Drugs / pyrimethamine
last change Aug 2026 re-read 2 minutes ago

pyrimethamine

Small molecule targets DHFR, STAT3 via inhibition

Developed for
malaria · Plasmodium falciparum malaria · HIV infectious disease · anemia · cerebral toxoplasmosis · pregnancy disorder · autoimmune disease · lymphoproliferative syndrome
+19 more · Plasmodium vivax malaria · toxoplasmosis · chronic lymphocytic leukemia/small lymphocytic lymphoma · familial amyotrophic lateral sclerosis · head and neck cancer · iron deficiency anemia · lymphatic system disorder · major depressive disorder · myelodysplastic syndrome · pneumocystosis · Sandhoff disease · Schistosoma mansoni infectious disease · schizophrenia · sexually transmitted disease · Tay-Sachs disease · urinary schistosomiasis · chorioretinitis · congenital toxoplasmosis · parasitemia
Investigated by
London School of Hygiene and Tropical Medicine · National Institute of Allergy and Infectious Diseases (NIAID) · Cheikh Anta Diop University, Senegal · Dafra Pharma · Erasmus Medical Center · Global Fund
+96 more · Hospital Clinic of Barcelona · Institut de Recherche pour le Developpement, Senegal · Malaria Consortium · Medical Research Council, South Africa · Ministry of Health, Senegal · Radboud University Medical Center · University of California, San Francisco · Centers for Disease Control and Prevention · Department of State for Health and Social Welfare, The Gambia · Deutscher Akademischer Austausch Dienst · European Commission · Glaxo Wellcome · Institute of Tropical Medicine, Belgium · Kenya Medical Research Institute · Malaria Research and Training Center, Bamako, Mali · Medical Research Council Unit, The Gambia · Papua New Guinea Institute of Medical Research · Professor Karen I Barnes · QIMR Berghofer Medical Research Institute · Research Institute for Development · Sanaria Inc. · Swiss Tropical & Public Health Institute · The PATH Malaria Vaccine Initiative (MVI) · United States Agency for International Development (USAID) · Washington University School of Medicine · World Health Organization · AIDSfonds · Agencia Española de Cooperación Internacional · Albert Einstein College of Medicine · Alliance for International Medical Action · Alliance médicale contre le paludisme, Mali · Bernhard Nocht Institute for Tropical Medicine · Beth Israel Deaconess Medical Center · Bill and Melinda Gates Foundation · Brigham and Women's Hospital · Bristol-Myers Squibb · Center for Primary Care and Public Health (Unisante), University of Lausanne, Switzerland · Centre for Global Health Research, Ghana · Centre national de recherche et de formation sur le paludisme · Charite University, Berlin, Germany · Chiang Mai University · DBL -Institute for Health Research and Development · Dana-Farber Cancer Institute · Department for International Development, United Kingdom · Department of Medical Services Ministry of Public Health of Thailand · Division Controle Medicale Scolaire, Ministry of Education, Senegal · Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) · Faculté des Sciences de la Santé, Bénin · French National Institute of Health and Medical Research · German Federal Ministry of Education and Research · GlaxoSmithKline · Harvard University · HealthNet TPO · Heidelberg University · INDEPTH Network · Institut National d'Etude et d'Action pour le Developpement de l'Education, Senegal · Institut des Sciences Biomédicales Appliquées, Bénin · KEMRI-Wellcome Trust Collaborative Research Program · Kilimanjaro Christian Medical Centre, Tanzania · Kwame Nkrumah University of Science and Technology · Lymphoma Research Foundation · Malaria Consortium, UK · Medical Research Council · Ministry of Foreign Affairs, France · Ministry of Health, Malawi · Ministry of health, Mali · Montefiore Medical Center · Muscular Dystrophy Association · National Institute for Medical Research, Tanzania · National Malaria Control Program, Benin · National Malaria Control Program, Niger · Pfizer · Seoul National University Hospital · Stanley Medical Research Institute · all 102 on the full record

Regulatory milestones approvals, filings & regulatory actions · 1 recorded

MilestoneJurisdictionBrandIndicationDateSentence it was read from
Approved US (FDA) DARAPRIM 1953-01-23 fda.gov

Trials 75 · started per year

today
US approved 1953
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PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 01 trial
Phase 0 NCT05678348 Aug 2023 → Jul 2025 head and neck cancer Washington University School of Medicine Completed No outcome recorded
Phase 110 trials
Phase 1 NCT04086719 Sep → Oct 2019 Bristol-Myers Squibb Completed No outcome recorded
Phase 1 NCT03057990 Sep 2019 → Jun 2021 myelodysplastic syndrome Montefiore Medical Center Withdrawn No outcome recorded
Phase 1 NCT03258762 Sep → Nov 2017 toxoplasmosis GlaxoSmithKline Completed No outcome recorded
Phase 1 NCT03083847 Jun 2017 → Jun 2019 malaria National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 1 NCT02511054 Jul 2015 → Oct 2016 malaria National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 1 NCT01973933 Jun → Aug 2013 Seoul National University Hospital Completed No outcome recorded
Phase 1 NCT00065390 Jul 2003 → Jun 2005 autoimmune disease, lymphatic system disorder, lymphoproliferative syndrome National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 1 NCT00013689 Mar 2001 → Mar 2003 autoimmune disease, lymphoproliferative syndrome National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 1 NCT00000973 ? → Mar 1995 HIV infectious disease, cerebral toxoplasmosis National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 1 NCT00000966 HIV infectious disease, cerebral toxoplasmosis Pfizer Completed No outcome recorded
Phase 1/211 trials
Phase 1/2 NCT07384624 Apr 2026 → Jun 2028 expected HIV infectious disease Erasmus Medical Center Not yet recruiting No outcome recorded
Phase 1/2 NCT06240520 Apr 2024 → May 2025 HIV infectious disease Erasmus Medical Center Unknown No outcome recorded
Phase 1/2 NCT04280692 Aug 2022 → Dec 2025 Plasmodium falciparum malaria University of Oxford Suspended No outcome recorded
Phase 1/2 NCT03952650 May 2019 → Feb 2021 malaria National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 1/2 NCT03525730 Apr 2018 → Jul 2019 HIV infectious disease Erasmus Medical Center Completed No outcome recorded
Phase 1/2 NCT02836002 Jun 2016 → Jun 2017 malaria Radboud University Medical Center Completed No outcome recorded
Phase 1/2 NCT01319448 Sep 2011 → Apr 2013 malaria, sickle cell disease London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 1/2 NCT01066663 Mar 2010 → Feb 2022 chronic lymphocytic leukemia/small lymphocytic lymphoma Dana-Farber Cancer Institute Completed No outcome recorded
Phase 1/2 NCT01083667 Nov 2009 → Dec 2014 familial amyotrophic lateral sclerosis Weill Medical College of Cornell University Completed No outcome recorded
Phase 1/2 NCT01102686 Aug 2009 → Nov 2010 Sandhoff disease, Tay-Sachs disease The Hospital for Sick Children Completed No outcome recorded
Phase 25 trials
Phase 2 NCT05081089 Oct → Dec 2021 Plasmodium falciparum malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 2 NCT02831023 Jul 2016 → Jan 2017 malaria University of California, San Francisco Completed No outcome recorded
Phase 2 NCT00322907 Apr 2000 → Jan 2003 malaria Center for Primary Care and Public Health (Unisante), University of Lausanne, Switzerland Terminated No outcome recorded
Phase 2 NCT00000794 ? → Apr 1998 HIV infectious disease, cerebral toxoplasmosis National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 2 NCT00000643 ? → May 1994 HIV infectious disease, cerebral toxoplasmosis National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 2/35 trials
Phase 2/3 NCT00561899 Aug 2007 → Feb 2008 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 2/3 NCT00510159 Aug → Oct 2007 urinary schistosomiasis Dafra Pharma Completed No outcome recorded
Phase 2/3 NCT00119132 Jun 2005 → Dec 2006 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 2/3 NCT00158574 Jan 2005 → Apr 2008 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 2/3 NCT00132561 Jun 2002 → Dec 2003 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 314 trials
Phase 3 NCT05946642 Jul 2023 → May 2024 malaria Malaria Consortium Unknown No outcome recorded
Phase 3 NCT00948896 Jun 2010 → Apr 2014 malaria University of California, San Francisco Completed No outcome recorded
Phase 3 NCT01136850 Nov 2009 → Dec 2012 anemia, malaria, sexually transmitted disease University of Melbourne Completed No outcome recorded
Phase 3 NCT01054651 Oct → Dec 2009 Schistosoma mansoni infectious disease Kenya Medical Research Institute Completed No outcome recorded
Phase 3 NCT00432367 Feb 2007 → Feb 2009 anemia, malaria, pregnancy disorder London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 3 NCT00484900 May 2006 → May 2007 Plasmodium falciparum malaria Dafra Pharma Completed No outcome recorded
Phase 3 NCT00274235 Jul 2005 → Mar 2008 malaria Research Institute for Development Completed No outcome recorded
Phase 3 NCT00123552 Nov 2004 → Jun 2006 malaria University of California, San Francisco Completed No outcome recorded
Phase 3 NCT00132548 Jun → Dec 2004 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 3 NCT00158561 Feb 2004 → Mar 2006 Plasmodium vivax malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 413 trials
Phase 4 NCT06337253 Mar → May 2024 Plasmodium falciparum malaria Malaria Consortium Unknown No outcome recorded
Phase 4 NCT05979896 Jul → Sep 2023 malaria Malaria Consortium Unknown No outcome recorded
Phase 4 NCT01651416 Jul → Dec 2012 anemia, malaria Centre for Global Health Research, Ghana Completed No outcome recorded
Phase 4 NCT01636895 Jan 2011 → Nov 2012 pregnancy disorder Malaria Consortium, UK Unknown No outcome recorded
Phase 4 NCT00376155 May 2006 → Feb 2007 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 4 NCT00372632 Dec 2005 → Apr 2008 Institute of Tropical Medicine, Belgium Completed No outcome recorded
Phase 4 NCT00125489 May → Dec 2005 Plasmodium falciparum malaria National Institute of Allergy and Infectious Diseases (NIAID) Completed No outcome recorded
Phase 4 NCT00164710 Apr → Sep 2005 Plasmodium falciparum malaria Centers for Disease Control and Prevention Completed No outcome recorded
Phase 4 NCT00367081 May 2003 → Aug 2004 AIDS, cerebral toxoplasmosis Department of Medical Services Ministry of Public Health of Thailand Completed No outcome recorded
Phase 4 NCT00168948 Mar 2003 → Aug 2005 anemia, malaria Charite University, Berlin, Germany Unknown No outcome recorded
Phase not applicable16 trials
NCT03454048 May → Nov 2018 Plasmodium falciparum malaria Radboud University Medical Center Completed No outcome recorded
NCT03079388 Feb 2017 → Sep 2019 nutritional disorder, pregnancy disorder Washington University School of Medicine Completed No outcome recorded
NCT03035305 Aug → Nov 2016 malaria Alliance for International Medical Action Completed No outcome recorded
NCT01634945 Apr 2012 → May 2013 anemia Swiss Federal Institute of Technology Completed No outcome recorded
NCT01454752 Nov 2011 → Feb 2012 anemia, malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
NCT00738946 Aug → Dec 2008 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
NCT00380146 Sep 2006 → Feb 2008 malaria Professor Karen I Barnes Completed No outcome recorded
NCT00331708 Apr 2006 → Jul 2007 malaria Professor Karen I Barnes Terminated No outcome recorded
NCT00258024 Nov 2005 → Sep 2007 anemia, malaria DBL -Institute for Health Research and Development Completed No outcome recorded
NCT00231452 Sep 2005 → Mar 2009 malaria Hospital Clinic of Barcelona Completed No outcome recorded
Also used as a comparator or background therapy in 35 trials
PhaseRegistry idDatesIndicationSponsorStatusOutcome
Phase 14 trials
Phase 1 NCT03599596 Comparator Sep → Dec 2018 malaria University College Hospital, Ibadan Unknown No outcome recorded
Phase 1 NCT02527005 Comparator Sep 2015 → Aug 2016 HIV infectious disease, malaria University of Ibadan Completed No outcome recorded
Phase 1 NCT02524444 Comparator Sep 2015 → Aug 2016 ORIYOMI OMOTOYOSI AKINYOTU Completed No outcome recorded
Phase 1 NCT00679744 Comparator May 2008 → Mar 2010 Sandhoff disease, Tay-Sachs disease Exsar Corporation Withdrawn No outcome recorded
Phase 22 trials
Phase 2 NCT02909712 Comparator Sep 2016 → Jan 2020 malaria, parasitemia, poisoning London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 2 NCT01132248 Comparator May 2010 → Dec 2012 urinary schistosomiasis Albert Schweitzer Hospital Completed No outcome recorded
Phase 2/31 trial
Phase 2/3 NCT00941785 Comparator Jul → Dec 2009 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 314 trials
Phase 3 NCT06173206 Comparator Jun → Dec 2024 malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 3 NCT04319380 Comparator Apr 2020 → Mar 2022 Plasmodium falciparum malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 3 NCT04189744 Comparator Dec 2019 → Oct 2022 Trichomonas vaginitis urogenital infection, bacterial vaginosis, malaria London School of Hygiene and Tropical Medicine Completed No outcome recorded
Phase 3 NCT02793622 Comparator Sep 2016 → Dec 2018 malaria University of California, San Francisco Completed No outcome recorded
Phase 3 NCT01746199 Comparator Dec 2013 → Oct 2015 HIV infectious disease, malaria Institut Pasteur Completed No outcome recorded
Phase 46 trials
Phase 4 NCT03178643 Comparator Jan 2018 → Dec 2020 Plasmodium falciparum malaria Duke University Completed No outcome recorded
Phase 4 NCT02592408 Comparator Nov 2015 → May 2016 malaria Menzies School of Health Research Completed No outcome recorded
Phase 4 NCT02575755 Comparator Oct 2012 → Jul 2016 Plasmodium falciparum malaria, pregnancy disorder Papua New Guinea Institute of Medical Research Unknown No outcome recorded
Phase 4 NCT01669941 Comparator Aug 2012 → Oct 2014 malaria, pregnancy disorder Kenya Medical Research Institute Completed No outcome recorded
Phase 4 NCT00964691 Comparator Aug 2009 → Aug 2010 malaria Ministry of Health and Medical Services, Solomon Islands Terminated No outcome recorded
Phase not applicable8 trials
NCT06869850 Background Sep 2025 → Dec 2027 expected cognitive impairment with or without cerebellar ataxia, kwashiorkor Washington University School of Medicine Recruiting No outcome recorded
NCT06002438 Background Oct 2023 → Dec 2024 protein-energy malnutrition Washington University School of Medicine Completed No outcome recorded
NCT04238845 Background Jul 2020 → Jul 2021 malaria, protein-energy malnutrition Institut de Recherche en Sciences de la Sante, Burkina Faso Unknown No outcome recorded
NCT00811421 Comparator Sep 2009 → Dec 2012 HIV infectious disease, malaria, pregnancy disorder Hospital Clinic of Barcelona Completed No outcome recorded
NCT00509015 Comparator Feb → Aug 2008 Plasmodium falciparum malaria Radboud University Medical Center Completed No outcome recorded

Evidence & citations 19 cited values

Every value below carries the sentence it was read from. 111 sources stand behind the page.

FieldValueCited text
Known as pyrimethamine “Patients with uncomplicated falciparum malaria and over six months of age were recruited in Cameroon, Mali, Rwanda and Sudan. 1,384 patients were randomly assigned to receive...” PMID 19366448 Apr 2009
109

“Treatment with a single dose of sulfadoxine /pyrimethamine plus three doses of amodiaquine or placebo was given to all study subjects at monthly intervals on three occasions...” NCT00944840

“antimalarial artemisinin-based combination therapy (ACT) artesunate +sulfamethoxypyrazine/pyrimethamine (As+SMP), administered in doses used for malaria, to treat Schistosoma...” PMID 19802383 Oct 2009

“Amodiaquine (10 mg/kg over 3 days) and Sulfadoxine Pyrimethamine (25 mg of sulfadoxine + 1.25 mg of pyrimethamine per kg in a single dose) or placebo administered over 3 rounds...” NCT00738946

“This preventive measures involves administering antimalarial drugs (Amodiaquine-Sulfadoxine-Pyrimethamine) to children aged 6- 59 months on a monthly basis during the high...” NCT04238845

“Sulfadoxine/Pyrimethanine-Amodiaquine (SP-AQ) is a combination therapy comprised of sulfadoxine and pyrimethamine (two antifolate antimicrobials) co-administered with amodiaquine.” NCT03178643

“IPTi doses 1 and 2, at ages 2 and 3 months, sulphadoxine 250mg, pyrimethamine 12.5mg IPTi doses 3, at 9 months of age, sulphadoxine 500mg, pyrimethamine 25mg” NCT00158574

“One cycle of SMC consisting of sulphadoxine - pyrimethamine (SP) 500mg/25 mg, and amodiaquine (AQ) 150mg on day 1, and AQ 150mg on days 2 and 3.” NCT04319380

“Intervention: Random assignment to receive either Cotrifazid, mefloquine or the standard treatment of quinine+sulfadoxine/pyrimethamine (SP).” NCT00322907

“Sulfadoxine-pyrimethamine (500 mg / 25 mg) given every 4 weeks, beginning at enrollment or at 13 weeks' gestation, whichever is later.” NCT03079388

“It is used in a fixed dose combination of 20 parts sulphadoxine with 1 part pyrimethamine given orally or intramuscularly.” NCT05979896

“One dose of SP (500 mg sulfadoxine plus 25 mg pyrimethamine, or half of the dose if body weight =\< 10 kg)” NCT01634945

“For children aged 6-11 months: sulfadoxine 250mg/pyrimethamine 12.5mg and amodiaquine 75mg” NCT03035305

“sulfadoxine-pyrimethamine IPTp will be administered following current WHO recommendations” NCT01132248

“3 tablets of sulfadoxine (500 mg) and pyrimethamine (25 mg) given at each ANC visit” NCT01669941

“Children will receive 500mg sulfadoxine plus 25mg pyrimethamine as one tablet” NCT06173206

“Sulphadoxine-pyrimethamine (500/25mg) according to age, given on day 1” NCT01454752

“SP(500mg sulfadoxine/25mg pyrimethamine)1.25mg SP per kg stat” NCT00561899

“One dose of Sulfadoxine 25mg/kg and pyrimethamine 1.25mg/kg” NCT00941785

“3 days of artesunate sulfadoxine/pyrimethamine on days 0-2” NCT02592408

NCT00361114

NCT00372632

NCT00432367

NCT00203736

NCT00304980

NCT01973933

NCT00964691

NCT06240520

NCT04280692

NCT05946642

NCT00123552

NCT05678348

NCT01189448

NCT02575755

NCT02836002

NCT00509015

NCT03083847

NCT00811421

NCT02527005

NCT01054651

NCT00682578

NCT00004317

NCT00120809

NCT00231452

NCT02909712

NCT00140361

NCT00132535

NCT02831023

NCT00679744

NCT01636895

NCT00168948

NCT00258024

NCT00209794

NCT01083667

NCT00852371

NCT00331708

NCT06337253

NCT01136850

NCT02793622

NCT01319448

NCT00132548

NCT01746199

NCT00299247

NCT03599596

NCT05081089

NCT00367081

NCT00125489

NCT00948896

NCT00274235

NCT01443130

NCT01066663

NCT00372294

NCT00460369

NCT00065390

NCT03454048

NCT00380146

NCT01651416

NCT03057990

NCT00452907

NCT00000643

NCT01103063

NCT06869850

NCT00158561

NCT00164710

NCT00132561

NCT00646126

NCT02524444

NCT00002064

NCT00000674

NCT06002438

NCT04189744

NCT00000727

NCT02511054

NCT00000794

NCT00000966

NCT00497471

NCT01102686

NCT00119132

NCT00206739

NCT04086719

NCT03525730

NCT00013689

NCT00376155

NCT07384624

NCT00300404

NCT00000666

NCT03258762

NCT00000973

NCT00951106

NCT03952650

Known as Chloridine ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as Daraprim “Six to 8 individuals, with ALPS will be treated for up to 3 months, initially, with twice-weekly pyrimethamine (Daraprim) at escalating doses adjusted by weight” NCT00065390
Known as GNF-PF-5586 ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as Malacide ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as NSC-3061 ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as Pirimetamina ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as PYR “either pyrimethamine (PYR) or chloroquine as a partner drug” NCT03952650
2

“Drug: Pyrimethamine (PYR)” NCT07384624

Pyrimethamine (PYR)” NCT02511054

Known as Pyrimethamine = Malocide Pyrimethamine = Malocide®” NCT01189448
Known as Pyrimethamine component of fansidar ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as Pyrimethaminum ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as RP-4753 ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as TCMDC-123831 ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as TCMDC-125860 ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Known as WR-2978 ChEMBL registry synonym — accepted as the source's own label CHEMBL36
Action Restore “If Hex A can function normally in presence of Pyrimethamine, this drug should be able restore the brain malfunction of these patients since Hex A can now efficiently break down...” NCT00679744
Modality Small molecule CHEMBL36
Route Oral oral azithromycin and pyrimethamine” NCT00000966
Target STAT3 “pyrimethamine may target a protein in tumor cells, called STAT3NCT01066663