soft tissue sarcoma · squamous cell carcinoma · testicular germ cell tumor · unilateral retinoblastoma · urinary bladder cancer · urothelial carcinoma · uterine cancer · uterine cervix neoplasm · vaginal cancer · vulva cancer · Wilms tumor · colon adenocarcinoma · fallopian tube carcinosarcoma · fallopian tube clear cell adenocarcinoma · fallopian tube endometrioid adenocarcinoma · fallopian tube mucinous adenocarcinoma · fallopian tube neoplasm · fallopian tube serous adenocarcinoma · fallopian tube transitional cell carcinoma · hereditary neoplastic syndrome · lung neoplasm · ovarian carcinosarcoma · ovarian clear cell adenocarcinoma · ovarian clear cell cancer · ovarian mucinous adenocarcinoma · ovarian seromucinous carcinoma · ovarian serous adenocarcinoma · ovarian transitional cell carcinoma · primary peritoneal serous adenocarcinoma · rectum adenocarcinoma
Investigated by
National Cancer Institute (NCI) · GlaxoSmithKline · Children's Oncology Group · Gynecologic Oncology Group · SCRI Development Innovations, LLC · H. Lee Moffitt Cancer Center and Research Institute
+198 more · Alliance for Clinical Trials in Oncology · St. Jude Children's Research Hospital · SmithKline Beecham · Case Comprehensive Cancer Center · M.D. Anderson Cancer Center · NYU Langone Health · AstraZeneca · City of Hope Medical Center · Fox Chase Cancer Center · Genentech, Inc. · Mayo Clinic · Memorial Sloan Kettering Cancer Center · Gustave Roussy, Cancer Campus, Grand Paris · National Institutes of Health (NIH) · Novartis Pharmaceuticals · Baylor College of Medicine · Children's Cancer and Leukaemia Group · Eastern Cooperative Oncology Group · Eli Lilly and Company · Infuseon Therapeutics, Inc. · Masonic Cancer Center, University of Minnesota · Michael Vogelbaum, MD, PhD · National Cancer Institute, France · Sanofi · Yale University · AGO Study Group · ARCAGY/ GINECO GROUP · Accelerated Community Oncology Research Network · Amgen · Bayer · Bristol-Myers Squibb · C17 Council · Children's Hospital Medical Center, Cincinnati · Columbia University · Duke University · German Society for Pediatric Oncology and Hematology GPOH gGmbH · Herbert Irving Comprehensive Cancer Center · Hospital JP Garrahan · NRG Oncology · National Pediatric Cancer Foundation · New Approaches to Neuroblastoma Therapy Consortium · North Eastern German Society of Gynaecological Oncology · SWOG Cancer Research Network · Targeted Therapy Technologies, LLC · The Hospital for Sick Children · The Methodist Hospital Research Institute · Unity Health Toronto · University Health Network, Toronto · University of Alabama at Birmingham · University of New Mexico · Weill Medical College of Cornell University · ALZA · Abbott · Actuate Therapeutics Inc. · Armando Santoro, MD · Ascenta Therapeutics · Assistance Publique - Hôpitaux de Paris · Astex Pharmaceuticals, Inc. · Athenex, Inc. · Aultman Health Foundation · Aventis Pharmaceuticals · Baili-Bio (Chengdu) Pharmaceutical Co., Ltd. · Benaroya Research Institute · Beth Israel Deaconess Medical Center · Blokhin's Russian Cancer Research Center · Cancer Research UK · Catholic University of the Sacred Heart · Celgene Corporation · Cellid Co., Ltd. · Central European Society for Anticancer Drug Research · Centre Francois Baclesse · Centre Oscar Lambret · Centre d'Etudes et de Recherche pour l'Intensification du Traitement du Diabète · Children's Cancer Group · all 204 on the full record

Regulatory milestones approvals, filings & regulatory actions · 6 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Label expansion US (FDA) TOPOTECAN HYDROCHLORIDE 2017-09-20 fda.gov
Label expansions (3) US (FDA) HYCAMTIN 1998-11-30 – 2006-06-14 fda.gov
Approved EU (EMA) Hycamtin 1996-11-12 europa.eu
Approved US (FDA) HYCAMTIN 1996-05-28 fda.gov

Trials 316 · started per year

today
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EU approved 1996
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PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 08 trials
Phase 0 NCT06942039 Sep 2025 → Dec 2030 expected atypical teratoid rhabdoid tumor, childhood medulloblastoma, embryonal tumor with multilayered rosettes, ependymoblastoma +5 C17 Council Recruiting No outcome recorded
Phase 0 NCT06972602 Apr → Dec 2025 overdue retinoblastoma Eye & ENT Hospital of Fudan University Recruiting No outcome recorded
Phase 0 NCT04947501 Jun 2021 → Jun 2026 overdue childhood malignant neoplasm, neuroblastoma Memorial Sloan Kettering Cancer Center Active not recruiting No outcome recorded
Phase 0 NCT03927274 Jun 2019 → May 2023 brain glioma H. Lee Moffitt Cancer Center and Research Institute Terminated No outcome recorded
Phase 0 NCT03193463 Nov 2017 → Nov 2018 glioma Michael Vogelbaum, MD, PhD Withdrawn No outcome recorded
Phase 0 NCT02500459 Jul 2015 → Nov 2018 brain neoplasm, malignant glioma Michael Vogelbaum, MD, PhD Terminated No outcome recorded
Phase 0 NCT02278510 Dec 2014 → Nov 2015 malignant glioma Michael Vogelbaum, MD, PhD Completed No outcome recorded
Phase 0 NCT01466855 Oct 2011 → Oct 2015 retinoblastoma Children's Hospital Medical Center, Cincinnati Terminated No outcome recorded
Phase 1100 trials
Phase 1 NCT06425419 Sep 2026 → Dec 2027 expected proliferative vitreoretinopathy, rhegmatogenous retinal detachment Massachusetts Eye and Ear Infirmary Not yet recruiting No outcome recorded
Phase 1 NCT06666712 Jun 2026 → Jan 2028 expected brain glioma, high grade astrocytic tumor Jeffrey N. Bruce Recruiting No outcome recorded
Phase 1 NCT07194044 Feb 2026 → Oct 2030 expected Ewing sarcoma H. Lee Moffitt Cancer Center and Research Institute Recruiting No outcome recorded
Phase 1 NCT06840886 Mar 2025 → Apr 2029 expected central nervous system neoplasm, cholangiocarcinoma, endometrial cancer, ovarian cancer Pheast Therapeutics Recruiting No outcome recorded
Phase 1 NCT04994977 May 2023 → Jul 2024 atypical choroid plexus papilloma, choroid plexus carcinoma Weill Medical College of Cornell University Terminated No outcome recorded
Phase 1 NCT05101551 Feb 2023 → Apr 2027 expected acute myeloid leukemia Norman J. Lacayo Recruiting No outcome recorded
Phase 1 NCT05429502 Dec 2022 → Feb 2025 neuroblastoma Novartis Pharmaceuticals Terminated No outcome recorded
Phase 1 NCT05353439 Jul 2022 → Feb 2026 overdue small cell lung carcinoma National Cancer Institute (NCI) Active not recruiting No outcome recorded
Phase 1 NCT05246111 Feb 2022 → Jun 2023 neoplasm Merck Healthcare KGaA, Darmstadt, Germany, an affiliate of Merck KGaA, Darmstadt, Germany Completed No outcome recorded
Phase 1 NCT04514497 Oct 2021 → Feb 2025 overdue metastatic malignant neoplasm, pancreatic adenocarcinoma, small cell lung carcinoma National Cancer Institute (NCI) Active not recruiting No outcome recorded
Phase 1/232 trials
Phase 1/2 NCT03554473 Sep 2018 → Jun 2022 small cell lung carcinoma National Cancer Institute (NCI) Completed No outcome recorded
Phase 1/2 NCT02030184 Jun 2017 → Jun 2019 large cell neuroendocrine carcinoma, small cell lung carcinoma University of Maryland, Baltimore Withdrawn No outcome recorded
Phase 1/2 NCT02866006 Oct 2016 → Dec 2021 cervical cancer Cellid Co., Ltd. Completed No outcome recorded
Phase 1/2 NCT02813135 Aug 2016 → Feb 2031 expected childhood malignant neoplasm Gustave Roussy, Cancer Campus, Grand Paris Recruiting No outcome recorded
Phase 1/2 NCT02514447 Oct 2015 → Sep 2018 small cell lung carcinoma G1 Therapeutics, Inc. Completed No outcome recorded
Phase 1/2 NCT02487095 Jul 2015 → Feb 2021 non-small cell lung carcinoma, ovarian neoplasm, small cell lung carcinoma, uterine cervix neoplasm National Cancer Institute (NCI) Completed No outcome recorded
Phase 1/2 NCT02303028 Mar 2015 → Jun 2022 cancer The Hospital for Sick Children Completed No outcome recorded
Phase 1/2 NCT02100007 Apr 2014 → Jan 2016 cancer MEI Pharma, Inc. Terminated No outcome recorded
Phase 1/2 NCT01690598 Nov 2012 → Jan 2015 ovarian carcinoma Vejle Hospital Completed No outcome recorded
Phase 1/2 NCT01600573 May 2012 → Mar 2017 ovarian cancer JSehouli Unknown No outcome recorded
Phase 2126 trials
Phase 2 NCT07076095 Aug 2025 → Aug 2028 expected small cell lung carcinoma SUNHO(China)BioPharmaceutical CO., Ltd. Not yet recruiting No outcome recorded
Phase 2 NCT06818721 Mar 2025 → Apr 2027 expected proliferative vitreoretinopathy, rhegmatogenous retinal detachment Unity Health Toronto Not yet recruiting No outcome recorded
Phase 2 NCT06679634 Feb 2025 → Nov 2029 expected retinoblastoma Targeted Therapy Technologies, LLC Recruiting No outcome recorded
Phase 2 NCT06548763 Nov 2024 → Jun 2026 overdue endometrial cancer Fudan University Not yet recruiting No outcome recorded
Phase 2 NCT06528496 Jul 2024 → Jul 2029 expected neuroblastoma Memorial Sloan Kettering Cancer Center Recruiting No outcome recorded
Phase 2 NCT05736952 Mar 2023 → Feb 2026 refractory malignant neoplasm Xinhua Hospital, Shanghai Jiao Tong University School of Medicine Withdrawn No outcome recorded
Phase 2 NCT05523869 Feb 2023 → Feb 2026 overdue proliferative vitreoretinopathy Unity Health Toronto Recruiting No outcome recorded
Phase 2 NCT05800587 Feb 2023 → Aug 2028 expected non-small cell lung carcinoma, small cell lung carcinoma Fox Chase Cancer Center Recruiting No outcome recorded
Phase 2 NCT05613088 Feb 2023 → Jun 2024 ovarian neoplasm Bristol-Myers Squibb Completed No outcome recorded
Phase 2 NCT05535166 Dec 2022 → Jul 2035 expected medulloblastoma St. Jude Children's Research Hospital Recruiting No outcome recorded
Show all 126 trials opens the full record — a long page
Phase 2/33 trials
Phase 2/3 NCT07145333 Aug 2025 → Sep 2026 expected small cell lung carcinoma Han Xu, M.D., Ph.D., FAPCR, Sponsor-Investigator, IRB Chair Active not recruiting No outcome recorded
Phase 2/3 NCT04681417 Mar 2021 → Jan 2035 expected retinoblastoma Institut Curie Recruiting No outcome recorded
Phase 2/3 NCT04055038 Sep 2019 → Sep 2021 BRCA1-related cancer predisposition, BRCA2-related cancer predisposition, ovarian cancer, serous adenocarcinoma Blokhin's Russian Cancer Research Center Unknown No outcome recorded
Phase 338 trials
Phase 3 NCT06937905 Feb 2026 → Feb 2029 expected neuroendocrine carcinoma French Cooperative Thoracic Intergroup Recruiting No outcome recorded
Phase 3 NCT07214779 Dec 2025 → Nov 2028 expected ovarian cancer Incyte Corporation Recruiting No outcome recorded
Phase 3 NCT06801834 Apr 2025 → Oct 2029 expected small cell lung carcinoma Gilead Sciences Recruiting No outcome recorded
Phase 3 NCT06647953 Mar 2025 → Mar 2029 expected pleuropulmonary blastoma Children's Oncology Group Recruiting No outcome recorded
Phase 3 NCT06500026 Aug 2024 → Dec 2026 expected small cell lung carcinoma Sichuan Baili Pharmaceutical Co., Ltd. Active not recruiting No outcome recorded
Phase 3 NCT03632798 Aug 2018 → Jun 2019 ovarian cancer Cordgenics, LLC Withdrawn No outcome recorded
Phase 3 NCT03475121 Jan 2018 → Jan 2023 unilateral retinoblastoma Hospital JP Garrahan Completed No outcome recorded
Phase 3 NCT03257267 Sep 2017 → Mar 2021 squamous cell carcinoma Regeneron Pharmaceuticals Completed No outcome recorded
Phase 3 NCT02903004 Apr 2016 → Dec 2018 ovarian neoplasm Fondazione Policlinico Universitario Agostino Gemelli IRCCS Completed No outcome recorded
Phase 3 NCT02631876 Mar 2016 → Jan 2019 fallopian tube cancer, malignant epithelial tumor of ovary, primary peritoneal carcinoma ImmunoGen, Inc. Completed No outcome recorded
Phase 41 trial
Phase 4 NCT00488709 May 2003 → Apr 2007 acute myeloid leukemia PETHEMA Foundation Completed No outcome recorded
Phase not applicable8 trials
NCT02786719 Jun 2016 → Feb 2019 neuroblastoma Baylor College of Medicine Completed No outcome recorded
NCT02551718 Sep 2015 → Jun 2020 acute leukemia of ambiguous lineage, acute lymphoblastic leukemia University of Washington Completed No outcome recorded
NCT01795430 Jul 2013 → Mar 2018 Ewing sarcoma of bone, extraskeletal Ewing sarcoma, supratentorial primitive neuroectodermal tumor City of Hope Medical Center Withdrawn No outcome recorded
NCT00980551 May 2010 → Mar 2012 retinoblastoma Children's Hospital Medical Center, Cincinnati Withdrawn No outcome recorded
NCT00720096 Jul 2008 → Oct 2009 ovarian cancer H. Lee Moffitt Cancer Center and Research Institute Terminated No outcome recorded
NCT00618813 Mar 2008 → Mar 2010 Ewing sarcoma of bone Children's Oncology Group Completed No outcome recorded
NCT00526318 Jan 2007 → Dec 2016 neuroblastoma German Society for Pediatric Oncology and Hematology GPOH gGmbH Unknown No outcome recorded
NCT00109798 Mar 2005 → Jul 2006 central nervous system neoplasm, lymphoma The Methodist Hospital Research Institute Withdrawn No outcome recorded
Also used as a comparator or background therapy in 137 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 120 trials
Phase 1 NCT06930755 Background May 2026 → May 2027 expected ovarian cancer Nerviano Medical Sciences Recruiting No outcome recorded
Phase 1 NCT05990738 Background Feb 2024 → Mar 2027 expected small cell lung carcinoma Boehringer Ingelheim Active not recruiting No outcome recorded
Phase 1 NCT05521984 Background Apr 2023 → Mar 2031 expected brain cancer, childhood malignant neoplasm Washington University School of Medicine Recruiting No outcome recorded
Phase 1 NCT05421897 Background Nov 2022 → Jan 2026 overdue neuroblastoma Children's Hospital Los Angeles Active not recruiting No outcome recorded
Phase 1 NCT04022876 Background Sep 2019 → Jul 2022 non-small cell lung carcinoma, small cell lung carcinoma Aileron Therapeutics, Inc. Terminated No outcome recorded
Phase 1/28 trials
Phase 1/2 NCT07437963 Background Jul 2026 → Sep 2029 expected ganglioneuroblastoma, neuroblastoma National Cancer Institute (NCI) Not yet recruiting No outcome recorded
Phase 1/2 NCT07141771 Background Dec 2025 → Jun 2030 expected small cell lung carcinoma Cancer Institute and Hospital, Chinese Academy of Medical Sciences Not yet recruiting No outcome recorded
Phase 1/2 NCT07334301 Background Nov 2024 → Dec 2030 expected neuroblastoma University of Birmingham Recruiting No outcome recorded
Phase 1/2 NCT05652686 Background Sep 2023 → Dec 2027 expected digestive system neuroendocrine neoplasm, large cell neuroendocrine carcinoma, prostate neuroendocrine neoplasm, small cell lung carcinoma Phanes Therapeutics Recruiting No outcome recorded
Phase 1/2 NCT05266196 Background Jan 2022 → Dec 2025 Ewing sarcoma, clear cell sarcoma, desmoplastic small round cell tumor, extraskeletal myxoid chondrosarcoma +4 Salarius Pharmaceuticals, LLC Unknown No outcome recorded
Phase 237 trials
Phase 2 NCT07321912 Background Jun 2026 → Jun 2031 expected Ewing sarcoma, osteosarcoma Milton S. Hershey Medical Center Recruiting No outcome recorded
Phase 2 NCT06933394 Background May 2025 → May 2031 expected neuroblastoma Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University Recruiting No outcome recorded
Phase 2 NCT06861244 Background Mar 2025 → Sep 2030 expected embryonal tumor with multilayered rosettes University of California, San Francisco Recruiting No outcome recorded
Phase 2 NCT06449209 Background Aug 2024 → Jun 2027 expected small cell lung carcinoma BioNTech SE Active not recruiting No outcome recorded
Phase 2 NCT05295589 Comparator Jun 2022 → Mar 2023 fallopian tube endometrioid adenocarcinoma, fallopian tube serous adenocarcinoma, ovarian endometrioid adenocarcinoma, ovarian serous adenocarcinoma +1 National Cancer Institute (NCI) Withdrawn No outcome recorded
Phase 2/37 trials
Phase 2/3 NCT07106528 Comparator Aug 2025 → Dec 2027 expected small cell lung carcinoma Peking Union Medical College Hospital Not yet recruiting No outcome recorded
Phase 2/3 NCT06161025 Comparator Feb 2024 → Feb 2028 expected Daiichi Sankyo Recruiting No outcome recorded
Phase 2/3 NCT05870748 Comparator Jul 2023 → Aug 2025 fallopian tube carcinoma, malignant epithelial tumor of ovary, primary peritoneal carcinoma Sutro Biopharma, Inc. Terminated No outcome recorded
Phase 2/3 NCT03651206 Comparator Jul 2020 → Jun 2027 expected ovarian carcinosarcoma, uterine carcinosarcoma ARCAGY/ GINECO GROUP Recruiting No outcome recorded
Phase 2/3 NCT03098030 Comparator Jun 2017 → Jan 2020 small cell lung carcinoma United Therapeutics Completed No outcome recorded
Phase 364 trials
Phase 3 NCT07708753 Comparator Jul 2026 → Oct 2029 expected fallopian tube cancer, primary peritoneal carcinoma, refractory malignant neoplasm CSPC Megalith Biopharmaceutical Co.,Ltd. Not yet recruiting No outcome recorded
Phase 3 NCT07545460 Comparator Jul 2026 → Dec 2028 expected fallopian tube cancer, malignant epithelial tumor of ovary, primary peritoneal carcinoma Sichuan Baili Pharmaceutical Co., Ltd. Not yet recruiting No outcome recorded
Phase 3 NCT07286266 Comparator Jun 2026 → Dec 2029 expected ovarian neoplasm GlaxoSmithKline Recruiting No outcome recorded
Phase 3 NCT07604766 Comparator Jun 2026 → Sep 2027 expected refractory malignant neoplasm Genmab Not yet recruiting No outcome recorded
Phase 3 NCT07546500 Comparator Apr 2026 → May 2028 expected ovarian cancer K-Group, Beta, Inc., a wholly owned subsidiary of Zentalis Pharmaceuticals, Inc Recruiting No outcome recorded
Phase 41 trial
Phase 4 NCT05874401 Background Oct 2023 → Oct 2027 expected small cell lung carcinoma Pharmacosmos A/S Recruiting No outcome recorded

Press releases naming this drug 1 release

DateIssuerRelease
2000-11-02 Gilead Sciences Gilead Begins Phase II Study of NX 211, Investigational Compound for the Treatment of Patients with Topotecan Resistant Ovarian Cancer gilead.com

Evidence & citations 33 cited values

Every value below carries the sentence it was read from. 458 sources stand behind the page.

FieldValueCited text
Known as Topotecan “One or more of the following may be assigned by the physician (physician's choice) per standard of care guidelines upon study enrollment following surgery: Cytarabine,...” NCT06861244
428

“Either Paclitaxel 80 mg/m2 as a 1-h infusion, on days 1,8,15,22 every 28 days or Pegylated Liposomal Doxorubicin (PLD) 40 mg/m2 given every 4 weeks or Topotecan 4mg/m2 IV on...” NCT04421547

“Study treatment in the arm A is left to the investigator appreciations. This may include immune checkpoint inhibitors, docetaxel, topotecan for primary lung tumors, and FOLFOX,...” NCT06937905

“Control chemotherapy treatment will be chosen from any of the following standard-of-care chemotherapy drugs or combinations: * Liposomal Doxorubicin; * Docetaxel; *...” NCT03949283

“Chemotherapy - carboplatin, paclitaxel, doxorubicin, pegylated liposomal doxorubicin or topotecan administered as a single agent or as a doublet, and will be administered at...” NCT00739830

“There will be six groups: 1) combination with paclitaxel, 2) combination with topotecan, 3) combination with doxorubicin, 4) combination with 5-fluorouracil, folinic acid, and...” NCT06840886

“Treatment of relapsed disease with single agent chemotherapy based on physician's choice of weekly paclitaxel, topotecan, pegylated liposomal doxorubicin, or gemcitabine.” NCT02282020

“Patients will recieve 3 cycles of carboplatin and gemcitabine followed by 3 cycles of taxol and carboplatin and then three cycles of adriamycin and topotecan.” NCT00157560

“The possible choices as defined by the protocol: * Paclitaxel * Gemcitabine * Pegylated liposomal doxorubicin (PLD) * TopotecanNCT07546500

Topotecan-Monotherapy Vs. Topotecan + Etoposide Vs.Topotecan + Gemcitabine in Therapy in Patients With Recurrent Ovarian Cancer” NCT00312988

“Chemotherapy list: * Liposomal Doxorubicin; * Docetaxel; * Paclitaxel; * Carboplatin; * Cisplatin; * Gemcitabine; * Topotecan;” NCT03632798

“Paclitaxel 70 mg/m2/d i.v. on Days 1, 8, and 15 in combination with Topotecan 1.75 mg/m2/d i.v. on Days 1, 8, and 15, q 28 d” NCT01405235

Topotecan: Intravenously infused on Days 1, 8, and 15 of each 4 - week treatment cycle at a daily dose of 4 mg/m².” NCT06990503

Topotecan 1,25 mg/m²/d administered as an i.v. infusion over 30 minutes once daily on days 1-5, every 21 days” NCT01047891

“Combination of seclidemstat with topotecan and cyclophosphamide, as assigned per parent protocol” NCT05266196

Topotecan 0.75 mg/m2 d 1-3 + cisplatin 60-75 mg/m2 or carboplatin AUC 4-5 d 1 every 3 weeks;” NCT04055038

Topotecan: 1,0 mg/m²/d, day 1-3; q21d Carboplatin: AUC 5 on day 3 after Topotecan, q21d” NCT00170625

“Oral topotecan will be supplied in topotecan capsules and oral HM30181A-US tablets” NCT03987685

Topotecan, topoisomerase 1 inhibitor; intravenous (multiple dose, single schedule)” NCT01849874

Topotecan is administered by an ambulatory infusion pump for 72 hours each week.” NCT00002986

“Cyclophosphamide and topotecan are both FDA-approved chemotherapy drugs.” NCT02298348

Topotecan (2 mg/m2 once daily i.v. on days -8, -7, -6, -5, -4)” NCT01342237

Topotecan, 4mg/m², Intravenous, Day 1, 8, 15 every 28 days” NCT03651206

“Topoisomerase 1 inhibitor: Topotecan or Irinotecan” NCT03257267

Topotecan at 1.0 mg/m2 or 1.5 mg/m2 for 3 days” NCT02030184

topotecan (4mg/m2 on D1,8,15 every 4 weeks)” NCT03699449

topotecan, cyclophosphamide, and etoposide” NCT03042429

Topotecan IV continuously over 72 hours.” NCT00053287

Topotecan, Lurbinectedin, or Amrubicin” NCT07218146

“Thioguanine Topotecan HCl Trametinib” NCT02551718

topotecan: 1.2 mg/m\^2 IV days 1-5” NCT01576692

“cyclophosphamide and/or topotecanNCT03236857

topotecan by intravenous infusion” NCT06692166

topotecan oral capsules 1.1 mg/m2” NCT00390806

“Thiotepa, Topotecan, Toremifene” NCT02788201

“including topotecan (1.2 mg/m” NCT07230626

topotecan(2mg/m2.d, d3-d5)” NCT06933394

“Hycamptin(R) (topotecan)” NCT00602667

“Drug: topotecanNCT00316173

TopotecanNCT01703910

TopotecanNCT02665065

TopotecanNCT05421897

topotecanNCT07214779

NCT00014443

NCT00812266

NCT00319969

NCT07286266

NCT02514447

NCT00003156

NCT00006125

NCT02866006

NCT00252889

NCT00117013

NCT01533181

NCT06612151

NCT05613088

NCT00038545

NCT01600573

NCT00006373

NCT00526799

NCT01783535

NCT03554473

NCT07076095

NCT04908787

NCT04799002

NCT02866370

NCT00521144

NCT02980809

NCT02631876

NCT01497873

NCT00410631

NCT00087126

NCT00553189

NCT00006199

NCT02348398

NCT02813135

NCT00588991

NCT07194044

NCT00343044

NCT03088813

NCT07189455

NCT04022876

NCT00107471

NCT01696032

NCT00770536

NCT00057837

NCT04106219

NCT00003198

NCT03227016

NCT00004055

NCT05303727

NCT06425419

NCT00856037

NCT01840943

NCT00477282

NCT00005811

NCT01492673

NCT00215956

NCT02114229

NCT00003064

NCT00004137

NCT05295589

NCT00187083

NCT00057720

NCT00003619

NCT00437307

NCT00320983

NCT00179712

NCT00002986

NCT07099898

NCT06972602

NCT00061308

NCT00006374

NCT06619236

NCT00826891

NCT06679634

NCT05535166

NCT00638898

NCT00422682

NCT00001335

NCT00002693

NCT00437073

NCT00087048

NCT00001333

NCT00313612

NCT02786719

NCT00732420

NCT01417806

NCT02419495

NCT06548763

NCT04661852

NCT00002643

NCT00250094

NCT02500459

NCT00005793

NCT00320359

NCT01177501

NCT00547651

NCT04213937

NCT00698516

NCT06828354

NCT00005792

NCT00325416

NCT00526318

NCT00628732

NCT07365241

NCT00006391

NCT00002625

NCT06449209

NCT03709680

NCT01931098

NCT01684878

NCT00040872

NCT00041015

NCT01266447

NCT02963090

NCT04947501

NCT00006454

NCT00436644

NCT00770731

NCT00003943

NCT04994977

NCT00004186

NCT01803269

NCT00317772

NCT00004188

NCT04455139

NCT06496048

NCT04428879

NCT00488709

NCT00033696

NCT00002950

NCT00187031

NCT06801834

NCT07334301

NCT00611468

NCT00541359

NCT00002705

NCT00217555

NCT00004006

NCT06942039

NCT00674674

NCT07145333

NCT00276276

NCT00002948

NCT00392340

NCT02308527

NCT00098956

NCT05353439

NCT03126916

NCT05652686

NCT00412503

NCT07141771

NCT05092360

NCT00102375

NCT05870748

NCT00980551

NCT00462787

NCT06128837

NCT06498479

NCT05101551

NCT00541138

NCT06500026

NCT02487095

NCT00005612

NCT07218809

NCT05874401

NCT06954246

NCT05800587

NCT00109798

NCT07545460

NCT05521984

NCT01231906

NCT06394492

NCT02100007

NCT00130858

NCT01798004

NCT00231855

NCT00049998

NCT04514497

NCT00135135

NCT06994195

NCT00548418

NCT07437963

NCT00002734

NCT00002588

NCT00516438

NCT00003732

NCT00657878

NCT00002587

NCT00842452

NCT00397293

NCT02569957

NCT00888810

NCT00003281

NCT05429502

NCT00610571

NCT00744081

NCT07604766

NCT06581380

NCT00005593

NCT02822157

NCT00054444

NCT00186888

NCT00003733

NCT00807079

NCT02584478

NCT00186849

NCT01466855

NCT00189566

NCT01606878

NCT00158886

NCT05736952

NCT00314678

NCT00003415

NCT00382733

NCT00072267

NCT00003745

NCT00194935

NCT00315211

NCT00005962

NCT07106528

NCT00257816

NCT01683149

NCT00003735

NCT00918320

NCT04681417

NCT06818721

NCT00703807

NCT00365547

NCT03165292

NCT00295243

NCT00460876

NCT00006032

NCT01003938

NCT00028925

NCT06930755

NCT06528496

NCT03600649

NCT05523869

NCT00267488

NCT04156347

NCT00308165

NCT00003967

NCT00379457

NCT03896503

NCT03154996

NCT03107988

NCT06751485

NCT04029688

NCT00315861

NCT01857934

NCT00005051

NCT01004874

NCT01593228

NCT00389766

NCT04739800

NCT04943627

NCT00003958

NCT00055614

NCT03098030

NCT02030964

NCT02390843

NCT00697476

NCT04902885

NCT00877110

NCT05990738

NCT04679064

NCT00043862

NCT00043927

NCT01121406

NCT01076400

NCT02354547

NCT00003382

NCT00499616

NCT00005029

NCT02481830

NCT00550784

NCT05246111

NCT02566993

NCT00808899

NCT00005026

NCT00005021

NCT00601003

NCT00828139

NCT00193583

NCT02649673

NCT02200757

NCT00003372

NCT01630018

NCT02421588

NCT00720096

NCT01736800

NCT04047251

NCT02101788

NCT00287963

NCT06459180

NCT03289910

NCT00259935

NCT00193570

NCT00003945

NCT00006012

NCT06172296

NCT00765973

NCT00800345

NCT02738346

NCT00005990

NCT04209855

NCT00618813

NCT04073550

NCT00976911

NCT06203210

NCT00316186

NCT00002395

NCT00003297

NCT00004979

NCT06161025

NCT00002537

NCT00466232

NCT07418749

NCT04768296

NCT03193463

NCT01039025

NCT00682279

NCT00322920

NCT00002814

NCT00025272

NCT00025311

NCT00483860

NCT03927274

NCT00193401

NCT00068484

NCT00003812

NCT00322751

NCT00287911

NCT06855069

NCT00193388

NCT00084565

NCT06616532

NCT05153239

NCT03061812

NCT00100477

NCT00003917

NCT07213804

NCT00276796

NCT01500720

NCT00002515

NCT03475121

NCT06666712

NCT00193297

NCT07321912

NCT04697628

NCT02107378

NCT07708753

NCT00305942

NCT00003331

NCT00003827

NCT00193245

NCT01690598

NCT00193167

NCT00567567

NCT02303028

NCT04239092

NCT03763123

NCT02278510

NCT05740566

NCT00523432

NCT01670175

NCT02357810

NCT02903004

NCT00070200

NCT00287859

NCT00170677

NCT00065182

NCT03059667

NCT05083000

NCT06647953

NCT00502892

NCT00502762

NCT00361803

NCT02684071

NCT04322318

NCT00652691

NCT00003340

NCT00881166

NCT00294190

NCT00114166

NCT01904253

NCT02502266

Known as Evotopin ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as Ff-10850 (liposomal topotecan) ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as Hycamptamine ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as Hycamptin ClinicalTrials.gov intervention name — accepted as the source's own label NCT00429559
Known as Hycamptin(R) (topotecan) Hycamptin(R) (topotecan)NCT00602667
Known as Hycamtin “Patients must have specific minimum neutrophil and platelet counts before administration of Hycamtin. The dose of Hycamtin is 0.75 mg/m2 by intravenous infusion over 30 minutes...” NCT00826891
9

“This study was designed to find the safest and most effective dose of a combination of two chemotherapy drugs, Hycamtin® (topotecan) and Paraplatin® (carboplatin), in people...” NCT00316186

“Veliparib (ABT888) and Topotecan (Hycamtin®) for Patients With Platinum-Resistant or Partially Platinum-Sensitive Relapse of Epithelial Ovarian Cancer With Negative or Unknown...” NCT01690598

“A Phase II Evaluation of Weekly Topotecan Hydrochloride (Hycamtin®, NSC #609699) in the Treatment of Persistent or Recurrent Carcinoma of the Cervix” NCT00087126

“The purpose of this study is to find out if giving oral HYCAMTIN to patients with relapsed small cell lung cancer benefits them.” NCT00276276

“The purpose of this study is to find out if Hycamtin given weekly is safe and effective for treating your endometrial cancer.” NCT00267488

“A Pilot Study Of Hycamtin (Topotecan) And Thalomid (Thalidomide) In Patients With Recurrent Malignant Gliomas” NCT00014443

Hycamtin (Topotecan): a lyophilisate for infusion in vials containing 4 mg” NCT00918320

Hycamtin (Topotecan)” NCT00770731

Hycamtin (topotecan)” NCT00698516

Known as Hycamtin MS “Topotecan (Hycamtin MS)” NCT00003415
Known as Nogitecan ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as nogitecan hydrochloride “METHODS: Patients were randomized 1:1 to tisotumab vedotin or investigator-choice chemotherapy (topotecan [nogitecan hydrochloride], vinorelbine, gemcitabine, irinotecan, or...” PMID 41644383 Dec 2025
Known as NSC-609699 “A Limited Access Phase II Trial of Weekly Topotecan (NSC #609699), Paclitaxel (NSC #673089), and Cisplatin (NSC #119875) in the Treatment of Advanced, Persistent, or Recurrent...” NCT00276796
6

“Topotecan hydrochloride, TOPO, NSC-609699; plus external-beam irradiation using linear accelerators with photon energies between 4 and 10 MV (electrons acceptable for the boost field).” NCT00002625

“A Phase II Evaluation of Weekly Topotecan Hydrochloride (Hycamtin®, NSC #609699) in the Treatment of Persistent or Recurrent Carcinoma of the Cervix” NCT00087126

“Phase II Evaluation of Three-Day Topotecan (NSC 609699) in Recurrent Platinum-Sensitive Ovarian or Primary Peritoneal Cancer” NCT00005029

“A Phase II Study of Continuous 21 Day Infusion of Topotecan (NSC # 609699) in Children With Relapsed Solid Tumors” NCT00003745

“Single-Agent Chemotherapy. Topotecan, TOPO, NSC-609699.” NCT00002705

“Topotecan, TOPO, NSC-609699.” NCT00002588

Known as NSC-641007 ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as NSC-759263 ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as Potactasol ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as SK&F S-104864-A ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as SK-S-104864-A ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as SKF 104864 “Topotecan (SKF 104864) With Recombinant GM-CSF (Sargramostim)” NCT00002950
1

“oral topotecan (SK&F-104864); lapatinib (GW572016)” NCT00682279

Known as TLI “Topotecan Liposomes Injection (TLI)” NCT00765973
Known as TOPO Topotecan hydrochloride, TOPO, NSC-609699; plus external-beam irradiation using linear accelerators with photon energies between 4 and 10 MV (electrons acceptable for the boost field).” NCT00002625
Known as Topotecan (as hydrochloride) ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as Topotecan - Hycamtin Topotecan - HycamtinNCT00610571
Known as Topotecan actavis ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as Topotecan eagle ChEMBL registry synonym — accepted as the source's own label CHEMBL84
Known as Topotecan HCl “Participants will receive topotecan HCl 1.25 mg per square meter per day, intravenously for 30-minutes duration, on Day 1 to Day 5 of each cycle.” NCT01840943
Known as Topotecan hospira ChEMBL registry synonym — accepted as the source's own label CHEMBL84